NCT02659397

Brief Summary

The purpose of this research study is to measure the amount of atorvastatin and ETC-1002 in the blood, to determine how ETC-1002 affects the level of LDL-cholesterol (bad cholesterol) and other markers of health and disease in blood and urine, and to see how ETC-1002 is tolerated in the body compared to placebo when added to stable atorvastatin 80 mg background therapy in statin-treated patients.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
68

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Dec 2015

Shorter than P25 for phase_2

Geographic Reach
1 country

19 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

December 1, 2015

Completed
1 month until next milestone

First Submitted

Initial submission to the registry

January 12, 2016

Completed
8 days until next milestone

First Posted

Study publicly available on registry

January 20, 2016

Completed
5 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 1, 2016

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 1, 2016

Completed
Last Updated

March 29, 2019

Status Verified

March 1, 2019

Enrollment Period

7 months

First QC Date

January 12, 2016

Last Update Submit

March 26, 2019

Conditions

Keywords

LDL-cholesterolHypercholesterolemiaETC-1002Adenosine triphosphate citrate lyaseAtorvastatin

Outcome Measures

Primary Outcomes (3)

  • Peak plasma concentration (Cmax) pharmacokinetics of atorvastatin and its active metabolites

    Fold change in Cmax from prior-to to following 2 week treatment with ETC-1002

    2 weeks

  • 24-hour area under the curve (AUC) pharmacokinetics of atorvastatin and its active metabolites

    Fold change in AUC from prior-to to following 2 week treatment with ETC-1002

    2 weeks

  • Percent change in LDL-cholesterol

    Percent Change from baseline to 4 week treatment, incremental lowering of LDL-C

    4 weeks

Secondary Outcomes (5)

  • Percent change in hsCRP

    4 weeks

  • Percent change in total cholesterol

    4 weeks

  • Percent change in non-HDL-cholesterol

    4 weeks

  • Percent change in apolipoprotein B

    4 weeks

  • 24-hour post dose plasma concentration pharmacokinetics of ETC-1002 and its active metabolite

    2 weeks

Study Arms (2)

ETC-1002 + Atorvastatin

EXPERIMENTAL

ETC-1002 180 mg treatment, oral once daily added-on to Atorvastatin 80 mg once daily

Drug: ETC-1002Drug: Atorvastatin

Placebo + Atorvastatin

PLACEBO COMPARATOR

Placebo treatment, oral once daily added-on to Atorvastatin 80 mg once daily

Drug: AtorvastatinDrug: Placebo

Interventions

Blinded ETC-1002 180 mg tablet once daily for 4 weeks (Weeks 1 to 4)

Also known as: bempedoic acid
ETC-1002 + Atorvastatin

Atorvastatin 80 mg tablet once daily for 8 weeks (Weeks -4 to 4)

ETC-1002 + AtorvastatinPlacebo + Atorvastatin

Blinded ETC-1002-matched placebo tablet once daily for 4 weeks (Weeks 1 to 4)

Placebo + Atorvastatin

Eligibility Criteria

Age18 Years - 70 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Taking daily stable statin doses for at least 4 weeks prior to screening visit.
  • LDL-C between 100-220 mg/dL for patients taking daily high-intensity statin (for 4 weeks prior to switching to sponsor -provided atorvastatin 80 mg/day and stopping all other lipid-regulating drugs and supplements) at the screening visit; or,
  • LDL-C between 115-220 mg/dL for patients taking moderate- or low-intensity statin (for 4 weeks prior to switching to sponsor -provided atorvastatin 80 mg/day and stopping all other lipid-regulating drugs and supplements) at the screening visit.
  • Must be willing to discontinue other lipid-regulating therapies during the study

You may not qualify if:

  • History of acute significant cardiovascular disease.
  • Current clinically significant cardiovascular disease.
  • History of inability to tolerate any statin at any dose due to muscle-related pain or weakness.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (19)

Unknown Facility

Anaheim, California, 92801, United States

Location

Unknown Facility

Los Angeles, California, 90057, United States

Location

Unknown Facility

Northridge, California, 91324, United States

Location

Unknown Facility

Clearwater, Florida, 33765, United States

Location

Unknown Facility

Jacksonville, Florida, 32216, United States

Location

Unknown Facility

Miami, Florida, 33126, United States

Location

Unknown Facility

Port Orange, Florida, 32127, United States

Location

Unknown Facility

Boise, Idaho, 83642, United States

Location

Unknown Facility

Chicago, Illinois, 60607, United States

Location

Unknown Facility

Springfield, Illinois, 62711, United States

Location

Unknown Facility

Louisville, Kentucky, 40213, United States

Location

Unknown Facility

Berlin, New Jersey, 08009, United States

Location

Unknown Facility

Rapid City, South Dakota, 57701, United States

Location

Unknown Facility

Carrollton, Texas, 75006, United States

Location

Unknown Facility

West Jordan, Utah, 84088, United States

Location

Unknown Facility

Arlington, Virginia, 22203, United States

Location

Unknown Facility

Lynchburg, Virginia, 24501, United States

Location

Unknown Facility

Richmond, Virginia, 23294, United States

Location

Unknown Facility

Renton, Washington, 98057, United States

Location

Related Publications (5)

  • Thompson PD, Rubino J, Janik MJ, MacDougall DE, McBride SJ, Margulies JR, Newton RS. Use of ETC-1002 to treat hypercholesterolemia in patients with statin intolerance. J Clin Lipidol. 2015 May-Jun;9(3):295-304. doi: 10.1016/j.jacl.2015.03.003. Epub 2015 Mar 19.

    PMID: 26073387BACKGROUND
  • Nikolic D, Mikhailidis DP, Davidson MH, Rizzo M, Banach M. ETC-1002: a future option for lipid disorders? Atherosclerosis. 2014 Dec;237(2):705-10. doi: 10.1016/j.atherosclerosis.2014.10.099. Epub 2014 Oct 31.

    PMID: 25463109BACKGROUND
  • Filippov S, Pinkosky SL, Newton RS. LDL-cholesterol reduction in patients with hypercholesterolemia by modulation of adenosine triphosphate-citrate lyase and adenosine monophosphate-activated protein kinase. Curr Opin Lipidol. 2014 Aug;25(4):309-15. doi: 10.1097/MOL.0000000000000091.

    PMID: 24978142BACKGROUND
  • Gutierrez MJ, Rosenberg NL, Macdougall DE, Hanselman JC, Margulies JR, Strange P, Milad MA, McBride SJ, Newton RS. Efficacy and safety of ETC-1002, a novel investigational low-density lipoprotein-cholesterol-lowering therapy for the treatment of patients with hypercholesterolemia and type 2 diabetes mellitus. Arterioscler Thromb Vasc Biol. 2014 Mar;34(3):676-83. doi: 10.1161/ATVBAHA.113.302677. Epub 2014 Jan 2.

    PMID: 24385236BACKGROUND
  • Ballantyne CM, Davidson MH, Macdougall DE, Bays HE, Dicarlo LA, Rosenberg NL, Margulies J, Newton RS. Efficacy and safety of a novel dual modulator of adenosine triphosphate-citrate lyase and adenosine monophosphate-activated protein kinase in patients with hypercholesterolemia: results of a multicenter, randomized, double-blind, placebo-controlled, parallel-group trial. J Am Coll Cardiol. 2013 Sep 24;62(13):1154-62. doi: 10.1016/j.jacc.2013.05.050. Epub 2013 Jun 13.

    PMID: 23770179BACKGROUND

MeSH Terms

Conditions

HyperlipidemiasHypercholesterolemia

Interventions

8-hydroxy-2,2,14,14-tetramethylpentadecanedioic acidAtorvastatin

Condition Hierarchy (Ancestors)

DyslipidemiasLipid Metabolism DisordersMetabolic DiseasesNutritional and Metabolic Diseases

Intervention Hierarchy (Ancestors)

PyrrolesAzolesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsHeptanoic AcidsFatty AcidsLipids

Study Officials

  • Mary McGowan, MD

    Esperion Therapeutics, Inc.

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 12, 2016

First Posted

January 20, 2016

Study Start

December 1, 2015

Primary Completion

July 1, 2016

Study Completion

July 1, 2016

Last Updated

March 29, 2019

Record last verified: 2019-03

Locations