NCT00514579

Brief Summary

The hypothesis of the study is double unit umbilical cord blood transplantation in adults will be associated with a one year survival rate of at least 40%.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
56

participants targeted

Target at P25-P50 for phase_2

Timeline
Completed

Started Aug 2007

Longer than P75 for phase_2

Geographic Reach
1 country

10 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

August 1, 2007

Completed
7 days until next milestone

First Submitted

Initial submission to the registry

August 8, 2007

Completed
2 days until next milestone

First Posted

Study publicly available on registry

August 10, 2007

Completed
6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 1, 2013

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

August 1, 2013

Completed
Last Updated

March 10, 2014

Status Verified

March 1, 2014

Enrollment Period

6 years

First QC Date

August 8, 2007

Last Update Submit

March 7, 2014

Conditions

Keywords

Cord Blood Stem Cell TransplantationHematologic MalignanciesLeukemiaMyelodysplastic Syndrome

Outcome Measures

Primary Outcomes (1)

  • Measure overall survival of double unit UCBT in adult patients with hematologic malignancies

    One year

Secondary Outcomes (9)

  • Measure incidence of donor-derived neutrophil and platelet recovery

    100 Days

  • Measure contribution of each unit to initial and sustained engraftment

    2 years

  • Measure incidence and severity of acute graft-versus-host disease

    100 Days

  • Measure incidence and severity of chronic GVHD

    1 year

  • Measure incidence of transplant-related mortality

    6 months

  • +4 more secondary outcomes

Study Arms (1)

Myeloablative double unit UCBT

OTHER

Myeloablative preparative regimen of chemotherapy and radiation followed by double unit umbilical cord blood transplantation

Procedure: Cord blood transplantation

Interventions

Myeloablative preparative regimen of chemotherapy and radiation followed by double unit umbilical cord blood transplantation

Myeloablative double unit UCBT

Eligibility Criteria

Age22 Years - 50 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64)

You may qualify if:

  • Age 22 - 50 years
  • Patients will have one of the following hematological malignancies:
  • Acute myelogenous leukemia (AML): Complete first remission (CR1) at high risk for relapse or Complete second remission (CR2)
  • Acute lymphoblastic leukemia (ALL): Complete first remission (CR1) at high risk for relapse or Complete second remission (CR2)
  • Acute undifferentiated leukemia (AUL) or biphenotypic leukemia: CR1 or CR2
  • Myelodysplastic Syndrome (MDS) with one of the following: Low and Intermediate-1 International Prognostic Scoring System (IPSS) score with Life-threatening neutropenia or thrombocytopenia; or Platelet transfusion dependence Intermediate-2 or High IPSS score Therapy-related disease: patient with history of chemotherapy and current evidence of MDS
  • Patients with adequate organ function and performance status criteria
  • Two Suitable Umbilical Cord Blood Units: a cryopreserved dose of at least 1.5 x 107 TNC/kg. If the unit contains red cells at time of cryopreservation, the cryopreserved dose must be at least 2.0 x 107 TNC/kg. Each unit must be at least 4/6 HLA-A and B antigen, and DRB1 allele matched with the recipient. Each unit must be at least 3/6 HLA-A, B DRB1 antigen matched to each other.

You may not qualify if:

  • Patient with suitable related donor
  • AML, ALL, AUL, biphenotypic leukemia beyond CR2
  • AML evolved from myelofibrosis
  • Any acute leukemia with:
  • Morphologic relapse or persistent disease in the BM
  • Active extra-medullary leukemia including active CNS leukemia
  • Requiring greater than two cycles of chemotherapy to obtain present remission status
  • Bone marrow aplasia (defined as BM cellularity \< 5% at transplant work-up)
  • MDS with 10% or greater bone marrow blasts at pre-transplant workup
  • Prior autologous or allogeneic HSC transplant at any time
  • Prior radiation therapy rendering patient ineligible for TBI
  • Any uncontrolled infection at time of study enrollment
  • Seropositive or NAT positive for HIV or HTLV1
  • Females who are pregnant or breast feeding
  • Patient unable to give informed consent or unable to comply with the treatment protocol including appropriate supportive care, follow-up, and research tests

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (10)

City of Hope

Duarte, California, 91010, United States

Location

University of California at Los Angeles

Los Angeles, California, 90095, United States

Location

H. Lee Moffitt Cancer Center and Research Institute

Tampa, Florida, 33612, United States

Location

Blood and Marrow Transplant Program at Northside Hospital

Atlanta, Georgia, 30342, United States

Location

Memorial Sloan Kettering Cancer Center

New York, New York, 10065, United States

Location

Duke University Medical Center

Durham, North Carolina, 27710, United States

Location

Case Western Reserve University

Cleveland, Ohio, 44106, United States

Location

Ohio State University Medical Center

Columbus, Ohio, 43210, United States

Location

University of Oklahoma

Oklahoma City, Oklahoma, 73104, United States

Location

University of Wisconsin-Madison

Madison, Wisconsin, 53792, United States

Location

MeSH Terms

Conditions

Hematologic NeoplasmsLeukemiaMyelodysplastic Syndromes

Interventions

Cord Blood Stem Cell Transplantation

Condition Hierarchy (Ancestors)

Neoplasms by SiteNeoplasmsHematologic DiseasesHemic and Lymphatic DiseasesNeoplasms by Histologic TypeBone Marrow Diseases

Intervention Hierarchy (Ancestors)

Stem Cell TransplantationCell TransplantationCell- and Tissue-Based TherapyBiological TherapyTherapeuticsTransplantationSurgical Procedures, Operative

Study Officials

  • Juliet Barker, MBBS

    Memorial Sloan Kettering Cancer Center

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
NETWORK
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 8, 2007

First Posted

August 10, 2007

Study Start

August 1, 2007

Primary Completion

August 1, 2013

Study Completion

August 1, 2013

Last Updated

March 10, 2014

Record last verified: 2014-03

Locations