NCT00497796

Brief Summary

The purpose of this research study is to investigate whether or not oral maribavir is safe and effective compared to oral ganciclovir for preventing CMV disease when administered for up to 14 weeks in patients who have had a liver transplant.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
307

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Jul 2007

Geographic Reach
1 country

55 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

July 5, 2007

Completed
4 days until next milestone

First Posted

Study publicly available on registry

July 9, 2007

Completed
14 days until next milestone

Study Start

First participant enrolled

July 23, 2007

Completed
2.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 14, 2009

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

September 14, 2009

Completed
5.7 years until next milestone

Results Posted

Study results publicly available

June 4, 2015

Completed
Last Updated

June 11, 2021

Status Verified

June 1, 2021

Enrollment Period

2.1 years

First QC Date

July 5, 2007

Results QC Date

May 4, 2015

Last Update Submit

June 2, 2021

Conditions

Keywords

cytomegalovirusCMVprophylaxisliverliver transplant

Outcome Measures

Primary Outcomes (1)

  • Number of Participants With Endpoint Committee (EC)-Confirmed Cytomegalovirus (CMV) Disease Within 6 Months Post-Transplantation

    All investigator-determined (protocol-defined) cases of CMV disease (i.e., symptomatic CMV infection or CMV organ disease), were adjudicated by an independent, blinded EC. Symptomatic CMV infection was defined as: CMV infection detected by a positive result from a CMV laboratory assay from at least one central laboratory assay (pp65 antigenemia or CMV DNA polymerase chain reaction \[PCR\] assay in plasma) and fever \>/=38 °C on \>/=2 occasions \>/=24 hours apart within a 7-day period and at least one of the following: new or increased malaise, two successive measurements of leucopenia (white blood cell \[WBC\] count \<3500/mm3 or a WBC count decrease of 20% if the cell count prior to onset of clinical symptoms was \>4000/mm3) \>/=24 hours apart, atypical lymphocytosis \>/=5%, and thrombocytopenia. CMV organ disease was defined as described by Ljungman et al., 2002.

    6 months post-transplant

Secondary Outcomes (12)

  • Number of Participants With CMV Infection or EC-confirmed CMV Disease Within 6 Months Post-Transplantation

    6 months post-transplant

  • Time to Onset of CMV Infection or EC-confirmed CMV Disease Within 6 Months Post-Transplantation

    6 months post-transplant

  • Number of Participants With Investigator-determined CMV Disease

    Through 6 months post-transplant (Day 1 to 100 days and 6 months post-transplant)

  • Number of Participants With EC-confirmed CMV Disease Within 100 Days Post-Transplantation

    100 days post-transplant

  • Number of Participants With CMV Infection or EC-confirmed CMV Disease Within 100 Days Post-Transplantation

    100 days post-transplant

  • +7 more secondary outcomes

Study Arms (2)

1

EXPERIMENTAL
Drug: maribavir

2

ACTIVE COMPARATOR
Drug: ganciclovir

Interventions

100mg twice a day for 14 weeks.

1

1000mg three times per day for 14 weeks.

2

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Orthotopic liver transplant recipient
  • Donor CMV seropositive / Recipient CMV seronegative
  • Enrolled within 10 days after liver transplant
  • Able to swallow tablets

You may not qualify if:

  • Multiple organ transplant
  • HIV infection
  • CMV disease
  • Use of other anti-CMV therapy at time of enrollment

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (55)

Mayo Clinic Arizona

Phoenix, Arizona, 85006, United States

Location

University of California at San Diego

La Jolla, California, 92103, United States

Location

Cedars-Sinai Medical Center

Los Angeles, California, 90048, United States

Location

UCLA Medical Center

Los Angeles, California, 90095, United States

Location

University of California at San Francisco

San Francisco, California, 94143, United States

Location

Stanford University Medical Center

Stanford, California, 94305, United States

Location

University of Colorado Health Sciences Center

Aurora, Colorado, 80045, United States

Location

Georgetown University

Washington D.C., District of Columbia, 20007, United States

Location

Mayo Clinic College of Medicine

Jacksonville, Florida, 32224, United States

Location

Tampa General

Tampa, Florida, 33606, United States

Location

Emory University

Atlanta, Georgia, 30322, United States

Location

Northwestern University Medical Center

Chicago, Illinois, 60611, United States

Location

Rush University Medical Center

Chicago, Illinois, 60612, United States

Location

University of Illinois at Chicago

Chicago, Illinois, 60612, United States

Location

University of Chicago Medical Center

Chicago, Illinois, 60637, United States

Location

University of Iowa Hospitals and Clinics

Iowa City, Iowa, 52242, United States

Location

University of Kansas Medical Center

Kansas City, Kansas, 66160, United States

Location

University of Kentucky Chandler Medical Center

Lexington, Kentucky, 40536, United States

Location

Jewish Hospital Louisville

Louisville, Kentucky, 40202, United States

Location

Tulane University Hospital and Clinic

New Orleans, Louisiana, 70112, United States

Location

Ochsner Clinic

New Orleans, Louisiana, 70121, United States

Location

New England Medical Center

Boston, Massachusetts, 02111, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02114, United States

Location

Beth Israel Deaconess Medical Center

Boston, Massachusetts, 02215, United States

Location

Lahey Clinic

Burlington, Massachusetts, 01805, United States

Location

University of Michigan

Ann Arbor, Michigan, 48109, United States

Location

Henry Ford Health System

Detroit, Michigan, 48202, United States

Location

University of Minnesota

Minneapolis, Minnesota, 55455, United States

Location

Mayo Clinic Rochester

Rochester, Minnesota, 55905, United States

Location

Washington University School of Medicine

St Louis, Missouri, 63110, United States

Location

University of Nebraska

Omaha, Nebraska, 68198, United States

Location

University of Medicine and Dentistry of New Jersey

Newark, New Jersey, 07101, United States

Location

NYU School of Medicine

New York, New York, 10016, United States

Location

Columbia University Medical Center

New York, New York, 10032, United States

Location

University of Rochester Medical Center- Strong Memorial

Rochester, New York, 14642, United States

Location

New York Medical College

Valhalla, New York, 10595, United States

Location

University of North Carolina, Chapel Hill

Chapel Hill, North Carolina, 27599, United States

Location

Duke University Medical Center

Durham, North Carolina, 27710, United States

Location

University of Cincinnati Medical Center

Cincinnati, Ohio, 45267, United States

Location

Cleveland Clinic Foundation

Cleveland, Ohio, 44195, United States

Location

Integris Baptist Medical Center

Oklahoma City, Oklahoma, 73112, United States

Location

Oregon Health and Sciences University

Portland, Oregon, 97239, United States

Location

University of Pennsylvania Hospital

Philadelphia, Pennsylvania, 19104, United States

Location

VA Pittsburgh Healthcare System

Pittsburgh, Pennsylvania, 15240, United States

Location

Medical University of South Carolina

Charleston, South Carolina, 29425, United States

Location

Methodist Transplant Institute

Memphis, Tennessee, 38104, United States

Location

Baylor University Medical Center (Dallas)

Dallas, Texas, 75246, United States

Location

Baylor College of Medicine (Houston)

Houston, Texas, 77030, United States

Location

Methodist Hospital

Houston, Texas, 77030, United States

Location

UT Memorial Hermann Hospital and Texas Liver Center

Houston, Texas, 77030, United States

Location

University of Texas Health Sciences Center at San Antonio

San Antonio, Texas, 78229, United States

Location

University of Virginia Health System

Charlottesville, Virginia, 22908, United States

Location

Virginia Commonwealth University

Richmond, Virginia, 23298, United States

Location

Univeristy of Washington Medical Center

Seattle, Washington, 98195-7110, United States

Location

Medical College of Wisconsin

Milwaukee, Wisconsin, 53226, United States

Location

Related Publications (2)

  • Vernooij RW, Michael M, Colombijn JM, Owers DS, Webster AC, Strippoli GF, Hodson EM. Pre-emptive treatment for cytomegalovirus viraemia to prevent cytomegalovirus disease in solid organ transplant recipients. Cochrane Database Syst Rev. 2025 Jan 14;1(1):CD005133. doi: 10.1002/14651858.CD005133.pub4.

  • Vernooij RW, Michael M, Ladhani M, Webster AC, Strippoli GF, Craig JC, Hodson EM. Antiviral medications for preventing cytomegalovirus disease in solid organ transplant recipients. Cochrane Database Syst Rev. 2024 May 3;5(5):CD003774. doi: 10.1002/14651858.CD003774.pub5.

MeSH Terms

Conditions

Cytomegalovirus Infections

Interventions

maribavirGanciclovir

Condition Hierarchy (Ancestors)

Herpesviridae InfectionsDNA Virus InfectionsVirus DiseasesInfections

Intervention Hierarchy (Ancestors)

AcyclovirGuanineHypoxanthinesPurinonesPurinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic Compounds

Results Point of Contact

Title
Study Director
Organization
Shire

Study Officials

  • Study Director

    Takeda

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
PREVENTION
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 5, 2007

First Posted

July 9, 2007

Study Start

July 23, 2007

Primary Completion

September 14, 2009

Study Completion

September 14, 2009

Last Updated

June 11, 2021

Results First Posted

June 4, 2015

Record last verified: 2021-06

Locations