NCT00468728

Brief Summary

This is a comparative study to investigate the safety and efficacy of PAR-101/OPT-80 (fidaxomicin) versus vancomycin in subjects with Clostridium difficile-associated diarrhea (CDAD).

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
535

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Oct 2006

Typical duration for phase_3

Geographic Reach
9 countries

116 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

October 4, 2006

Completed
7 months until next milestone

First Submitted

Initial submission to the registry

May 1, 2007

Completed
2 days until next milestone

First Posted

Study publicly available on registry

May 3, 2007

Completed
2.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 11, 2009

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 11, 2009

Completed
1.6 years until next milestone

Results Posted

Study results publicly available

July 29, 2011

Completed
Last Updated

April 21, 2017

Status Verified

March 1, 2017

Enrollment Period

3.2 years

First QC Date

May 1, 2007

Results QC Date

July 1, 2011

Last Update Submit

March 23, 2017

Conditions

Keywords

CDAD, Clostridium difficile, diarrheaClostridium difficile-Associated Diarrhea

Outcome Measures

Primary Outcomes (1)

  • Cure Rate at End of Therapy

    Percentage of subjects with 3 or fewer unformed stools for 2 consecutive days and maintained through the end of therapy, and the subject no longer needed specific anti-Clostridium antibacterial treatment after completion of the course of study medication.

    Study day 10 (+/- 2 days)

Secondary Outcomes (2)

  • Recurrence

    Study days 11-40

  • Global Cure

    End of Study

Study Arms (2)

1

ACTIVE COMPARATOR

Vancomycin

Drug: Vancomycin

2

EXPERIMENTAL

PAR-101/OPT-80

Drug: PAR-101/OPT-80

Interventions

capsules

2

Capsules

1

Eligibility Criteria

Age16 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Males/females with CDAD
  • Females must use adequate contraception
  • Signed informed consent

You may not qualify if:

  • Life-threatening CDAD
  • Toxic megacolon
  • Pregnant
  • Concurrent use of diarrheal agents
  • Participation in other trials

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (116)

Unknown Facility

Gadsden, Alabama, United States

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Phoenix, Arizona, United States

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Hot Springs, Arkansas, United States

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La Mesa, California, United States

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Modesto, California, United States

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Palm Springs, California, United States

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Rancho Mirage, California, United States

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San Jose, California, United States

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Santa Ana, California, United States

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Vallejo, California, United States

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Washington D.C., District of Columbia, United States

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Miami, Florida, United States

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Port Orange, Florida, United States

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Sarasota, Florida, United States

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Marietta, Georgia, United States

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Savannah, Georgia, United States

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Idaho Falls, Idaho, United States

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Chicago, Illinois, United States

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Maywood, Illinois, United States

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Indianapolis, Indiana, United States

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Bowling Green, Kentucky, United States

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Jena, Louisiana, United States

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New Orleans, Louisiana, United States

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Baltimore, Maryland, United States

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Boston, Massachusetts, United States

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West Roxbury, Massachusetts, United States

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Detroit, Michigan, United States

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Keego Harbor, Michigan, United States

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Royal Oak, Michigan, United States

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Minneapolis, Minnesota, United States

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Tupelo, Mississippi, United States

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Columbia, Missouri, United States

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Butte, Montana, United States

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Cedar Knolls, New Jersey, United States

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Neptune City, New Jersey, United States

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The Bronx, New York, United States

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Charlotte, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Fargo, North Dakota, United States

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Akron, Ohio, United States

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Amherst, Ohio, United States

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Cleveland, Ohio, United States

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Columbus, Ohio, United States

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Dayton, Ohio, United States

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Philadelphia, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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Charleston, South Carolina, United States

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Rapid City, South Dakota, United States

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Sioux Falls, South Dakota, United States

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San Antonio, Texas, United States

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Winchester, Virginia, United States

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Seattle, Washington, United States

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Charleston, West Virginia, United States

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Aalst, Belgium

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Alast, Belgium

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Antwerp, Belgium

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Brussels, Belgium

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Columbia, Belgium

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Ghent, Belgium

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Kortrijk, Belgium

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Liège, Belgium

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Mons, Belgium

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Montigny-le-Tilleul, Belgium

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Wilrijk, Belgium

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Calgary, Alberta, Canada

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Edmonton, Alberta, Canada

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Hamilton, Ontario, Canada

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Toronto, Ontario, Canada

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Chicoutimi, Quebec, Canada

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Montreal, Quebec, Canada

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Saint-Jérôme, Quebec, Canada

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Sherbrooke, Quebec, Canada

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Trois-Rivières, Quebec, Canada

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Amiens, France

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Caen, France

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Clichy, France

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Garches, France

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Grenoble, France

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Lille, France

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Tourcoing, France

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Tours, France

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Valenciennes, France

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Cologne, Germany

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Düsseldorf, Germany

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Frankfurt, Germany

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Hanover, Germany

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Hofheim am Taunus, Germany

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Lübeck, Germany

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Magdeburg, Germany

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Regensburg, Germany

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Busto Arsizio, Italy

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Genova, Italy

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Milan, Italy

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Modena, Italy

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Torino, Italy

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Badalona, Spain

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Barcelona, Spain

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Madrid, Spain

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Palma de Mallorca, Spain

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Seville, Spain

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Eskilstuna, Sweden

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Gothenburg, Sweden

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Örebro, Sweden

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Great Yarmouth, Norfolk, United Kingdom

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Derriford, Plymouth, United Kingdom

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Barnsley, United Kingdom

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Brighton, United Kingdom

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Cambridge, United Kingdom

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Edinburgh, United Kingdom

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Liege, United Kingdom

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London, United Kingdom

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Nottingham, United Kingdom

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Oxford, United Kingdom

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Oxon, United Kingdom

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Surrey, United Kingdom

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York, United Kingdom

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Related Publications (5)

  • Cornely OA, Crook DW, Esposito R, Poirier A, Somero MS, Weiss K, Sears P, Gorbach S; OPT-80-004 Clinical Study Group. Fidaxomicin versus vancomycin for infection with Clostridium difficile in Europe, Canada, and the USA: a double-blind, non-inferiority, randomised controlled trial. Lancet Infect Dis. 2012 Apr;12(4):281-9. doi: 10.1016/S1473-3099(11)70374-7. Epub 2012 Feb 8.

  • D'Agostino RB Sr, Collins SH, Pencina KM, Kean Y, Gorbach S. Risk estimation for recurrent Clostridium difficile infection based on clinical factors. Clin Infect Dis. 2014 May;58(10):1386-93. doi: 10.1093/cid/ciu107. Epub 2014 Mar 5.

  • Cornely OA, Miller MA, Fantin B, Mullane K, Kean Y, Gorbach S. Resolution of Clostridium difficile-associated diarrhea in patients with cancer treated with fidaxomicin or vancomycin. J Clin Oncol. 2013 Jul 1;31(19):2493-9. doi: 10.1200/JCO.2012.45.5899. Epub 2013 May 28.

  • Cornely OA, Miller MA, Louie TJ, Crook DW, Gorbach SL. Treatment of first recurrence of Clostridium difficile infection: fidaxomicin versus vancomycin. Clin Infect Dis. 2012 Aug;55 Suppl 2(Suppl 2):S154-61. doi: 10.1093/cid/cis462.

  • Figueroa I, Johnson S, Sambol SP, Goldstein EJ, Citron DM, Gerding DN. Relapse versus reinfection: recurrent Clostridium difficile infection following treatment with fidaxomicin or vancomycin. Clin Infect Dis. 2012 Aug;55 Suppl 2(Suppl 2):S104-9. doi: 10.1093/cid/cis357.

MeSH Terms

Conditions

Clostridium InfectionsDiarrhea

Interventions

Vancomycin

Condition Hierarchy (Ancestors)

Gram-Positive Bacterial InfectionsBacterial InfectionsBacterial Infections and MycosesInfectionsSigns and Symptoms, DigestiveSigns and SymptomsPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

GlycopeptidesGlycoconjugatesCarbohydratesPeptidesAmino Acids, Peptides, and Proteins

Results Point of Contact

Title
Chief Scientific Officer
Organization
Optimer Pharmaceuticals, Inc.

Study Officials

  • Dr. Sherwood Gorbach, MD

    Optimer Pharmaceuticals, Inc.

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
LTE60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 1, 2007

First Posted

May 3, 2007

Study Start

October 4, 2006

Primary Completion

December 11, 2009

Study Completion

December 11, 2009

Last Updated

April 21, 2017

Results First Posted

July 29, 2011

Record last verified: 2017-03

Data Sharing

IPD Sharing
Will share

http://www.merck.com/clinical-trials/pdf/Merck%20Procedure%20on%20Clinical%20Trial%20Data%20Access%20Final\_Updated%20July\_9\_2014.pdf http://engagezone.msd.com/ds\_documentation.php

Locations