NCT00454246

Brief Summary

This study will assess the efficacy and safety of methoxy polyethylene glycol-epoetin beta (Mircera) in the maintenance of hemoglobin levels in patients who have previously received treatment with epoetin alfa or darbepoetin alfa, and who are transitioning from chronic kidney disease stage 4 through dialysis. Patients will be randomized either to receive Mircera or to remain on their existing therapy; the initial monthly dose of subcutaneous (sc) Mircera (120-360 micrograms) will be based on the average weekly dose of epoetin alfa or darbepoetin alfa administered in the week preceding the switch to Mircera. At the initiation of dialysis, patients in the Mircera group will receive monthly intravenous (iv) Mircera at a starting dose based on their previous (sc) dose, and those in the control group will receive weekly (iv) epoetin alfa. The anticipated time on study treatment is 1-2 years, and the target sample size is 500+ individuals.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
111

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Apr 2007

Shorter than P25 for phase_3

Geographic Reach
1 country

78 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 29, 2007

Completed
1 day until next milestone

First Posted

Study publicly available on registry

March 30, 2007

Completed
2 days until next milestone

Study Start

First participant enrolled

April 1, 2007

Completed
10 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 1, 2008

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 1, 2008

Completed
3.9 years until next milestone

Results Posted

Study results publicly available

December 16, 2011

Completed
Last Updated

December 16, 2011

Status Verified

November 1, 2011

Enrollment Period

10 months

First QC Date

March 29, 2007

Results QC Date

March 29, 2011

Last Update Submit

November 14, 2011

Conditions

Outcome Measures

Primary Outcomes (1)

  • Percentage of Patients Able to Maintain Hemoglobin (Hb) Within 10-12 g/dL

    Efficacy analyses were not performed.

    6-7 months post initiation of dialysis

Secondary Outcomes (2)

  • Dose Adjustments

    5 months post-randomization through onset of dialysis, and post-dialysis initiation through study end.

  • Number of Participants Assessed for AEs and SAEs

    First dose of medication through 15 days post last dose (up to 8 months)

Study Arms (3)

methoxy polyethylene glycol-epoetin beta

EXPERIMENTAL

120-360 micrograms methoxy polyethylene glycol-epoetin beta subcutaneous (sc) monthly starting dose, for a minimum of 5 months to a maximum of 18 months. Dosage was adjusted to maintain a hemoglobin target range of ≥10 g/dL to ≤12 g/dL.

Drug: methoxy polyethylene glycol-epoetin beta

Epoetin alfa

ACTIVE COMPARATOR

Patients randomized to the reference arm continued to receive their standard of care dose and regimen of epoetin alfa subcutaneous once per week for a minimum of 5 months to a maximum of 18 months. Subcutaneous injections were to be administered in the same part of the body (ie, thigh, abdomen or arm) throughout the study. Dosage was adjusted to maintain a hemoglobin target range of ≥10 g/dL to ≤12 g/dL.

Drug: epoetin alfa

Darbepoetin alfa

ACTIVE COMPARATOR

Patients randomized to the reference arm continued to receive their standard of care dose and regimen of darbepoetin subcutaneous once every two weeks for a minimum of 5 months and a maximum of 18 months. Subcutaneous injections were to be administered in the same part of the body (ie, thigh, abdomen or arm) throughout the study. Dosage was adjusted to maintain a hemoglobin target range of ≥10 g/dL to ≤12 g/dL.

Drug: darbepoetin alfa

Interventions

Methoxy polyethylene glycol-epoetin beta was provided as a sterile single-use injectable solution in a 1-mL prefilled syringe containing 0.3 mL or 0.6 mL solution. The methoxy polyethylene glycol-epoetin beta injectable solution was formulated in sodium phosphate, sodium sulfate, mannitol, methionine and poloxamer 188, pH 6.2 and did not contain any preservative. Participants received methoxy polyethylene glycol-epoetin beta subcutaneous once a month.

Also known as: Mircera
methoxy polyethylene glycol-epoetin beta

Standard of care as prescribed, per individual participant, subcutaneous once per week. Subcutaneous injections were to be administered in the same part of the body (ie, thigh, abdomen or arm) throughout the study.

Epoetin alfa

Standard of care as prescribed, per individual participant, darbepoetin alfa subcutaneous once every two weeks. Subcutaneous injections were to be administered in the same part of the body (ie, thigh,abdomen or arm) throughout the study.

Darbepoetin alfa

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • adult patients, \>=18 years of age;
  • chronic kidney disease stage IV not requiring dialysis;
  • expected to initiate dialysis within 18 months;
  • \<=Glomerular Filtration Rate (GFR)\<=29.

You may not qualify if:

  • failing renal allograft in place;
  • acute or chronic bleeding within 8 weeks prior to screening;
  • transfusion of red blood cells within 8 weeks prior to screening;
  • poorly controlled hypertension;
  • immunosuppressive therapy in the 12 weeks prior to screening.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (78)

Unknown Facility

Birmingham, Alabama, United States

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Mobile, Alabama, United States

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Phoenix, Arizona, United States

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El Dorado, Arkansas, United States

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Hot Springs, Arkansas, United States

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Bakersfield, California, United States

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Glendale, California, United States

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Granada Hills, California, 91344, United States

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Los Angeles, California, United States

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Orange, California, United States

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Palm Springs, California, United States

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Riverside, California, United States

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San Diego, California, United States

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Yuba City, California, United States

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Colorado Springs, Colorado, United States

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Lakewood, Colorado, United States

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Stamford, Connecticut, United States

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Miami, Florida, United States

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Ocala, Florida, United States

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Orlando, Florida, United States

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Palm Beach Gardens, Florida, United States

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Pembroke Pines, Florida, United States

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Tampa, Florida, United States

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Atlanta, Georgia, United States

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Augusta, Georgia, United States

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Macon, Georgia, United States

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Meridan, Idaho, 83642, United States

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Evergreen Park, Illinois, United States

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Fort Wayne, Indiana, United States

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Wichita, Kansas, United States

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Baton Rouge, Louisiana, United States

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Shreveport, Louisiana, United States

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Germantown, Maryland, United States

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Boston, Massachusetts, United States

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Springfield, Massachusetts, United States

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Detroit, Michigan, United States

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Milwaukee, Michigan, United States

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Royal Oak, Michigan, United States

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Columbus, Mississippi, United States

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St Louis, Missouri, United States

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Omaha, Nebraska, United States

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Voorhees Township, New Jersey, United States

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West Orange, New Jersey, 07052, United States

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Brooklyn, New York, United States

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Buffalo, New York, United States

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Flushing, New York, United States

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Great Neck, New York, United States

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Mineola, New York, United States

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Springfield Gardens, New York, United States

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Syracuse, New York, United States

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The Bronx, New York, United States

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Durham, North Carolina, United States

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Greenville, North Carolina, United States

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Raleigh, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Maimisburg, Ohio, United States

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Toledo, Ohio, United States

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Portland, Oregon, United States

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Erie, Pennsylvania, United States

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Lewistown, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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Providence, Rhode Island, United States

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Columbia, South Carolina, United States

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Greenville, South Carolina, United States

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Orangeburg, South Carolina, United States

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Chattanooga, Tennessee, United States

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Dyersburg, Tennessee, United States

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Houston, Texas, 77024, United States

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San Antonio, Texas, United States

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Temple, Texas, United States

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Alexandria, Virginia, United States

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Fairfax, Virginia, United States

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Richmond, Virginia, United States

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Salem, Virginia, United States

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Bluefield, West Virginia, United States

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Morgantown, West Virginia, United States

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Appleton, Wisconsin, United States

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MeSH Terms

Conditions

Anemia

Interventions

continuous erythropoietin receptor activatorEpoetin AlfaDarbepoetin alfa

Condition Hierarchy (Ancestors)

Hematologic DiseasesHemic and Lymphatic Diseases

Intervention Hierarchy (Ancestors)

ErythropoietinColony-Stimulating FactorsGlycoproteinsGlycoconjugatesCarbohydratesHematopoietic Cell Growth FactorsCytokinesIntercellular Signaling Peptides and ProteinsPeptidesAmino Acids, Peptides, and ProteinsProteinsBiological Factors

Results Point of Contact

Title
Medical Communications
Organization
Hoffman-LaRoche

Study Officials

  • Clinical Trials

    Hoffmann-La Roche

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 29, 2007

First Posted

March 30, 2007

Study Start

April 1, 2007

Primary Completion

February 1, 2008

Study Completion

February 1, 2008

Last Updated

December 16, 2011

Results First Posted

December 16, 2011

Record last verified: 2011-11

Locations