NCT00445172

Brief Summary

The purpose of this study is to investigate the safety and efficacy of long-term E0302 administration in patients with Amyotrophic Lateral Sclerosis (ALS).

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
135

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Feb 2008

Longer than P75 for phase_2

Geographic Reach
1 country

42 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 6, 2007

Completed
2 days until next milestone

First Posted

Study publicly available on registry

March 8, 2007

Completed
11 months until next milestone

Study Start

First participant enrolled

February 1, 2008

Completed
9.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 31, 2017

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 31, 2017

Completed
Last Updated

June 18, 2023

Status Verified

August 1, 2017

Enrollment Period

9.2 years

First QC Date

March 6, 2007

Last Update Submit

June 16, 2023

Conditions

Keywords

Amyotrophic Lateral SclerosisMotor NeuronsMuscular Atrophy

Outcome Measures

Primary Outcomes (1)

  • Number of participants with Adverse Events as a Measure of safety

    Every 3 months

Secondary Outcomes (3)

  • Survival rate

    Every 3 months

  • Functional rating scale

    Every 3 months

  • Percent-predicted forced vital capacity (%FVC.)

    Every 3 months

Study Arms (1)

1

EXPERIMENTAL
Drug: E0302 (mecobalamin)

Interventions

Intramuscular injection, mecobalamin twice a week.

1

Eligibility Criteria

Age20 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients who have completed Phase II/III study of E0302 (E0302-J081-761, hereafter referred to as Study 761) except for those patients who discontinued the treatment of Study 761. Completed patients are defined as those who completed the treatment period of Study 761, those on 24-hour use of non-invasive positive pressure ventilation (NIPPV), or those who eventually resulted in the use of NIPPV.
  • Patients who are able to submit written informed consent. If patients are duly capable of study consent but are unable to sign (or affix a seal) by themselves due to aggravation of disease condition, written informed consent can be obtained from a legally authorized representative who can sign on behalf of the patients after confirming the patients' agreement to study participation.

You may not qualify if:

  • Patients with cognitive impairment.
  • Pregnant women or women who may have a possibility of becoming pregnant.
  • Patients or their partners who are not willing to use reliable contraception.
  • Patients with severe disease in the renal, cardiovascular, hematological, or hepatic system (severe disease will be judged referring to "Ministry of Health, Labor and Welfare (MHLW) Drug Safety Dept. Notification No. 80, Drug Safety Classification Criteria for Severity of Adverse Drug Reaction by Medicinal Products, Grade 3." However, an event due to the primary disease will be precluded).
  • Patients with malignant tumor.
  • Patients who participated in another clinical study after the completion of Study 761.
  • Patients with present illness or history of drug allergy or severe allergic disease (anaphylactic shock).
  • Patients who are judged to be ineligible for study entry by the investigator or subinvestigator.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (42)

Unknown Facility

Nagoya, Aichi-ken, Japan

Location

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Aomori, Aomori, Japan

Location

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Chiba, Chiba, Japan

Location

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Touon-shi, Ehime, Japan

Location

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Fukuoka, Fukuoka, Japan

Location

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Kitakyushi-shi, Fukuoka, Japan

Location

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Fukushima, Fukushima, Japan

Location

Unknown Facility

Maebashi, Gunma, Japan

Location

Unknown Facility

Higashihiroshima-shi, Hiroshima, Japan

Location

Unknown Facility

Miyoshi-shi, Hiroshima, Japan

Location

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Otake-shi, Hiroshima, Japan

Location

Unknown Facility

Sapporo, Hokkaido, Japan

Location

Unknown Facility

Kanazawa, Ishikawa-ken, Japan

Location

Unknown Facility

Ichinoseki-shi, Iwate, Japan

Location

Unknown Facility

Sagamihara-shi, Kanagawa, Japan

Location

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Yokohama, Kanagawa, Japan

Location

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Nangoku-shi, Kochi, Japan

Location

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Kyoto, Kyoto, Japan

Location

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Tsu, Mie-ken, Japan

Location

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Sendai, Miyagi, Japan

Location

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Watari-gun, Miyagi, Japan

Location

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Nagano, Nagano, Japan

Location

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Higashisonogi-gun, Nagasaki, Japan

Location

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Kashiwazaki-shi, Niigata, Japan

Location

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Niigata, Niigata, Japan

Location

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Tsukubo-gun, Okayama-ken, Japan

Location

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Ginowan-shi, Okinawa, Japan

Location

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Toyonaka-shi, Osaka, Japan

Location

Unknown Facility

Hasuda-shi, Saitama, Japan

Location

Unknown Facility

Saitama-shi, Saitama, Japan

Location

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Hamamatsu, Shizuoka, Japan

Location

Unknown Facility

Shizuoka, Shizuoka, Japan

Location

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Shimotsuke-shi, Tochigi, Japan

Location

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Tokushima, Tokushima, Japan

Location

Unknown Facility

Yoshinogawa-shi, Tokushima, Japan

Location

Unknown Facility

Bunkyo-ku, Tokyo, Japan

Location

Unknown Facility

Kodaira-shi, Tokyo, Japan

Location

Unknown Facility

Ōta-ku, Tokyo, Japan

Location

Unknown Facility

Wakayama, Wakayama, Japan

Location

Unknown Facility

Yonezawa-shi, Yamagata, Japan

Location

Unknown Facility

Shimonoseki-shi, Yamaguchi, Japan

Location

Unknown Facility

Yanai-shi, Yamaguchi, Japan

Location

MeSH Terms

Conditions

Amyotrophic Lateral SclerosisMuscular Atrophy

Interventions

mecobalamin

Condition Hierarchy (Ancestors)

Spinal Cord DiseasesCentral Nervous System DiseasesNervous System DiseasesMotor Neuron DiseaseNeurodegenerative DiseasesTDP-43 ProteinopathiesNeuromuscular DiseasesProteostasis DeficienciesMetabolic DiseasesNutritional and Metabolic DiseasesNeuromuscular ManifestationsNeurologic ManifestationsAtrophyPathological Conditions, AnatomicalPathological Conditions, Signs and SymptomsSigns and Symptoms

Study Officials

  • Kazunori Saeki

    Neuroscience Clinical Development Section. JAC PCU. Eisai Co., Ltd.

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 6, 2007

First Posted

March 8, 2007

Study Start

February 1, 2008

Primary Completion

March 31, 2017

Study Completion

March 31, 2017

Last Updated

June 18, 2023

Record last verified: 2017-08

Locations