NCT00385697

Brief Summary

The primary purpose of this protocol is to assess the efficacy, tolerability, and safety of MGA031 when administered according to 3 different MGA031 dosing regimens in children and adults with recent-onset (diagnosis within past 12 weeks) type 1 diabetes mellitus. All regimens will be administered as an addition to insulin and other standard of care treatments. Efficacy will be defined primarily by the capacity of MGA031 to markedly reduce typical insulin requirements while maintaining relatively normal blood sugar levels. Other studies involving the study drug use the name hOKT3γ1 (Ala-Ala). MGA031, a humanized monoclonal antibody, is the name used for hOKT3γ1 (Ala-Ala) that is produced by MacroGenics, Inc. The United States Adopted Name (USAN) for MGA031 is teplizumab.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
554

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Oct 2006

Longer than P75 for phase_2

Geographic Reach
15 countries

110 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

October 1, 2006

Completed
6 days until next milestone

First Submitted

Initial submission to the registry

October 7, 2006

Completed
4 days until next milestone

First Posted

Study publicly available on registry

October 11, 2006

Completed
3.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2010

Completed
1.2 years until next milestone

Study Completion

Last participant's last visit for all outcomes

August 1, 2011

Completed
12.4 years until next milestone

Results Posted

Study results publicly available

December 5, 2023

Completed
Last Updated

December 5, 2023

Status Verified

November 1, 2023

Enrollment Period

3.7 years

First QC Date

October 7, 2006

Results QC Date

February 23, 2023

Last Update Submit

November 30, 2023

Conditions

Keywords

RandomizedDouble BlindParallel GroupControlled Clinical Trial

Outcome Measures

Primary Outcomes (4)

  • Number of Subjects in Segment 2 With Both a Total Daily Insulin Dose of Less Than 0.5 U/kg/Day and Hemoglobin A1c (HbA1c) Level of Less Than 6.5%.

    This is a composite endpoint is based on the proportion of subjects who have both a total daily insulin dose \<0.5 U/Kg/day and an HbAlc level 6.5% at 52 weeks after randomization.

    52 weeks after randomization

  • Number of Subjects in Segment 1 With Both a Total Daily Insulin Dose of Less Than 0.5 U/kg/Day and Hemoglobin A1c (HbA1c) Level of Less Than 6.5%.

    This is a composite endpoint based on the proportion of subjects who have both a total daily insulin dose \<0.5 U/Kg/day and an HbAlc level 6.5%

    52 weeks after first dose

  • Mean HbA1c Change From Baseline in Segment 2

    Comparison among study treatments of average change from baseline HbA1C. This endpoint will be assessed in a hierarchical manner only if the composite primary endpoint shows a statistically significant difference between arms

    52 weeks after randomization

  • Mean HbA1c Change From Baseline in Segment 1

    The average change in HbA1c levels after dosing.

    52 weeks after first dose

Secondary Outcomes (8)

  • Change From Baseline in C-peptide Area Under the Curve (AUC) in Segment 2

    104 weeks after randomization

  • Change From Baseline in C-peptide AUC in Segment 1

    104 weeks after first dose

  • Number of Subjects in Segment 2 With Both a Total Daily Insulin Dose of Less Than 0.5 U/kg/Day and HbA1c Level of Less Than 6.5%

    104 weeks after randomization

  • Number of Subjects in Segment 1 With Both a Total Daily Insulin Dose of Less Than 0.5 U/kg/Day and HbA1c Level of Less Than 6.5%

    104 weeks after first dose

  • Number of Subjects in Segment 2 With Both a Total Daily Insulin Dose of Less Than 0.5 U/kg/Day and HbA1c Level of Less Than 7.0%.

    at 52 weeks after randomization

  • +3 more secondary outcomes

Study Arms (5)

Double-blind Herold Regimen

EXPERIMENTAL

Full dose of teplizumab IV for 14 days, repeated at Week 26

Biological: Teplizumab

Double-blind 33.3% Herold Regimen

EXPERIMENTAL

One third full dose of teplizumab IV for 14 days, repeated at Week 26

Biological: Teplizumab

Double-blind Curtailed Herold Regimen

EXPERIMENTAL

Full dose of teplizumab IV for 6 days followed by placebo for 8 days, repeated at Week 26

Biological: Teplizumab

Double-blind Placebo

PLACEBO COMPARATOR

Placebo IV dosing daily for 14 days repeated at Week 26

Drug: Placebo

Open-label Herold Regimen

EXPERIMENTAL

Full dose of teplizumab IV for 14 days, repeated at Week 26

Biological: Teplizumab

Interventions

TeplizumabBIOLOGICAL

Daily IV dosing for 14 days, repeated at Week 26

Also known as: MGA031
Double-blind 33.3% Herold RegimenDouble-blind Curtailed Herold RegimenDouble-blind Herold RegimenOpen-label Herold Regimen

Daily IV dosing for 14 days, repeated at Week 26

Double-blind Placebo

Eligibility Criteria

Age8 Years - 35 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Subjects must meet all of the following criteria:
  • Enrollment (Segment #1) or randomization (Segment #2) on Study Day 0 within 12 weeks of first visit to any physician for symptoms or signs of diabetes. Study Day 0 is the first day of study drug dosing.
  • Diagnosis of type 1 diabetes mellitus, according to the American Diabetes Association (ADA) criteria
  • Requirement for injected insulin therapy
  • Have a detectable fasting or stimulated C-peptide level (above the lower limit of detection of the assay)
  • One positive result on testing for any of the following antibodies:
  • islet-cell autoantibodies (ICA512/IA-2),
  • glutamic acid decarboxylase autoantibodies, or
  • insulin autoantibodies (if present during first 2 weeks, but not beyond 2 weeks, of insulin treatment)
  • Male or female
  • Subject must be in one of the following age groups:
  • Age 18-35 years
  • Age 12-17 years pending approval by Data Monitoring Committee
  • Age 8-11 years pending approval by Data Monitoring Committee
  • Body weight ≥ 36 kg

You may not qualify if:

  • Subjects must have none of the following:
  • Prior administration of a monoclonal antibody -- within the 1 year before enrollment or randomization at Study Day 0 -- that could potentially prevent or confound a therapeutic response to MGA031
  • Participation in any type of therapeutic drug or vaccine clinical trial within the 12 weeks before enrollment or randomization
  • Any medical condition that, in the opinion of the investigator, would interfere with safe completion of the trial
  • Pregnant or lactating females
  • Prior murine OKT®3 treatment at any time before enrollment or randomization
  • Current or planned therapy with exenatide or any other agents that stimulate pancreatic beta cell regeneration or insulin secretion
  • Current or planned therapy with inhaled insulin
  • Uncompensated heart failure, fluid overload, myocardial infarction or evidence of ischemic heart disease, or other serious cardiac disease within the 12 weeks before enrollment or randomization
  • History of epilepsy, cancer, cystic fibrosis, sickle cell anemia, neuropathy, peripheral vascular disease or cerebrovascular disease
  • Newly diagnosed hypothyroidism (not currently being treated but which, in the opinion of the investigator, should be treated) or active Graves' disease
  • Eczema, asthma or severe atopic disease requiring treatment within the 12 weeks before enrollment or randomization
  • Evidence of active infection, such as fever ≥ 38.0 degrees Celsius (100.5 degrees Fahrenheit)
  • Known or suspected infection with human immunodeficiency virus (HIV)
  • Evidence of active hepatitis B (HBV) or hepatitis C virus (HCV)
  • +5 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (115)

UAB School of Medicine

Birmingham, Alabama, 35294, United States

Location

NEA Clinic

Jonesboro, Arkansas, 72401, United States

Location

Arkansas Children's Hospital

Little Rock, Arkansas, 72202, United States

Location

Diabetes Medical Center of California

Northridge, California, 91325, United States

Location

UCSF Medical Center

San Francisco, California, 94143, United States

Location

University of Colorado Health Sciences Center

Aurora, Colorado, 80045, United States

Location

Yale University

New Haven, Connecticut, 06519, United States

Location

Christiana Care Research Institute

Newark, Delaware, 19713, United States

Location

Richard Hays, MD

Wellington, Florida, 33414, United States

Location

Atlanta Diabetes Associates

Atlanta, Georgia, 30309, United States

Location

Humphrey Diabetes Center

Boise, Idaho, 87702, United States

Location

Rocky Mountain Diabetes & Osteoporosis Center

Idaho Falls, Idaho, 83404, United States

Location

Riley Hospital for Children

Indianapolis, Indiana, 46202, United States

Location

University of Iowa Children's Hospital

Iowa City, Iowa, 52242-1083, United States

Location

Mid-America Diabetes Associates, PA

Wichita, Kansas, 67211, United States

Location

Commonwealth Biomedical Research, LLC

Madisonville, Kentucky, 42431, United States

Location

St. Agnes Hospital

Baltimore, Maryland, 21229, United States

Location

Maryland Diabetes & Endocrine Associates

Rockville, Maryland, 20852, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02114, United States

Location

Baystate Medical Center

Springfield, Massachusetts, 01199, United States

Location

Alzohaili Medical Consultants

Dearborn, Michigan, 48126, United States

Location

The Children's Mercy Hospital

Kansas City, Missouri, 64108, United States

Location

Creighton Diabetes Center

Omaha, Nebraska, 68131, United States

Location

Saint Barnabas Medical Center

Livingston, New Jersey, 07039, United States

Location

University of Medicine & Dentistry of NJ

New Brunswick, New Jersey, 08901, United States

Location

Albany Medical Center

Albany, New York, 12208, United States

Location

Schneider Children's Hospital

New Hyde Park, New York, 11040, United States

Location

Joslin Diabetes Center

Syracuse, New York, 13214, United States

Location

Cleveland Clinic

Cleveland, Ohio, 44195, United States

Location

St. Mary Medical Center

Langhorne, Pennsylvania, 19047, United States

Location

Sumter Medical Specialists

Sumter, South Carolina, 29150, United States

Location

University Diabetes & Endocrine Consultants

Chattanooga, Tennessee, 37403, United States

Location

Methodist Healthcare

Memphis, Tennessee, 38104, United States

Location

Research Institute of Dallas

Dallas, Texas, 75231, United States

Location

Spectra Research Center

McAllen, Texas, 78503, United States

Location

Diabetes and Glandular Disease Research

San Antonio, Texas, 78229, United States

Location

Endocrine Research Specialists

Ogden, Utah, 84403, United States

Location

Pacific Northwest Research Institute

Seattle, Washington, 98122, United States

Location

Medical College of Wisconsin

Milwaukee, Wisconsin, 53226, United States

Location

Alberta Children's Hospital

Calgary, Alberta, T3B 6A8, Canada

Location

University of Manitoba

Winnipeg, Manitoba, R3E0Z2, Canada

Location

University Health Sciences Centre

St. John's, Newfoundland and Labrador, A1B3V6, Canada

Location

Capital District Health Authority

Halifax, Nova Scotia, B3H2YN, Canada

Location

Oxford AIM Clinic

London, Ontario, N6A 5R9, Canada

Location

Children's Hospital of Western

London, Ontario, N6A5W9, Canada

Location

FN Brno- Detska nemocnice

Brno, 62500, Czechia

Location

FN Hradec Kralove

Hradec Králové, 50005, Czechia

Location

Nemocnice Jihlava

Jihlava, 58633, Czechia

Location

FN Kralovske Vinohrady

Prague, 10034, Czechia

Location

Fakultni nemocnice v Motole

Prague, 150 06, Czechia

Location

Masarykova nemocnice v Usti nad Labem

Ústí nad Labem, 40113, Czechia

Location

Tartu University Hospital

Puusepa, Tartu, 51014, Estonia

Location

East Tallinn Central Hospital

Tallinn, Estonia

Location

Universitätsklinikum Heidelberg

Heidelberg, Baden-Wurttemberg, 69120, Germany

Location

Medizinische Universitätsklinik Ulm

Ulm, Baden-Wurttemberg, 89070, Germany

Location

Herz-und Diabetszentrum Nordrhein-Westfalen

Bad Oeynhausen, North Rhine-Westphalia, 32545, Germany

Location

Charité-Hochschulmedizin Berlin

Berlin, 12200, Germany

Location

Universitatsklinik Giessen

Giessen, 35392, Germany

Location

Nizam's Institute of Medical Sciences

Hyderabad, Andhra Pradesh, 500082, India

Location

King George Hospital

Visakhapatnam, Andhra Pradesh, 530002, India

Location

Gujarat Endocrine Centre

Ahmedabad, Gujarat, 380006, India

Location

DHL Research Centre

Ahmedabad, Gujarat, 380015, India

Location

Bharti Research Institute of Diabetes & Endocrinology

Karnāl, Haryana, 132001, India

Location

Bangalore Diabetes Centre

Bangalore, Karnataka, 560043, India

Location

Diabetes Thyroid Hormone Research Institute PVT LTD

Indore, Madhya Pradesh, 452001, India

Location

Diabetes Action Centre

Mumbai, Maharashtra, 400067, India

Location

Gandhi Endocrinology and Diabetes Centre

Nagpur, Maharashtra, 440010, India

Location

Endocrine Clinic

Nashik, Maharashtra, 422013, India

Location

Grant Medical Foundation

Pune, Maharashtra, 411001, India

Location

Fortis Escorts Hospital

Jaipur, Rajasthan, 302017, India

Location

B.P.Poddar Hospital and Medical Research Ltd

Kolkata, West Bengal, 700053, India

Location

Medwin Hospitals

Hyderabad, 500001, India

Location

Pushpawati Singhania Research Institute

New Delhi, 110017, India

Location

Soroka Medical Centre

Beersheba, 84101, Israel

Location

Hillel Yaffe Medical Center

Hadera, 38100, Israel

Location

Rambam Medical Centre

Haifa, 31096, Israel

Location

Wolfson Medical Centre

Holon, 58100, Israel

Location

National Centre for Childhood and Diabetes

Petah Tikva, 49202, Israel

Location

Chaim Sheba Medical Center

Ramat Gan, 56261, Israel

Location

P. Stradins Clinical University Hospital

Riga, 1002, Latvia

Location

Hospital CIMA Santa Engracia

San Pedro Garza García, Nuevo León, 66260, Mexico

Location

Hospital Mexico-Americano

Guadalajara, 44620, Mexico

Location

Hospital General de Mexico

Mexico City, 06726, Mexico

Location

Hospital Central

San Luis Potosí City, 78240, Mexico

Location

Diabeter Center for Pediatric and Adolescent Diabetes Care and Research

Rotterdam, 3011TG, Netherlands

Location

Samodzielny Publiczny Szpital Kliniczny Akademi Medycznej w Bialymstoku

Bialystok, 15-276, Poland

Location

Oddzial Diabetologiczny Klinika Pediatrii

Gdansk, 80-952, Poland

Location

Wojewodzki Specjalistyczny Szpital Dzieciecy

Kielce, 25-734, Poland

Location

Uniwersytecki Szpital Kliniczny

Lodz, 91-738, Poland

Location

I. Szpital Miejski im. Dr. E. Sonnenberga w Lodzi

Lodz, 92115, Poland

Location

Powiatowy Zespot Szpitali w Olesnicy, Oddzial Chorob Wewnetrznych

Oleśnica, 56400, Poland

Location

Klinika Endokrynologii i Diabetologii Wieku Rozwojowego

Wroclaw, 51-376, Poland

Location

S.C. Minimed S.R.L.

Bacau, 600164, Romania

Location

Institutul de Diabet

Bucharest, 020045, Romania

Location

Centrul Medical "Sanatatea ta"

Bucharest, 20725, Romania

Location

Spitulul Clinic Judetean de Urgenta Cluj

Cluj-Napoca, 400006, Romania

Location

Spitalul Clinic Judetean de Urgenta

Iași, 700111, Romania

Location

Spitalul Judetean Satu Mare

Satu Mare, 440055, Romania

Location

Hospital Universitari Dr. Josep Trueta de Girona

Girona, Gerona, 17007, Spain

Location

Hospital Universitario Principe de Asturias

Alcalá de Henares, Madrid, 28805, Spain

Location

Hospital Germans Trias i Pujol

Badalona, 8916, Spain

Location

Hospital Clinic I Provincial

Barcelona, 8036, Spain

Location

Fundacion Jimenez Diaz

Madrid, 28040, Spain

Location

Universitetssjukhuset i Linkoping

Linköping, 58185, Sweden

Location

Universitetssjukhuset i Lund

Lund, 22185, Sweden

Location

Sodersjukhuset AB

Stockholm, 11883, Sweden

Location

Donetsk Regional Children Clinical Hospital

Donetsk, 83052, Ukraine

Location

V. Danilevsky Institute of Endocrine Pathology Problems

Kharkiv, 61070, Ukraine

Location

Kharkiv Regional Clinical Children's Hospital

Kharkiv, 61093, Ukraine

Location

Ukrainian Scientific and Practical Center of Endocrine Surgery

Kyiv, 02175, Ukraine

Location

Ukranian Children Specialised Clinical Hospital

Kyiv, 02175, Ukraine

Location

Regional Clinical Endocrinological Dispensary

Vinnitsa, 21010, Ukraine

Location

Zaporizhzhya Regional Pediatric Hospital

Zaporizhzhya, 69035, Ukraine

Location

Addenbrookes Hospital

Cambridge, Cambridgeshire, CB20QQ, United Kingdom

Location

Royal Devon and Exeter Hospital

Exeter, Devon, EX25DW, United Kingdom

Location

Related Publications (2)

  • Ajmal N, Bogart MC, Khan P, Max-Harry IM, Healy AM, Nunemaker CS. Identifying Promising Immunomodulators for Type 1 Diabetes (T1D) and Islet Transplantation. J Diabetes Res. 2024 Dec 20;2024:5151171. doi: 10.1155/jdr/5151171. eCollection 2024.

  • Sherry N, Hagopian W, Ludvigsson J, Jain SM, Wahlen J, Ferry RJ Jr, Bode B, Aronoff S, Holland C, Carlin D, King KL, Wilder RL, Pillemer S, Bonvini E, Johnson S, Stein KE, Koenig S, Herold KC, Daifotis AG; Protege Trial Investigators. Teplizumab for treatment of type 1 diabetes (Protege study): 1-year results from a randomised, placebo-controlled trial. Lancet. 2011 Aug 6;378(9790):487-97. doi: 10.1016/S0140-6736(11)60931-8. Epub 2011 Jun 28.

MeSH Terms

Conditions

Diabetes Mellitus, Type 1

Interventions

teplizumab

Condition Hierarchy (Ancestors)

Diabetes MellitusGlucose Metabolism DisordersMetabolic DiseasesNutritional and Metabolic DiseasesEndocrine System DiseasesAutoimmune DiseasesImmune System Diseases

Results Point of Contact

Title
Sharon Rowland
Organization
Provention Bio, Inc

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
LTE60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 7, 2006

First Posted

October 11, 2006

Study Start

October 1, 2006

Primary Completion

June 1, 2010

Study Completion

August 1, 2011

Last Updated

December 5, 2023

Results First Posted

December 5, 2023

Record last verified: 2023-11

Data Sharing

IPD Sharing
Will not share

Locations