NCT00377572

Brief Summary

The purpose of this study is to find out if adding omalizumab to standard asthma treatment results in a safer, more effective, and longer lasting asthma treatment strategy than standard treatment alone, in inner-city children with mild to severe asthma.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
419

participants targeted

Target at P75+ for phase_4 asthma

Timeline
Completed

Started Oct 2006

Longer than P75 for phase_4 asthma

Geographic Reach
1 country

8 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

September 14, 2006

Completed
4 days until next milestone

First Posted

Study publicly available on registry

September 18, 2006

Completed
13 days until next milestone

Study Start

First participant enrolled

October 1, 2006

Completed
3.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2009

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2009

Completed
3.5 years until next milestone

Results Posted

Study results publicly available

June 7, 2013

Completed
Last Updated

March 21, 2017

Status Verified

February 1, 2017

Enrollment Period

3.2 years

First QC Date

September 14, 2006

Results QC Date

January 11, 2013

Last Update Submit

February 14, 2017

Conditions

Keywords

ImmunoglobulinsImmunoglobulin Eomalizumabanti-IgE

Outcome Measures

Primary Outcomes (1)

  • Maximum Number of Asthma Symptom Days

    Maximum symptom days was calculated as the largest of the following variables: number of days with wheezing, chest tightness, or cough; number of nights of sleep disturbance; and number of days when activities were affected. This symptom scale ranges from 0 to 14 days per a 2-week look-back period. A higher score reflected a greater number of asthma symptoms. Data represent an average of those collected in the time period (weeks 12-60), where at least one value was available in this assessment period and at baseline for a participant.

    Weeks 12-60: 12 months of assessments starting 12 weeks after the initiation of study treatment.

Secondary Outcomes (16)

  • Economic Outcome: Comparison of Number of Missed School Days Due to Asthma

    Weeks 12-60: 12 months of assessments starting 12 weeks after the initiation of study treatment.

  • Economic Outcome: Number of Missed Work Days by Caretaker Due to Asthma

    Weeks 12-60: 12 months of assessments starting 12 weeks after the initiation of study treatment.

  • Child Asthma Control Test (C-ACT) Score

    Weeks 12-60: 12 months of assessments starting 12 weeks after the initiation of treatment.

  • Asthma Control Test (ACT) Score

    Weeks 12-60: 12 months of assessments starting 12 weeks after the initiation of study treatment.

  • Forced Expiratory Volume in 1 Second (FEV1) % Predicted

    Weeks 12-60: 12 months of assessments starting 12 weeks after the initiation of study treatment.

  • +11 more secondary outcomes

Study Arms (2)

Omalizumab (Xolair) + Conventional Therapy

EXPERIMENTAL

Omalizumab was administered subcutaneously every 2 or 4 weeks over a period of 60 weeks to participants classified as having moderate to severe asthma. Doses (mg) and dosing frequency were determined by serum total IgE level (IU/mL) and body weight (kg). Also, participants continued with their conventional asthma therapy according to the National Asthma Education and Prevention Program (NAEPP-II, 2002) guidelines, under the management of an asthma specialist health care provider.

Biological: omalizumab

Placebo + Conventional Therapy

PLACEBO COMPARATOR

Placebo was administered subcutaneously every 2 or 4 weeks over a period of 60 weeks to participants classified as having moderate to severe asthma. Doses (mg) and dosing frequency were determined by serum total IgE level (IU/mL) and body weight (kg). Also, participants continued with their conventional asthma therapy according to the National Asthma Education and Prevention Program (NAEPP-II, 2002) guidelines, under the management of an asthma specialist health care provider.

Biological: omalizumab placebo

Interventions

omalizumabBIOLOGICAL

Subcutaneous injections of omalizumab will be administered every 2 or 4 weeks along with standard of care for asthma for 60 weeks, beginning with the Randomization Visit. Dosage is dependent on participant's individual characteristics.

Also known as: Xolair®, Anti-IgE antibody,humanized monoclonal
Omalizumab (Xolair) + Conventional Therapy

Subcutaneous injections of placebo will be administered every 2 or 4 weeks along with standard of care for asthma for 60 weeks, beginning with the Randomization Visit. Dosage is dependent on participant's individual characteristics.

Placebo + Conventional Therapy

Eligibility Criteria

Age6 Years - 20 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Both body weight and total serum IgE suitable for omalizumab dosing.
  • Diagnosis of asthma made by a physician more than 1 year prior to study entry OR diagnosis of asthma made less than 1 year prior to study entry but have had asthma symptoms for longer than 1 year prior to study entry
  • Are receiving long-term asthma control therapy OR have symptoms consistent with persistent asthma OR have evidence of uncontrolled disease
  • Positive prick skin test to at least one perennial allergen (e.g., dust mite, cockroach, mold, cat, dog, rat, mouse)
  • Live in a preselected zip code are
  • Able to perform spirometry measurements
  • Willing to sign informed consent or have parent or guardian willing to provide informed consent
  • Previously had chicken pox or received varicella (chicken pox) vaccine
  • Have some form of health care insurance that covers costs of medications

You may not qualify if:

  • If participant meets any of these criteria, they are not eligible at that time but may be reassessed:
  • Systemic prednisone (or equivalent) during the 2 weeks prior to Visit 2
  • Systemic prednisone (or equivalent) for more than 30 of the 60 days prior to study entry
  • Pregnancy or breastfeeding
  • Acute sinusitis or chest infection requiring antibiotics within 1 month of study screening
  • Currently participating in another asthma-related clinical trial or have previously participated in an another asthma-related trial within 1 month of study entry
  • Does not sleep at least 4 nights per week in one home
  • Lives with a foster parent
  • Does not have access to a phone
  • Plans to move during the study
  • Previously treated with anti-IgE therapy within 1 year of study entry
  • Currently receiving or received hyposensitization therapy to any allergen in the year prior to study entry
  • Previously received hyposensitization therapy to dust mite, Alternaria, or cockroach for more than 6 months in the 3 years prior to study entry
  • If participant meets any of these criteria, they are not eligible for the study and may not be reassessed:
  • Significant medical illness. More information on this criterion can be found in the protocol.
  • +6 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (8)

University of Arizona Health Sciences Center

Tucson, Arizona, 245018, United States

Location

National Jewish Medical and Research Center

Denver, Colorado, 80206, United States

Location

Children's National Medical Center

Washington D.C., District of Columbia, 20010, United States

Location

Children's Memorial Hospital

Chicago, Illinois, 60614, United States

Location

Boston University School of Medicine

Boston, Massachusetts, 02118, United States

Location

Columbia University Medical Center

New York, New York, 10029, United States

Location

Rainbow Babies and Children's Hospital

Cleveland, Ohio, 44106, United States

Location

University of Texas Southwestern Medical Center

Dallas, Texas, 75390, United States

Location

Related Publications (6)

  • Ayres JG, Higgins B, Chilvers ER, Ayre G, Blogg M, Fox H. Efficacy and tolerability of anti-immunoglobulin E therapy with omalizumab in patients with poorly controlled (moderate-to-severe) allergic asthma. Allergy. 2004 Jul;59(7):701-8. doi: 10.1111/j.1398-9995.2004.00533.x.

    PMID: 15180756BACKGROUND
  • Busse W, Corren J, Lanier BQ, McAlary M, Fowler-Taylor A, Cioppa GD, van As A, Gupta N. Omalizumab, anti-IgE recombinant humanized monoclonal antibody, for the treatment of severe allergic asthma. J Allergy Clin Immunol. 2001 Aug;108(2):184-90. doi: 10.1067/mai.2001.117880.

    PMID: 11496232BACKGROUND
  • Mvula M, Larzelere M, Kraus M, Moisiewicz K, Morgan C, Pierce S, Post R, Nash T, Moore C. Prevalence of asthma and asthma-like symptoms in inner-city schoolchildren. J Asthma. 2005 Feb;42(1):9-16. doi: 10.1081/jas-200044746.

    PMID: 15801322BACKGROUND
  • Szefler SJ, Apter A. Advances in pediatric and adult asthma. J Allergy Clin Immunol. 2005 Mar;115(3):470-7. doi: 10.1016/j.jaci.2004.12.1123.

    PMID: 15753890BACKGROUND
  • Busse WW, Morgan WJ, Gergen PJ, Mitchell HE, Gern JE, Liu AH, Gruchalla RS, Kattan M, Teach SJ, Pongracic JA, Chmiel JF, Steinbach SF, Calatroni A, Togias A, Thompson KM, Szefler SJ, Sorkness CA. Randomized trial of omalizumab (anti-IgE) for asthma in inner-city children. N Engl J Med. 2011 Mar 17;364(11):1005-15. doi: 10.1056/NEJMoa1009705.

  • Szefler SJ, Casale TB, Haselkorn T, Yoo B, Ortiz B, Kattan M, Busse WW. Treatment Benefit with Omalizumab in Children by Indicators of Asthma Severity. J Allergy Clin Immunol Pract. 2020 Sep;8(8):2673-2680.e3. doi: 10.1016/j.jaip.2020.03.033. Epub 2020 Apr 13.

Related Links

MeSH Terms

Conditions

Asthma

Interventions

Omalizumabanti-IgE antibodies

Condition Hierarchy (Ancestors)

Bronchial DiseasesRespiratory Tract DiseasesLung Diseases, ObstructiveLung DiseasesRespiratory HypersensitivityHypersensitivity, ImmediateHypersensitivityImmune System Diseases

Intervention Hierarchy (Ancestors)

Antibodies, Anti-IdiotypicAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsAntibodies, Monoclonal, HumanizedAntibodies, MonoclonalSerum GlobulinsGlobulins

Results Point of Contact

Title
Director, Clinical Research Program
Organization
DAIT/NIAID

Study Officials

  • William W. Busse, MD

    University of Wisconsin, Madison

    STUDY CHAIR
  • George T. O'Connor, MD, MS

    Boston University

    PRINCIPAL INVESTIGATOR
  • Jacqueline Pongracic, MD

    Ann & Robert H Lurie Children's Hospital of Chicago

    PRINCIPAL INVESTIGATOR
  • Jamen Chmiel, MD

    Rainbow Babies and Children's Hospital

    PRINCIPAL INVESTIGATOR
  • Rebecca S. Gruchalla, MD, PhD

    University of Texas Southwestern Medical Center

    PRINCIPAL INVESTIGATOR
  • Andrew Liu, MD

    National Jewish Health

    PRINCIPAL INVESTIGATOR
  • Meyer Kattan, MD, CM

    Columbia University

    PRINCIPAL INVESTIGATOR
  • Wayne Morgan, MD, CM

    University of Arizona Health Sciences Center

    PRINCIPAL INVESTIGATOR
  • Stephen Teach, MD, MPH

    Children's National Research Institute

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 4
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, CARE PROVIDER
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
NIH
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 14, 2006

First Posted

September 18, 2006

Study Start

October 1, 2006

Primary Completion

December 1, 2009

Study Completion

December 1, 2009

Last Updated

March 21, 2017

Results First Posted

June 7, 2013

Record last verified: 2017-02

Data Sharing

IPD Sharing
Will share

Participant level data and additional relevant materials are available to the public in the Immunology Database and Analysis Portal (ImmPort). ImmPort is a long-term archive of clinical and mechanistic data from DAIT-funded grants and contracts.

Available IPD Datasets

Individual Participant Data Set (SDY211)Access
Study Protocol (SDY211)Access
Study summary, -design, -adverse event(s), -interventions, -medications, -demographics, -study files. (SDY211)Access

Locations