NCT00358956

Brief Summary

This will be a Phase II, open label study to establish the effect of once-daily oral doses of ZD6474 100mg in subjects with locally advanced or metastatic hereditary medullary thyroid cancer in whom no standard therapeutic option is available.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
19

participants targeted

Target at below P25 for phase_2

Timeline
Completed

Started Aug 2006

Longer than P75 for phase_2

Geographic Reach
8 countries

9 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

July 28, 2006

Completed
4 days until next milestone

First Posted

Study publicly available on registry

August 1, 2006

Completed
Same day until next milestone

Study Start

First participant enrolled

August 1, 2006

Completed
1.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 1, 2008

Completed
4.7 years until next milestone

Results Posted

Study results publicly available

August 31, 2012

Completed
1.7 years until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2014

Completed
Last Updated

January 30, 2017

Status Verified

December 1, 2016

Enrollment Period

1.4 years

First QC Date

July 28, 2006

Results QC Date

April 27, 2011

Last Update Submit

December 7, 2016

Conditions

Keywords

medullary thyroid cancerMTChereditary medullary thyroid cancerthyroid cancer

Outcome Measures

Primary Outcomes (1)

  • Objective Response Rate (ORR)

    The ORR is the number of patients that are responders ie those patients with a confirmed best objective response of complete response (CR) or partial response (PR) as defined by RECIST criteria. The categories for best objective response are CR, PR, stable disease (SD)\>= 12 weeks, progressive disease (PD) or NE.

    RECIST assessed at screening (up to 3 weeks prior to first dose), then every 12 weeks (± 2 weeks), from date of first dose to objective progression, up to and including discontinuation of study treatment.

Secondary Outcomes (6)

  • Progression-Free Survival (PFS)

    RECIST assessed at screening (up to 3 weeks prior to first dose), then every 12 weeks (± 2 weeks), from date of first dose to objective progression, up to and including discontinuation of study treatment.

  • Disease Control Rate (DCR)

    RECIST assessed at screening (up to 3 weeks prior to first dose), then every 12 weeks (± 2 weeks), from date of first dose to objective progression, up to and including discontinuation of study treatment.

  • World Heath Organization (WHO) Performance Status

    WHO PS assessed at screening (up to 3 weeks prior to first dose), baseline and then every 12 weeks (± 2 weeks), up to and including discontinuation of study treatment.

  • Symptomatic Response

    Symptomatic diarrhea was assessed using stool frequency diaries. Baseline was established using the average of the 4 days immediately prior to first dose, then weekly until discontinuation of study treatment.

  • Biochemical Response Calcitonin (CTN )

    Blood samples for analysis of CTN were taken at screening (0, 1, 4, and 8 hours to determine the baseline CTN/CEA level) then every 4 weeks until discontinuation Time point(s) at which outcome measure was assessed. (Limit: 255 characters)

  • +1 more secondary outcomes

Study Arms (1)

1

EXPERIMENTAL
Drug: ZD6474 (vandetanib)

Interventions

100 mg once daily oral tablet

Also known as: Caprelsa™
1

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Provision of written informed consent
  • Previously confirmed histological diagnosis of locally advanced or metastatic hereditary medullary thyroid carcinoma without standard therapeutic options
  • Aged 18 or over and a life expectancy of more than 12 weeks

You may not qualify if:

  • The last dose of prior chemo/radiation received less than 4 weeks before the start of study therapy
  • Congenital long QT syndrome or 1st degree relative with unexplained sudden death under 40 years of age, history of arrhythmia

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (9)

Research Site

Little Rock, Arkansas, United States

Location

Research Site

Boston, Massachusetts, United States

Location

Research Site

St Leonards, Australia

Location

Research Site

Sherbrooke, Quebec, Canada

Location

Research Site

Pisa, Italy

Location

Research Site

Utrecht, Netherlands

Location

Research Site

Bucharest, Romania

Location

Research Site

Madrid, Spain

Location

Research Site

Basel, Switzerland

Location

Related Publications (1)

  • Robinson BG, Paz-Ares L, Krebs A, Vasselli J, Haddad R. Vandetanib (100 mg) in patients with locally advanced or metastatic hereditary medullary thyroid cancer. J Clin Endocrinol Metab. 2010 Jun;95(6):2664-71. doi: 10.1210/jc.2009-2461. Epub 2010 Apr 6.

    PMID: 20371662BACKGROUND

Related Links

MeSH Terms

Conditions

Thyroid NeoplasmsCarcinoma, MedullaryFamilial medullary thyroid carcinoma

Interventions

vandetanib

Condition Hierarchy (Ancestors)

Endocrine Gland NeoplasmsNeoplasms by SiteNeoplasmsHead and Neck NeoplasmsEndocrine System DiseasesThyroid DiseasesCarcinoma, NeuroendocrineNeuroendocrine TumorsNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeAdenocarcinomaCarcinomaNeoplasms, Glandular and EpithelialNeoplasms, Ductal, Lobular, and MedullaryNeoplasms, Nerve Tissue

Results Point of Contact

Title
Trial Transparency Team
Organization
Sanofi

Study Officials

  • Clinical Sciences & Operations

    Sanofi

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 28, 2006

First Posted

August 1, 2006

Study Start

August 1, 2006

Primary Completion

January 1, 2008

Study Completion

May 1, 2014

Last Updated

January 30, 2017

Results First Posted

August 31, 2012

Record last verified: 2016-12

Locations