NCT00341705

Brief Summary

The Second Multicenter Hemophilia Cohort Study (MHCS-II) will evaluate and prospectively follow approximately 4500 persons with hemophilia who were exposed to hepatitis C virus (HCV). The vast majority will have been infected with HCV, and approximately 1/3 will have been infected with human immunodeficiency virus (HIV). Primary objectives are to quantify the rates of liver decompensation, hepatocellular carcinoma, and non-Hodgkin lymphoma and to evaluate candidate clinical, genetic, virologic, serologic and immunologic markers that are likely to be on the causal pathway for these conditions. Candidate clinical and laboratory markers will be examined longitudinally to define changes over time and their relationships to one another. Collaborative studies will focus on genome scanning and evaluation of candidate genetic loci for susceptibility or resistance to HCV and HIV infections or to the diseases that result from these infections. Additional studies will identify response and complication rates of various anti-HCV and anti-HIV regimens in the setting of comprehensive clinical care of persons with hemophilia.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
2,565

participants targeted

Target at P75+ for all trials

Timeline
Completed

Started Apr 2001

Longer than P75 for all trials

Geographic Reach
8 countries

48 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

April 27, 2001

Completed
5.1 years until next milestone

First Submitted

Initial submission to the registry

June 19, 2006

Completed
2 days until next milestone

First Posted

Study publicly available on registry

June 21, 2006

Completed
6.8 years until next milestone

Study Completion

Last participant's last visit for all outcomes

April 2, 2013

Completed
Last Updated

December 17, 2019

Status Verified

April 2, 2013

First QC Date

June 19, 2006

Last Update Submit

December 14, 2019

Conditions

Keywords

AIDSCancerHepatitis C VirusHIVNatural HistoryHemophiliaHepatitis C

Eligibility Criteria

Age13 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Must be registered patient with an inherited coagulation disorder at a participating MHCS-II center. Disorders include hemophilia A or B (congenital factor VIII or IX deficiency), deficiencies in other factors such as V or XI, and vonWillebrand's disease. (Unless noted otherwise, all of the disorders will collectively be referred to as hemophilia .) All such hemophilia and vonWillebrand s disease patients are to be recruited as study participants.
  • Since January 1, 1993, must have had at least one positive result on a licensed assay for HCV antibodies, HIV antibodies, or HIV RNA.
  • Must be at least 13 years of age at enrollment.
  • Must provide signed informed consent or, for minors, signed assent plus signed informed consent from the parent or guardian.

You may not qualify if:

  • Is not a patient with an inherited coagulation disorder.
  • Does not have a positive test for HCV antibodies, HIV antibodies, or HIV RNA on a licensed assay performed since January 1, 1993.
  • Is less than 13 years of age.
  • Lacks informed consent/assent.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (48)

University of Arizona

Tucson, Arizona, 85724, United States

Location

University of California, Davis

Davis, California, 95616, United States

Location

Children's Hospital of Orange County

Orange, California, 92613, United States

Location

University of California, San Francisco

San Francisco, California, 94143, United States

Location

University of Colorado

Denver, Colorado, 80220-3706, United States

Location

Christiana Hospital

Wilmington, Delaware, United States

Location

Georgetown University

Washington D.C., District of Columbia, 20007-2197, United States

Location

Childrens National Medical Center

Washington D.C., District of Columbia, United States

Location

Emory University

Atlanta, Georgia, 30322-1102, United States

Location

University of Illinois

Chicago, Illinois, 60612, United States

Location

Childrens Memorial Hospital, Chicago

Chicago, Illinois, 60614-3394, United States

Location

St. Vincent's Hospital

Indianapolis, Indiana, United States

Location

Tulane University

New Orleans, Louisiana, 70112-2699, United States

Location

Wayne State University Hutzel Hospital

Detroit, Michigan, 48201, United States

Location

University of Minnesota

Minneapolis, Minnesota, 55415, United States

Location

University of Mississippi

Jackson, Mississippi, 39216, United States

Location

St. Louis University

St Louis, Missouri, 63104, United States

Location

University of New Mexico

Albuquerque, New Mexico, 87131, United States

Location

University of Buffalo

Buffalo, New York, United States

Location

North Shore Long Island Jewish Health System

Lake Success, New York, 11042, United States

Location

Cornell University

New York, New York, 10021-4872, United States

Location

Mt. Sinai Medical Center

New York, New York, 10029-0574, United States

Location

University of North Carolina

Chapel Hill, North Carolina, 27599-7030, United States

Location

Wake Forest University

Winston-Salem, North Carolina, 27103, United States

Location

Childrens Hospital, Cinncinati

Cincinnati, Ohio, 45229-3039, United States

Location

University of Cincinnati

Cincinnati, Ohio, 45267, United States

Location

Ohio State University

Columbus, Ohio, 43210-1240, United States

Location

Wright State University

Dayton, Ohio, 45435, United States

Location

University of Oklahoma

Oklahoma City, Oklahoma, United States

Location

Milton Hershey Medical Center

Hershey, Pennsylvania, 17033, United States

Location

University of Pennsylvania

Philadelphia, Pennsylvania, 19104-6056, United States

Location

Thomas Jefferson University

Philadelphia, Pennsylvania, 19107-6541, United States

Location

Palmentto Health Alliance

Columbia, South Carolina, 29202, United States

Location

University of Tennessee

Memphis, Tennessee, 38103, United States

Location

Vanderbilt University

Nashville, Tennessee, 37232, United States

Location

University of Texas, Houston

Houston, Texas, 77030, United States

Location

University of Texas, San Antonio

San Antonio, Texas, United States

Location

University of Utah

Salt Lake City, Utah, 84112, United States

Location

Childrens Hospital of Wisconsin

Milwaukee, Wisconsin, United States

Location

Hospital Brigadeiro

São Paulo, Brazil

Location

University of Sao Paulo

São Paulo, Brazil

Location

South East Health Care Corporation

New Brunswick, Canada

Location

Hospices Civils de Lyon

Lyon, France

Location

University of Bonn

Bonn, Germany

Location

Laikon General Hospital of Athens

Athens, Greece

Location

University of Florence

Florence, Italy

Location

University de Milano

Milan, Italy

Location

Karolinska Institute St. Gorans Hospital

Stockholm, Sweden

Location

Related Publications (3)

  • Mannucci PM, Tuddenbam EG. The hemophilias: progress and problems. Semin Hematol. 1999 Oct;36(4 Suppl 7):104-17.

    PMID: 10595759BACKGROUND
  • Kroner BL, Rosenberg PS, Aledort LM, Alvord WG, Goedert JJ. HIV-1 infection incidence among persons with hemophilia in the United States and western Europe, 1978-1990. Multicenter Hemophilia Cohort Study. J Acquir Immune Defic Syndr (1988). 1994 Mar;7(3):279-86.

    PMID: 8106967BACKGROUND
  • Eyster ME, Diamondstone LS, Lien JM, Ehmann WC, Quan S, Goedert JJ. Natural history of hepatitis C virus infection in multitransfused hemophiliacs: effect of coinfection with human immunodeficiency virus. The Multicenter Hemophilia Cohort Study. J Acquir Immune Defic Syndr (1988). 1993 Jun;6(6):602-10.

    PMID: 8098752BACKGROUND

MeSH Terms

Conditions

Hepatic InsufficiencyCarcinoma, HepatocellularLymphoma, Non-HodgkinAcquired Immunodeficiency SyndromeNeoplasmsHepatitis CHemophilia A

Condition Hierarchy (Ancestors)

Liver DiseasesDigestive System DiseasesAdenocarcinomaCarcinomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeLiver NeoplasmsDigestive System NeoplasmsNeoplasms by SiteLymphomaLymphoproliferative DisordersLymphatic DiseasesHemic and Lymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesHIV InfectionsBlood-Borne InfectionsCommunicable DiseasesInfectionsSexually Transmitted Diseases, ViralSexually Transmitted DiseasesLentivirus InfectionsRetroviridae InfectionsRNA Virus InfectionsVirus DiseasesSlow Virus DiseasesGenital DiseasesUrogenital DiseasesImmunologic Deficiency SyndromesHepatitis, Viral, HumanFlaviviridae InfectionsHepatitisBlood Coagulation Disorders, InheritedBlood Coagulation DisordersHematologic DiseasesCoagulation Protein DisordersHemorrhagic DisordersGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and Abnormalities

Study Officials

  • James J Goedert, M.D.

    National Cancer Institute (NCI)

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
observational
Sponsor Type
NIH

Study Record Dates

First Submitted

June 19, 2006

First Posted

June 21, 2006

Study Start

April 27, 2001

Study Completion

April 2, 2013

Last Updated

December 17, 2019

Record last verified: 2013-04-02

Locations