NCT00262782

Brief Summary

RATIONALE: Drugs used in chemotherapy, such as fludarabine, work in different ways to stop the growth of cancer cells, either by killing the cells or by stopping them from dividing. Sometimes, the cancer may not need treatment until it progresses. In this case, observation may be sufficient. It is not yet known whether fludarabine is more effective than observation in treating chronic lymphocytic leukemia. PURPOSE: This randomized phase III trial is studying fludarabine to see how well it works compared to observation only in treating patients with stage 0, stage I, or stage II B-cell chronic lymphocytic leukemia.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
877

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Apr 1997

Longer than P75 for phase_3

Geographic Reach
2 countries

117 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

April 1, 1997

Completed
7.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2004

Completed
1 year until next milestone

First Submitted

Initial submission to the registry

December 6, 2005

Completed
1 day until next milestone

First Posted

Study publicly available on registry

December 7, 2005

Completed
4.5 years until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2010

Completed
Last Updated

February 20, 2020

Status Verified

February 1, 2020

Enrollment Period

7.7 years

First QC Date

December 6, 2005

Last Update Submit

February 18, 2020

Conditions

Keywords

B-cell chronic lymphocytic leukemiastage 0 chronic lymphocytic leukemiastage I chronic lymphocytic leukemiastage II chronic lymphocytic leukemia

Study Arms (2)

Fludarabine

EXPERIMENTAL
Drug: Fludarabine

watch & wait

NO INTERVENTION

Interventions

Fludarabine i.v. (25 mg/m2/d, d1-5) q28d; max 6 cycles

Also known as: Fludura
Fludarabine

Eligibility Criteria

Age18 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
DISEASE CHARACTERISTICS: * Confirmed diagnosis of B-cell chronic lymphocytic leukemia * Rai stage 0-II (Binet stage A) disease * Meets 1 of the following criteria: * High-risk disease, as defined by the following: * Serum thymidine kinase level \> 7.0 U/L * Elevated β2-microglobulin level * Presence of non-nodular bone marrow infiltration * Short lymphocyte doubling time * Low-risk disease * Meets none of the criteria (as listed above) for high-risk disease PATIENT CHARACTERISTICS: Performance status * Not specified Life expectancy * More than 6 months Hematopoietic * No autoimmune hemolytic anemia * No thrombocytopenia Hepatic * Not specified Renal * Not specified Other * No severe organ dysfunction * No other prior or concurrent malignancy PRIOR CONCURRENT THERAPY: Chemotherapy * No prior chemotherapy * No other concurrent chemotherapy

Contact the study team to discuss eligibility requirements. They can help determine if this study is right for you.

Sponsors & Collaborators

Study Sites (117)

Allg. Krankenhaus der Stadt Wien Universitaets-Kinderklinik

Vienna, 1090, Austria

Location

Hanuschkrankenhaus

Vienna, A-1140, Austria

Location

Klinikum St. Marien

Amberg, D-92224, Germany

Location

Internistische Praxis - Arnstadt

Arnstadt, 99310, Germany

Location

Zentralklinikum Augsburg

Augsburg, DOH-86156, Germany

Location

Kreiskrankenhaus Aurich

Aurich, D-26603, Germany

Location

Regional Hospital Am Plattenwald

Bad Friedrichshall, 74172, Germany

Location

Regional Hospital Bad Hersfeld

Bad Hersfeld, 36251, Germany

Location

Arzt fuer Innere Medizin - Bad Reichenhall

Bad Reichenhall, 83435, Germany

Location

Humaine - Clinic

Bad Saarow, 15526, Germany

Location

Ermstalklinik Bad Urach

Bad Urach, D-72574, Germany

Location

Internistische Praxis - Berlin

Berlin, 10969, Germany

Location

Internistische Gemeinschaftspraxis - Berlin

Berlin, 13347, Germany

Location

Haematologisch-Onkologische Schwerpunktpraxis

Berlin, 13357, Germany

Location

Internistische Praxis - Berlin

Berlin, 14052, Germany

Location

Internistische Gemeinschaftspraxis - Berlin

Berlin, 14195, Germany

Location

Charite - Campus Charite Mitte

Berlin, D-10117, Germany

Location

Charite - Universitaetsmedizin Berlin - Campus Benjamin Franklin

Berlin, D-12200, Germany

Location

Charite - Campus Virchow Klinikum

Berlin, D-13353, Germany

Location

Gemeinschaftspraxis - Betzdorf

Betzdorf, 57518, Germany

Location

Praxis Dres. F.& G. Doering

Bremen, 28205, Germany

Location

Krankenhaus Burglengenfeld

Burglengenfeld, 93133, Germany

Location

Praxis Fuer Haematologie Internistische Onkologie

Cologne, D-50677, Germany

Location

Medizinische Universitaetsklinik I at the University of Cologne

Cologne, D-50924, Germany

Location

Onkologische Schwerpunktpraxis

Cottbus, D-03046, Germany

Location

Staedtisches Klinikum Dessau

Dessau, D-06847, Germany

Location

Onkologische Gemeinschaftspraxis - Dresden

Dresden, 01127, Germany

Location

Michael Schaefers und Partner

Duisburg, D-47051, Germany

Location

Universitaetsklinik Duesseldorf

Düsseldorf, D-40225, Germany

Location

Internistische Gemeinschaftpraxis - Ehingen

Ehingen, 89584, Germany

Location

Onkologische Schwerpunktpraxis - Erding

Erding, 85435, Germany

Location

Internistische/Onkologische Praxis - Erfurt

Erfurt, 99084, Germany

Location

Onkologische Schwerpunkt Praxis

Erlangen, D-91052, Germany

Location

St. Antonius Hospital

Eschweiler, DOH-52249, Germany

Location

Universitaetsklinikum Essen

Essen, D-45122, Germany

Location

Staedtische Kliniken Esslingen

Esslingen am Neckar, 73730, Germany

Location

Internistische Gemeinschaftspraxis - Forchheim

Forchheim, 91301, Germany

Location

Klinikum Garmisch - Partenkirchen

Garmisch-Partenkirchen, N 82467, Germany

Location

Gemeinschaftspraxis - Germering

Germering, 82110, Germany

Location

Internistische Praxisgemeinschaft

Germering, 82110, Germany

Location

Klinik Fuer Innere Medizin, Hematology/Oncology, Ernst Moritz Armdt Universitaet

Greifswald, D-17487, Germany

Location

Onkologische Gemeinschaftspraxis - Gross-Gerau

Groß-Gerau, 64521, Germany

Location

St. Marien Hospital at Katholisches Krankenhaus hagen gem. GmbH

Hagen, 58095, Germany

Location

Allgemeines Krankenhaus Hagen

Hagen, D-58095, Germany

Location

Internistische Praxis - Halle

Halle, 06108, Germany

Location

Internistische Gemeinschaftspraxis - Halle

Halle, 06110, Germany

Location

Martin Luther Universitaet

Halle, D-06097, Germany

Location

Praxis fur Innere Medizin - Hamburg

Hamburg, 22457, Germany

Location

Allgemeines Krankenhaus St. Georg

Hamburg, D-20099, Germany

Location

Universitaetsklinikum Hamburg-Eppendorf

Hamburg, D-20246, Germany

Location

Schwerpunktpraxis Haematologie/Onkologie - Hannover

Hanover, 30169, Germany

Location

Facharzt fuer Allgemeinmedizin - Hausham

Hausham, 83734, Germany

Location

Facharzt fuer Innere Medizin - Hechingen

Hechingen, 72379, Germany

Location

Onkologische Schwerpunktpraxis Heidelberg

Heidelberg, 69115, Germany

Location

Universitatsklinikum Heidelberg

Heidelberg, 69120, Germany

Location

Medizinischen Klinik Dr. R. Schindlbeck

Herrsching am Ammersee, 82211, Germany

Location

Oncological Specialist Practice

Hildesheim, 31134, Germany

Location

Universitaetsklinikum des Saarlandes

Homburg, D-66421, Germany

Location

Clinic for Bone Marrow Transplantation and Hematology and Oncology

Idar-Oberstein, D-55743, Germany

Location

Praxis am Evangelischen Krankenhaus Bethanien

Iserlohn, D-58644, Germany

Location

Internistische Gemeinschaftspraxis - Jena

Jena, 07743, Germany

Location

Westpfalz-Klinikum GmbH

Kaiserslautern, D-67653, Germany

Location

Staedt Klinikum Karlsruhe GGMBH

Karlsruhe, 76133, Germany

Location

Facharzt Fuer Jnnere Medizin

Karlsruhe, 76135, Germany

Location

St. Vincentius-Kliniken

Karlsruhe, D-76137, Germany

Location

Internistische Gemeinschaftspraxis - Kassel

Kassel, 34117, Germany

Location

Staedtische Krankenhaus Kiel

Kiel, 23116, Germany

Location

Internistische Onkologische Praxis - Kronach

Kronach, 96317, Germany

Location

Internistische Praxis - Landshut

Landshut, 84028, Germany

Location

Onkologische Schwerpunktpraxis Leer

Leer, D-26789, Germany

Location

Klinikum Lippe - Lemgo

Lemgo, D-32657, Germany

Location

Universitaetsklinkum Magdeburg der Otto-von-Guericke-Universitaet Magdeburg

Magdeburg, D-39120, Germany

Location

Gemeinschaftspraxis

Mannheim, D-68161, Germany

Location

Philipps-Universitaet Marburg Klinikum

Marburg, D-35033, Germany

Location

Internistische Gemeinschaftspraxis - Memmingen

Memmingen, 87700, Germany

Location

Klinikum Minden

Minden, D-32427, Germany

Location

Haematologische Praxis - Moenchengladbach

Mönchengladbach, 41239, Germany

Location

Klinikum Innenstadt

Munich, 80331, Germany

Location

Krankenhaus Muenchen Schwabing

Munich, 80804, Germany

Location

Hamatologische Schwerpunktpraxis

Munich, 81679, Germany

Location

Munich Oncologic Practice at Elisenhof

Munich, D-80335, Germany

Location

Klinikum der Universitaet Muenchen - Grosshadern Campus

Munich, D-81377, Germany

Location

Staedtisches Krankenhaus Muenchen - Harlaching

Munich, D-81545, Germany

Location

Klinikum Garmisch-Partenkirchen GmbH Abteilung fuer Innere Medizin Murnau

Murnau am Staffelsee, 82418, Germany

Location

Haematologisch-onkologische Gemeinschaftspraxis - Muenster

Münster, 48149, Germany

Location

Internistische Praxis - Neuenkirchen

Neuenkirchen, 48485, Germany

Location

Onkologische Schwerpunktpraxis Dr. Schmidt

Neunkirchen, D-66538, Germany

Location

Praxis fuer Haematologie und Interne Onkologie

Norderstedt, 22844, Germany

Location

Sudharz-Krankenhaus Nordhausen gGmbH

Nordhausen, 99734, Germany

Location

Klinikum Nuernberg - Klinikum Nord

Nuremberg, D-90419, Germany

Location

Internistische Gemeinschaftspraxis - Offenbach

Offenbach, 63065, Germany

Location

Hematologische Praxis

Oldenburg, 26121, Germany

Location

Gemeinschaftliche Schwerpunktpraxis - Osnabrueck

Osnabrück, 49074, Germany

Location

Municipal Hospital Complex

Pforzheim, D-75178, Germany

Location

Hematologische Onkologische Praxis

Regensburg, 93047, Germany

Location

Jakobi Krankenhaus

Rheine, 48431, Germany

Location

Klinik und Poliklinik fuer Innere Medizin - Universitaet Rostock

Rostock, D-18057, Germany

Location

Schwerpunktpraxis Fuer Haematologie Und Onkologie

Saarbruecke, N-66113, Germany

Location

Caritasklinik St. Theresia

Saarbrücken, D-66113, Germany

Location

Onkologische Schwerpunktpraxis - Schrobenhausen

Schrobenhausen, 86529, Germany

Location

Praxis - Schwenningen

Schwenningen, 78054, Germany

Location

St. Marien - Krankenhaus Siegen GMBH

Siegen, D-57072, Germany

Location

Evang. Jung-Stilling Hospital

Siegen, D-57074, Germany

Location

Praxisgemeinschaft - Stade

Stade, 21680, Germany

Location

Onkologische Schwerpunktpraxis - Straubing

Straubing, 94315, Germany

Location

Haematologische Praxis

Stuttgart, D-70173, Germany

Location

Diakonie Klinikum Stuttgart

Stuttgart, D-70176, Germany

Location

Onkologische Gemeinschaftspraxis - Trier

Trier, 54290, Germany

Location

Southwest German Cancer Center at Eberhard-Karls-University

Tübingen, D-72076, Germany

Location

Universitaetsklinikum Ulm

Ulm, D-89081, Germany

Location

St. Marien Hospital

Vechta, D-49377, Germany

Location

Gemeinschaftspraxis - Weiden

Weiden, 92637, Germany

Location

Haematologisch-Onkologische Schwerpunktpraxis - Weilheim

Weilheim, 82362, Germany

Location

Internistische Praxis - Wendlingen

Wendlingen, 73240, Germany

Location

Kliniken St. Antonius

Wuppertal, D-42283, Germany

Location

Hamatologisch - Onkologische Praxis Wurzburg

Würzburg, 97070, Germany

Location

Medizinische Klinik und Poliklinik II - Universitaetsklinikum Wuerzburg

Würzburg, D-97070, Germany

Location

Related Publications (10)

  • Gobel M, Eisele L, Mollmann M, Huttmann A, Johansson P, Scholtysik R, Bergmann M, Busch R, Dohner H, Hallek M, Seiler T, Stilgenbauer S, Klein-Hitpass L, Duhrsen U, Durig J. Progranulin is a novel independent predictor of disease progression and overall survival in chronic lymphocytic leukemia. PLoS One. 2013 Aug 23;8(8):e72107. doi: 10.1371/journal.pone.0072107. eCollection 2013.

    PMID: 24009671BACKGROUND
  • Sachanas S, Pangalis GA, Fink AM, Bahlo J, Fischer K, Levidou G, Kyrtsonis MC, Bartzi V, Vassilakopoulos TP, Kalpadakis C, Koulieris E, Moschogiannis M, Yiakoumis X, Tsirkinidis P, Angelopoulou MK, Eichhorst B, Hallek M. Small Lymphocytic Lymphoma: Analysis of Two Cohorts Including Patients in Clinical Trials of the German Chronic Lymphocytic Leukemia Study Group (GCLLSG) or in "Real-Life" Outside of Clinical Trials. Anticancer Res. 2019 May;39(5):2591-2598. doi: 10.21873/anticanres.13382.

    PMID: 31092457BACKGROUND
  • Bergmann MA, Eichhorst BF, Busch R, et al.: Early and risk-adapted therapy with fludarabine in high-risk Binet stage A CLL patients prolongs progression free survival but not overall survival: results of the CLL1 protocol of the German CLL Study Group (GCLLSG). [Abstract] Blood 110 (11): A-2038, 2007.

    RESULT
  • Bergmann MA, Eichhorst BF, Busch R, et al.: Prospective evaluation of prognostic parameters in early stage chronic lymphocytic leukemia (CLL): results of the CLL1-protocol of the German CLL Study Group (GCLLSG). [Abstract] Blood 110 (11): A-625, 2007.

    RESULT
  • Hoechstetter MA, Busch R, Eichhorst B, Buhler A, Winkler D, Eckart MJ, Vehling-Kaiser U, Schimke H, Jager U, Hurtz HJ, Hopfinger G, Hartmann F, Fuss H, Abenhardt W, Blau I, Freier W, Muller L, Goebeler M, Wendtner CM, Bahlo J, Fischer K, Bentz M, Emmerich B, Dohner H, Hallek M, Stilgenbauer S. Early, risk-adapted treatment with fludarabine in Binet stage A chronic lymphocytic leukemia patients: results of the CLL1 trial of the German CLL study group. Leukemia. 2017 Dec;31(12):2833-2837. doi: 10.1038/leu.2017.246. Epub 2017 Aug 14. No abstract available.

  • Hoechstetter MA, Busch R, Eichhorst B, Buhler A, Winkler D, Bahlo J, Robrecht S, Eckart MJ, Vehling-Kaiser U, Jacobs G, Jager U, Hurtz HJ, Hopfinger G, Hartmann F, Fuss H, Abenhardt W, Blau I, Freier W, Muller L, Goebeler M, Wendtner C, Fischer K, Herling CD, Starck M, Bentz M, Emmerich B, Dohner H, Stilgenbauer S, Hallek M. Prognostic model for newly diagnosed CLL patients in Binet stage A: results of the multicenter, prospective CLL1 trial of the German CLL study group. Leukemia. 2020 Apr;34(4):1038-1051. doi: 10.1038/s41375-020-0727-y. Epub 2020 Feb 10.

  • Langerbeins P, Giza A, Robrecht S, Cramer P, von Tresckow J, Al-Sawaf O, Fink AM, Furstenau M, Kutsch N, Simon F, Goede V, Hoechstetter M, Niemann CU, da Cunha-Bang C, Kater A, Dubois J, Gregor M, Staber PB, Tausch E, Schneider C, Stilgenbauer S, Eichhorst B, Fischer K, Hallek M. Reassessing the chronic lymphocytic leukemia International Prognostic Index in the era of targeted therapies. Blood. 2024 Jun 20;143(25):2588-2598. doi: 10.1182/blood.2023022564.

  • Jaramillo S, Agathangelidis A, Schneider C, Bahlo J, Robrecht S, Tausch E, Bloehdorn J, Hoechstetter M, Fischer K, Eichhorst B, Goede V, Hallek M, Dohner H, Rosenquist R, Ghia P, Stamatopoulos K, Stilgenbauer S. Prognostic impact of prevalent chronic lymphocytic leukemia stereotyped subsets: analysis within prospective clinical trials of the German CLL Study Group (GCLLSG). Haematologica. 2020 Nov 1;105(11):2598-2607. doi: 10.3324/haematol.2019.231027.

  • Kreuzberger N, Damen JA, Trivella M, Estcourt LJ, Aldin A, Umlauff L, Vazquez-Montes MD, Wolff R, Moons KG, Monsef I, Foroutan F, Kreuzer KA, Skoetz N. Prognostic models for newly-diagnosed chronic lymphocytic leukaemia in adults: a systematic review and meta-analysis. Cochrane Database Syst Rev. 2020 Jul 31;7(7):CD012022. doi: 10.1002/14651858.CD012022.pub2.

  • Pflug N, Bahlo J, Shanafelt TD, Eichhorst BF, Bergmann MA, Elter T, Bauer K, Malchau G, Rabe KG, Stilgenbauer S, Dohner H, Jager U, Eckart MJ, Hopfinger G, Busch R, Fink AM, Wendtner CM, Fischer K, Kay NE, Hallek M. Development of a comprehensive prognostic index for patients with chronic lymphocytic leukemia. Blood. 2014 Jul 3;124(1):49-62. doi: 10.1182/blood-2014-02-556399. Epub 2014 May 5.

MeSH Terms

Conditions

Leukemia, Lymphocytic, Chronic, B-Cell

Interventions

fludarabine

Condition Hierarchy (Ancestors)

Leukemia, B-CellLeukemia, LymphoidLeukemiaNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic DiseasesLymphoproliferative DisordersLymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Study Officials

  • Michael Hallek, MD

    Medizinische Universitaetsklinik I at the University of Cologne

    STUDY CHAIR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 6, 2005

First Posted

December 7, 2005

Study Start

April 1, 1997

Primary Completion

December 1, 2004

Study Completion

June 1, 2010

Last Updated

February 20, 2020

Record last verified: 2020-02

Data Sharing

IPD Sharing
Will not share

Locations