NCT00241189

Brief Summary

This is a study to determine the safety of the immunosuppressive rapamycin in patients with systemic sclerosis with diffuse cutaneous scleroderma. The effects (both good and bad) are being compared to another group of systemic sclerosis patients receiving methotrexate

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
17

participants targeted

Target at below P25 for phase_1

Timeline
Completed

Started Aug 2002

Longer than P75 for phase_1

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

August 1, 2002

Completed
3.2 years until next milestone

First Submitted

Initial submission to the registry

October 14, 2005

Completed
4 days until next milestone

First Posted

Study publicly available on registry

October 18, 2005

Completed
8 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2006

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2006

Completed
Last Updated

April 11, 2016

Status Verified

April 1, 2016

Enrollment Period

3.8 years

First QC Date

October 14, 2005

Last Update Submit

April 8, 2016

Conditions

Keywords

Systemic sclerosisSclerodermaRapamycinMethotrexate

Outcome Measures

Primary Outcomes (2)

  • Adverse events

  • Modified Rodnan Skin thickness score

Secondary Outcomes (11)

  • Forced vital capacity

  • Diffusing capacity (DLCO)

  • Health Assessment Questionnaire-Disability Index

  • Mahler Dyspnea Index

  • Medical Outcomes Questionnaire SF-36

  • +6 more secondary outcomes

Study Arms (2)

Rapamycin

EXPERIMENTAL

Patients take oral rapamycin 6 mg daily (and dose adjusted to keep a serum trough level of 5-15 ng/ml) for one year

Drug: rapamycin

Methotrexate

ACTIVE COMPARATOR

Methotrexate 20 mg taken orally weekly for one year

Drug: methotrexate

Interventions

Also known as: rapimmune
Rapamycin
Methotrexate

Eligibility Criteria

Age18 Years - 70 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Satisfy American College of Rheumatology classification criteria for systemic sclerosis
  • Have skin thickening proximal to the elbows and/or knees (diffuse scleroderma)
  • Cutaneous involvement for less than 5 years from the onset of the first non-Raynaud's manifestation

You may not qualify if:

  • Severe intractable malabsorption
  • Chronic debilitation from any underlying disease
  • Off putative disease modifying therapies for one month prior to entry

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Philip Clements, MD

Los Angeles, California, 90095-1670, United States

Location

Related Publications (1)

  • Su TI, Khanna D, Furst DE, Danovitch G, Burger C, Maranian P, Clements PJ. Rapamycin versus methotrexate in early diffuse systemic sclerosis: results from a randomized, single-blind pilot study. Arthritis Rheum. 2009 Dec;60(12):3821-30. doi: 10.1002/art.24986.

MeSH Terms

Conditions

Scleroderma, SystemicScleroderma, Diffuse

Interventions

SirolimusMethotrexate

Condition Hierarchy (Ancestors)

Connective Tissue DiseasesSkin and Connective Tissue DiseasesSkin Diseases

Intervention Hierarchy (Ancestors)

MacrolidesLactonesOrganic ChemicalsAminopterinPterinsPteridinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic Compounds

Study Officials

  • Philip J Clements, MD, MPH

    University of California, Los Angeles

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
SINGLE
Who Masked
INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
MD, MPH

Study Record Dates

First Submitted

October 14, 2005

First Posted

October 18, 2005

Study Start

August 1, 2002

Primary Completion

June 1, 2006

Study Completion

June 1, 2006

Last Updated

April 11, 2016

Record last verified: 2016-04

Locations