NCT00212758

Brief Summary

Treatment with growth hormone (GH; a hormone made by the body that stimulates growth) has been shown to be helpful in treating children with chronic kidney disease who fail to grow. The amount of growth that is seen in children treated with growth hormone varies widely for unknown reasons. Growth hormone works by producing another hormone in the liver called insulin-like growth factor-1, or IGF-1 for short. IGF-1 stimulates the bones to grow. The amount of IGF-1 in the blood may directly affect the amount of growth in each child. At this time, growth hormone therapy in children depends on giving a certain dose of growth hormone for each child based on his or her weight. If after 3-6 months on this dose of growth hormone the change in height is not enough, then the dose of growth hormone is increased until enough growth is seen. This method of dosing of growth hormone may take a long time and is complicated and time-consuming. The purpose of this study is to measure the amount of IGF-1 produced by the body as a result of giving 2 different doses of growth hormone in children for 7 days only. The study investigator hopes to find the most favorable level of IGF-1 generated after 7 days of growth hormone that correlates with good growth of children with kidney disease. Then instead of dosing growth hormone by weight, like is done now, researchers can dose growth hormone by the amount of IGF-1 that the body produces. Being able to dose more effectively will save valuable time for the child to grow and will shorten the overall duration of growth hormone therapy. The investigators will also determine the effect of inflammatory cytokines Il-6 and TNF-alpha on growth hormone insensitivity and hence IGF-1 generation test in the same population.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
17

participants targeted

Target at below P25 for phase_4

Timeline
Completed

Started Jan 2005

Longer than P75 for phase_4

Geographic Reach
1 country

8 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 1, 2005

Completed
9 months until next milestone

First Submitted

Initial submission to the registry

September 14, 2005

Completed
7 days until next milestone

First Posted

Study publicly available on registry

September 21, 2005

Completed
2.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2008

Completed
2 years until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2010

Completed
1.5 years until next milestone

Results Posted

Study results publicly available

October 26, 2011

Completed
Last Updated

October 26, 2011

Status Verified

October 1, 2011

Enrollment Period

3.3 years

First QC Date

September 14, 2005

Results QC Date

July 22, 2011

Last Update Submit

October 22, 2011

Conditions

Keywords

Short staturechildrenkidney failure, chronicGrowth

Outcome Measures

Primary Outcomes (1)

  • The Change in Amount of Insulin Like Growth Factor (IGF-I) Generated (Day 8-day 1)

    We will measure the amount of serum IGF-I generated after 7 days of growth hormone therapy (Day8-Day1).

    Day 1 & Day 8

Secondary Outcomes (1)

  • Change in Height at 56 Weeks

    week 1, week 56

Study Arms (2)

Low- Standard GH dose

ACTIVE COMPARATOR

This arm will receive Low dose of growth hormone (GH) (Nutropin AQ), for 7 days in a cross over design. Low dose GH will be 0.025 mg/kg/day. This will be followed by 2 weeks of wash out, then subjects will receive and the standard dose of Nutropin AQ (GH) at 0.05 mg/kg/dose given subcutaneously for another 7 days. IGF-I levels are measured after 7 days of the Low and the Standard dose of GH. After that all subjects will be treated with the standard dose of GH therapy of 0.05 mg/kg/day for 6 months and re-evaluated. If growth is adequate then subjects will continue on standard dose of GH for another 6 months for a total of 12 months.

Drug: Nutropin AQ

Standard-Low GH dose (7 Days)

ACTIVE COMPARATOR

This arm will receive Standard dose of growth hormone (GH) (Nutropin AQ), for 7 days in a cross over design. Standard dose GH will be 0.5 mg/kg/day. This will be followed by 2 weeks of wash out, then subjects will receive and the Low dose of Nutropin AQ (GH) at 0.025 mg/kg/dose given subcutaneously for another 7 days. IGF-I levels are measured after 7 days of the Low and the Standard dose of GH. After that all subjects will be treated with the standard dose of GH therapy of 0.05 mg/kg/day for 6 months and re-evaluated. If growth is adequate then subjects will continue on standard dose of GH for another 6 months for a total of 12 months.

Drug: Nutropin AQ

Interventions

Nutropin AQ

Also known as: Growth hormone
Low- Standard GH doseStandard-Low GH dose (7 Days)

Eligibility Criteria

Age2 Years - 18 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Males and females between 2-18 years of age with chronic renal failure.
  • Estimated creatinine clearance between 25-75 ml/min/1.73 m2 calculated by the Schwartz formula.
  • Height standard deviation score (SDS) more than -1.88 or annual height velocity SD of more than -2.0 for age and sex for the preceding 6 months.
  • No history of growth hormone therapy.
  • Bone age less than 16 years for boys and less than 13 years for girls.
  • Subjects with chronic kidney failure who are off steroid therapy or other drugs that interfere with growth for at least 6 months.

You may not qualify if:

  • Subjects on dialysis and kidney transplant recipients.
  • Patients with significant renal osteodystrophy or an intact parathyroid (PTH) level more than 500 pg/ml over the last 3 months prior to enrollment.
  • Diabetes mellitus.
  • History of malignancy.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (8)

Loma Linda UMC & Children's Hospital

Loma Linda, California, 92350, United States

Location

University of California in Los Angeles (UCLA)

Los Angeles, California, 90095-1752, United States

Location

Stanford University Medical Center

Stanford, California, 94305-5208, United States

Location

Legacy Emanuel Children's Hospital

Portland, Oregon, 97227, United States

Location

Oregon Health & Science University

Portland, Oregon, 97239, United States

Location

Texas Children's Hospital

Houston, Texas, 77030, United States

Location

UT Houston Medical School

Houston, Texas, 77030, United States

Location

University of Washington, Children's Hospital & Regional Medical Center

Seattle, Washington, 98105, United States

Location

Related Publications (2)

  • Buckway CK, Guevara-Aguirre J, Pratt KL, Burren CP, Rosenfeld RG. The IGF-I generation test revisited: a marker of GH sensitivity. J Clin Endocrinol Metab. 2001 Nov;86(11):5176-83. doi: 10.1210/jcem.86.11.8019.

    PMID: 11701674BACKGROUND
  • Al-Uzri A, Swinford RD, Nguyen T, Jenkins R, Gunsul A, Kachan-Liu SS, Rosenfeld R. The utility of the IGF-I generation test in children with chronic kidney disease. Pediatr Nephrol. 2013 Dec;28(12):2323-33. doi: 10.1007/s00467-013-2570-0. Epub 2013 Sep 7.

MeSH Terms

Conditions

Kidney Failure, ChronicDwarfism, PituitaryDwarfism

Interventions

Growth Hormone

Condition Hierarchy (Ancestors)

Renal Insufficiency, ChronicRenal InsufficiencyKidney DiseasesUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and SymptomsBone Diseases, DevelopmentalBone DiseasesMusculoskeletal DiseasesBone Diseases, EndocrineHypopituitarismPituitary DiseasesHypothalamic DiseasesBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesEndocrine System DiseasesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and Abnormalities

Intervention Hierarchy (Ancestors)

Pituitary Hormones, AnteriorPituitary HormonesPeptide HormonesHormonesHormones, Hormone Substitutes, and Hormone AntagonistsPeptidesAmino Acids, Peptides, and Proteins

Limitations and Caveats

Slow enrollment and the small number of participants in the study is the main limitation.

Results Point of Contact

Title
Dr. Amira Al-Uzri
Organization
Oregon Health & Science University

Study Officials

  • Amira Y Al-Uzri, M.D.

    Oregon Health and Science University

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
LTE60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 4
Allocation
RANDOMIZED
Masking
NONE
Purpose
DIAGNOSTIC
Intervention Model
CROSSOVER
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Associate Professor

Study Record Dates

First Submitted

September 14, 2005

First Posted

September 21, 2005

Study Start

January 1, 2005

Primary Completion

May 1, 2008

Study Completion

May 1, 2010

Last Updated

October 26, 2011

Results First Posted

October 26, 2011

Record last verified: 2011-10

Locations