NCT00207857

Brief Summary

Nearly all patients with Duchenne's Muscular Dystrophy (DMD) have scoliosis. Posterior instrumented spinal fusion, which is a surgery to correct scoliosis, has been shown to improve quality of life and satisfaction of both parents and families. The progressive muscular weakness leads to the development of scoliosis soon after the child has become unable to walk. The muscular weakness and scoliosis also affect the pulmonary function of these children. Pulmonary Function Tests (PFT) have been used to determine "pulmonary fitness" prior to surgery as a way to determine how well or if the child will tolerate surgery. Children with poor results on the PFT are determined to be too fragile to tolerate such a large operation. The physicians conducting this study feel that the PFT may be inaccurate and that this may not be the best single test to determine "pulmonary fitness". The physicians conducting the study think things like the time of day the study is done, how tired you are when you complete the test, and how well you understand the test may affect the results of the test.

Trial Health

30
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Timeline
Completed

Started Mar 2004

Geographic Reach
1 country

1 active site

Status
withdrawn

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

March 1, 2004

Completed
1.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 1, 2005

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

August 1, 2005

Completed
1 month until next milestone

First Submitted

Initial submission to the registry

September 13, 2005

Completed
8 days until next milestone

First Posted

Study publicly available on registry

September 21, 2005

Completed
Last Updated

February 4, 2015

Status Verified

February 1, 2015

Enrollment Period

1.4 years

First QC Date

September 13, 2005

Last Update Submit

February 2, 2015

Conditions

Keywords

Duchenne's Muscular DystrophyScoliosis

Outcome Measures

Primary Outcomes (1)

  • PFT training

    2 weeks

Study Arms (1)

With and Without PFTs

Eligibility Criteria

Age6 Years - 21 Years
Sexmale
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Male
  • Duchenne's Muscular Dystrophy with diagnosed confirmed by a neurologist
  • No longer able to ambulate for any meaningful amount of time
  • No previous spinal operation

You may not qualify if:

  • Any other type of muscular dystrophy or spinal muscular atrophy
  • Tracheotomy
  • Contractures of the upper extremities that would preclude using arm span as an estimation for height
  • Previous spinal surgery
  • Asthma, recurrent pneumonia, or other chronic lung disease

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Children's Healthcare of Atlanta @ Scottish Rite

Atlanta, Georgia, 30342, United States

Location

MeSH Terms

Conditions

Muscular Dystrophy, DuchenneScoliosis

Condition Hierarchy (Ancestors)

Muscular DystrophiesMuscular Disorders, AtrophicMuscular DiseasesMusculoskeletal DiseasesNeuromuscular DiseasesNervous System DiseasesGenetic Diseases, X-LinkedGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesSpinal CurvaturesSpinal DiseasesBone Diseases

Study Officials

  • Tim Schrader, MD

    Children's Orthopaedics of Atlanta

    PRINCIPAL INVESTIGATOR
0

Study Design

Study Type
observational
Time Perspective
PROSPECTIVE
Sponsor Type
OTHER

Study Record Dates

First Submitted

September 13, 2005

First Posted

September 21, 2005

Study Start

March 1, 2004

Primary Completion

August 1, 2005

Study Completion

August 1, 2005

Last Updated

February 4, 2015

Record last verified: 2015-02

Locations