NCT00202436

Brief Summary

In this project we plan to evaluate the effectiveness of erythrocytapheresis against phlebotomy, both regarding the impact on the reduction in iron overload as well as reduction in patient "burden". Aspects of cost effectiveness will be included in the final analysis. Results of the study would allow decision-making based on Evidence Based Medicine on the "best" therapeutic options available for newly-diagnosed as well as existing primary hemochromatosis patients.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
40

participants targeted

Target at below P25 for phase_3

Timeline
Completed

Started Oct 2004

Longer than P75 for phase_3

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

October 1, 2004

Completed
12 months until next milestone

First Submitted

Initial submission to the registry

September 13, 2005

Completed
7 days until next milestone

First Posted

Study publicly available on registry

September 20, 2005

Completed
3.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2008

Completed
9 months until next milestone

Study Completion

Last participant's last visit for all outcomes

September 1, 2009

Completed
Last Updated

October 20, 2009

Status Verified

October 1, 2009

Enrollment Period

4.2 years

First QC Date

September 13, 2005

Last Update Submit

October 19, 2009

Conditions

Outcome Measures

Primary Outcomes (1)

  • Treatment duration and number of treatments

    Ferritine value 50 microgr/l

Secondary Outcomes (1)

  • Decline in hemoglobin levels, restitution in liver functions, patient discomfort en costs

    Ferritine value 50microgr/l

Study Arms (2)

1

ACTIVE COMPARATOR

Phlebotomy

Procedure: PhlebotomyProcedure: Erythrocytapheresis

2

ACTIVE COMPARATOR

Erythrocytapheresis

Procedure: PhlebotomyProcedure: Erythrocytapheresis

Interventions

PhlebotomyPROCEDURE

Removal of 500 ml whole blood

Also known as: Bloodletting
12

machinal removal of erythrocytes

Also known as: Therapeutic erythrocytapheresis
12

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Hereditary haemochromatosis patients

You may not qualify if:

  • Malignancies, severe arrhythmias, congestive heart failure and/or recent angina, severe liver disease, epileptic seizures preceding in last 3 months before planned treatment

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Sanquin Blood Bank Southeast Region

Maastricht, 6229 GR, Netherlands

Location

Related Publications (2)

  • Rombout-Sestrienkova E, Winkens B, van Kraaij M, van Deursen CTBM, Janssen MCH, Rennings AMJ, Evers D, Kerkhoffs JL, Masclee A, Koek GH. A predictive model for estimating the number of erythrocytapheresis or phlebotomy treatments for patients with naive hereditary hemochromatosis. J Clin Apher. 2021 Jun;36(3):340-347. doi: 10.1002/jca.21867. Epub 2020 Dec 24.

  • Rombout-Sestrienkova E, Nieman FH, Essers BA, van Noord PA, Janssen MC, van Deursen CT, Bos LP, Rombout F, van den Braak R, de Leeuw PW, Koek GH. Erythrocytapheresis versus phlebotomy in the initial treatment of HFE hemochromatosis patients: results from a randomized trial. Transfusion. 2012 Mar;52(3):470-7. doi: 10.1111/j.1537-2995.2011.03292.x. Epub 2011 Aug 16.

MeSH Terms

Conditions

Hemochromatosis

Interventions

PhlebotomyBloodletting

Condition Hierarchy (Ancestors)

Metal Metabolism, Inborn ErrorsMetabolism, Inborn ErrorsGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesIron OverloadIron Metabolism DisordersMetabolic DiseasesNutritional and Metabolic Diseases

Intervention Hierarchy (Ancestors)

Blood Specimen CollectionSpecimen HandlingClinical Laboratory TechniquesDiagnostic Techniques and ProceduresDiagnosisPuncturesTherapeuticsSurgical Procedures, OperativeInvestigative Techniques

Study Officials

  • Eva Rombout, MD

    Sanquin Research and Blood Bank Divisions

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
SINGLE
Who Masked
OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER

Study Record Dates

First Submitted

September 13, 2005

First Posted

September 20, 2005

Study Start

October 1, 2004

Primary Completion

December 1, 2008

Study Completion

September 1, 2009

Last Updated

October 20, 2009

Record last verified: 2009-10

Locations