NCT00124709

Brief Summary

This study consists of a 3-year double-blind phase during which patients will receive atopic dermatitis (AD) treatment either with pimecrolimus cream 1% long-term management (LTM) or with a conventional corticosteroid-based treatment (1:1 ratio), followed by a 2 to 3-year open-label (OL) phase (all patients receiving pimecrolimus cream 1% LTM). At the end of the double-blind phase, the two treatment groups will be compared with respect to their efficacy in controlling AD; at the end of the OL phase, the incidence of asthma at the age of 6 years will be compared.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
1,091

participants targeted

Target at P75+ for phase_4

Timeline
Completed

Started Oct 2003

Longer than P75 for phase_4

Geographic Reach
1 country

36 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

October 1, 2003

Completed
1.8 years until next milestone

First Submitted

Initial submission to the registry

July 26, 2005

Completed
2 days until next milestone

First Posted

Study publicly available on registry

July 28, 2005

Completed
2.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 1, 2008

Completed
10 months until next milestone

Study Completion

Last participant's last visit for all outcomes

November 1, 2008

Completed
2.4 years until next milestone

Results Posted

Study results publicly available

March 23, 2011

Completed
Last Updated

March 23, 2011

Status Verified

February 1, 2011

Enrollment Period

4.3 years

First QC Date

July 26, 2005

Results QC Date

December 8, 2010

Last Update Submit

February 25, 2011

Conditions

Keywords

Atopic, dermatitis, asthma, children, modificationAtopic dermatitis/atopy

Outcome Measures

Primary Outcomes (2)

  • Atopic Dermatitis (AD) Disease Control Over 36 Months

    Proportion of disease-free days in Step 2 or less (per Patient) using total number of days in study as the denominator- double-blind phase. Intent to Treat Population: defined as all randomized patients who were dispensed study medication and had at least one post baseline efficacy measurement.

    36 months

  • Effect of Early Use of Pimecrolimus Cream 1% in Reducing the Incidence of Asthma at 6 Years of Age

    Note: The results for this efficacy variable are not reported due to early termination of the study.

    6 years

Secondary Outcomes (5)

  • Long Term Safety in Infants and Young Children

    6 years

  • Incidence of Allergic Rhinitis, Allergic Conjunctivitis and Food Allergies

    6 years (36 month Double-Blind Phase)

  • Corticosteroid and Pimecrolimus Drug Use

    48 months

  • Atopic Dermatitis (AD) Remission Time

    36 month Double-Blind Phase

  • Patient/Caregiver Quality of Life

    From Baseline to Visit 5 , 6, 8, 10, 12, and 14

Study Arms (2)

1

EXPERIMENTAL

Pimecrolimus

Drug: Pimecrolimus

2

ACTIVE COMPARATOR

Corticosteroid

Drug: Corticosteroid

Interventions

Pimecrolimus cream 1 %

Also known as: Elidel
1

conventional corticosteroid-based treatment

2

Eligibility Criteria

Age3 Months - 18 Months
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Diagnosis of atopic dermatitis
  • Family history of atopy
  • to 18 months of age at baseline
  • At least mild atopic dermatitis at baseline (investigator global assessment \[IGA\] greater or equal to 2)
  • Clinical evidence of atopic dermatitis for no longer than 3 months

You may not qualify if:

  • Diagnosis of or substantial clinical evidence for food or other allergies at baseline
  • Other protocol related criteria may apply

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (36)

Alabama Allergy and Asthma Center

Birmingham, Alabama, 35209, United States

Location

Northwest Arkansas Pediatric Clinic, P.A.

Fayetteville, Arkansas, 72703, United States

Location

The Children's Clinic of Jonesboro

Jonesboro, Arkansas, 72401, United States

Location

Southern California Research

Mission Viejo, California, 92691, United States

Location

Children's Hospital of Orange County

Orange, California, 92868, United States

Location

Stanford Dermatology Clinic and Clinical Trials Dept

Redwood City, California, 94063, United States

Location

Capital Allergy Respiratory Disease Center

Sacramento, California, 95819, United States

Location

Children's Hospital San Diego

San Diego, California, 92123, United States

Location

Allergy and Asthma Medical Group of Diablo Valley, Inc./ Clinical Research Division

Walnut Creek, California, 94598, United States

Location

National Jewish Medical and Research Center

Denver, Colorado, 80206, United States

Location

Dermatology Associates and Research

Coral Gables, Florida, 33134, United States

Location

Emerald Coast Clinical Research

Pensacola, Florida, 32503, United States

Location

Children's Memorial Hospital

Chicago, Illinois, 60614, United States

Location

Indiana University Outpatient Clinical Research

Indianapolis, Indiana, 46202, United States

Location

Central Kentucky Research Associates

Lexington, Kentucky, 40509, United States

Location

Dermatology Specialists

Louisville, Kentucky, 40202, United States

Location

Rx R & D

Metarie, Louisiana, 70002, United States

Location

Johns Hopkins Hospital

Baltimore, Maryland, 21287, United States

Location

Children's Hospital - Boston

Boston, Massachusetts, 02115, United States

Location

Dermatology, PLLC

Ann Arbor, Michigan, 48103, United States

Location

Mayo Clinic Rochester

Rochester, Minnesota, 55905, United States

Location

Central Dermatology

St Louis, Missouri, 63117, United States

Location

Skin Specialists, P.C.

Omaha, Nebraska, 68144, United States

Location

Dartmouth-Hitchcock Medical Center/Dermatology Section

Lebanon, New Hampshire, 03756, United States

Location

Children's Medical Group

Hopewell Junction, New York, 12533, United States

Location

Dermatology Associates of St. Luke's - Roosevelt

New York, New York, 10025, United States

Location

Calcagno Research and Development

Gresham, Oregon, 97030, United States

Location

Oregon Health Science University - Dermatology Dept.

Portland, Oregon, 97201, United States

Location

The Childrens' Hospital of Philadelphia

Philadelphia, Pennsylvania, 19104, United States

Location

Allegheny General Hospital

Pittsburgh, Pennsylvania, 15212, United States

Location

Tennessee Clinical Research Center

Nashville, Tennessee, 37215, United States

Location

Texas Children's Hospital, BCM

Houston, Texas, 77030, United States

Location

Alpine Medical Group, LLC

Salt Lake City, Utah, 84102, United States

Location

Granger Medical Clinic

West Valley City, Utah, 84120, United States

Location

Virginia Clinical Research

Norfolk, Virginia, 23507, United States

Location

Asthma Inc

Seattle, Washington, 98105, United States

Location

Related Publications (1)

  • Spergel JM, Boguniewicz M, Schneider L, Hanifin JM, Paller AS, Eichenfield LF. Food Allergy in Infants With Atopic Dermatitis: Limitations of Food-Specific IgE Measurements. Pediatrics. 2015 Dec;136(6):e1530-8. doi: 10.1542/peds.2015-1444.

MeSH Terms

Conditions

Dermatitis, AtopicDermatitisAsthma

Interventions

pimecrolimusAdrenal Cortex Hormones

Condition Hierarchy (Ancestors)

Skin Diseases, GeneticGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesSkin DiseasesSkin and Connective Tissue DiseasesSkin Diseases, EczematousHypersensitivity, ImmediateHypersensitivityImmune System DiseasesBronchial DiseasesRespiratory Tract DiseasesLung Diseases, ObstructiveLung DiseasesRespiratory Hypersensitivity

Intervention Hierarchy (Ancestors)

HormonesHormones, Hormone Substitutes, and Hormone Antagonists

Results Point of Contact

Title
Study Director
Organization
Novartis Pharmaceuticals

Study Officials

  • Novartis Pharmaceuticals

    Novartis Pharmaceuticals

    STUDY CHAIR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 4
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY

Study Record Dates

First Submitted

July 26, 2005

First Posted

July 28, 2005

Study Start

October 1, 2003

Primary Completion

January 1, 2008

Study Completion

November 1, 2008

Last Updated

March 23, 2011

Results First Posted

March 23, 2011

Record last verified: 2011-02

Locations