NCT00121667

Brief Summary

The purpose of this clinical research study is to learn whether Saxagliptin added to Metformin therapy is more effective than Metformin alone as a treatment for type 2 diabetic subjects who are not sufficiently controlled with Metformin alone

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
1,462

participants targeted

Target at P75+ for phase_3 diabetes-mellitus-type-2

Timeline
Completed

Started Aug 2005

Longer than P75 for phase_3 diabetes-mellitus-type-2

Geographic Reach
9 countries

152 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

July 18, 2005

Completed
3 days until next milestone

First Posted

Study publicly available on registry

July 21, 2005

Completed
11 days until next milestone

Study Start

First participant enrolled

August 1, 2005

Completed
1.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 1, 2006

Completed
3.3 years until next milestone

Study Completion

Last participant's last visit for all outcomes

February 1, 2010

Completed
1.2 years until next milestone

Results Posted

Study results publicly available

April 8, 2011

Completed
Last Updated

April 29, 2015

Status Verified

March 1, 2015

Enrollment Period

1.2 years

First QC Date

July 18, 2005

Results QC Date

March 15, 2011

Last Update Submit

April 8, 2015

Conditions

Outcome Measures

Primary Outcomes (1)

  • Baseline and Change From Baseline in Hemoglobin A1c (A1C) at Week 24

    Mean change from baseline is adjusted for baseline value.

    Baseline, Week 24

Secondary Outcomes (3)

  • Baseline and Change From Baseline in Fasting Plasma Glucose (FPG) at Week 24

    Baseline, Week 24

  • Percentage of Participants Achieving Therapeutic Glycemic Response (A1C < 7.0%) at Week 24

    Week 24

  • Baseline and Change From Baseline at Week 24 in Postprandial Glucose (PPG) Area Under the Curve (AUC)

    Baseline, Week 24

Other Outcomes (18)

  • Overall Summary of Adverse Events During ST+LT Treatment Period

    AEs: up to last treatment day + 1 day or last visit day in the ST+LT period; SAEs: up to last treatment day + 30 days or last visit day + 30 days in the LT+ST period. Mean duration of exposure: 124, 118, 130, 95 wks respectively for 2.5mg, 5mg, 10 mg, pla

  • Marked Laboratory Abnormalities - During ST + LT Treatment Period

    Lab assessments taken during and up to 14 days after the last dose of study drug during the ST + LT Treatment Period. Mean duration of exposure: 124, 118, 130, 95 weeks, respectively, for 2.5mg, 5mg, 10 mg, placebo.

  • Baseline and Changes From Baseline in Hemoglobin During the ST + LT Period

    Weeks 0, 2, 4, 6, 8, 10, 12, 14, 16, 18, 20, 22, 24, 30, 37, 50, 63, 76, 89, 102, 115, 128, 141, 154, 167, 180, 193, 206

  • +15 more other outcomes

Study Arms (4)

Saxagliptin + Metformin (A)

EXPERIMENTAL

Pioglitazone 15-45 mg (as needed for rescue)

Drug: Saxagliptin + MetforminDrug: Pioglitazone

Saxagliptin + Metformin (B)

EXPERIMENTAL

Pioglitazone 15-45 mg (as needed for rescue)

Drug: Saxagliptin + MetforminDrug: Pioglitazone

Saxagliptin + Metformin (C)

EXPERIMENTAL

Pioglitazone 15-45 mg (as needed for rescue)

Drug: Saxagliptin + MetforminDrug: Pioglitazone

Placebo+ Metformin (D)

PLACEBO COMPARATOR

Pioglitazone 15-45 mg (as needed for rescue)

Drug: Placebo + MetforminDrug: Pioglitazone

Interventions

Tablets, Oral, 2.5 mg Saxagliptin (plus flexible metformin dose), Once daily (24 weeks ST, 42 months LT)

Also known as: BMS-477118
Saxagliptin + Metformin (A)

Tablets, Oral, 0 mg, Once daily (24 weeks ST, 42 months LT)

Placebo+ Metformin (D)

Tablets, Oral, 15 - 45 mg (as needed for rescue)

Placebo+ Metformin (D)Saxagliptin + Metformin (A)Saxagliptin + Metformin (B)Saxagliptin + Metformin (C)

Eligibility Criteria

Age18 Years - 77 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Type 2 diabetes mellitus requiring treatment with at least 1500 mg but not greater than 2550 mg of a maximum tolerated dose of Metformin therapy for at least 8 weeks prior to screening.
  • HbA1c \>= 7.0% and \<= 10.0 %
  • Body mass index \<= 40 kg/m2
  • Fasting C-peptide \>= 1 ng/dL

You may not qualify if:

  • Symptomatic poorly controlled diabetes
  • Recent cardiac or cerebrovascular event
  • Serum creatinine \>= 1.5 mg/dL for males and \>= 1.4 mg/dL for females

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (152)

Local Institution

Anniston, Alabama, United States

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Birmingham, Alabama, United States

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Calera, Alabama, United States

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Haleyville, Alabama, United States

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Mesa, Arizona, United States

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Phoenix, Arizona, United States

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Jonesboro, Arkansas, United States

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Little Rock, Arkansas, United States

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Sherwood, Arkansas, United States

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Encino, California, United States

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Fountain Valley, California, United States

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Fresno, California, United States

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Los Angeles, California, United States

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Mission Viejo, California, United States

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Northridge, California, United States

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Orange, California, United States

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Roseville, California, United States

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Sacramento, California, United States

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Spring Valley, California, United States

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Tustin, California, United States

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Castle Rock, Colorado, United States

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Colorado Springs, Colorado, United States

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Denver, Colorado, United States

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Golden, Colorado, United States

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Loveland, Colorado, United States

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Altamonte Springs, Florida, United States

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Chipley, Florida, United States

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Cocoa Beach, Florida, United States

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Coral Gables, Florida, United States

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Fort Lauderdale, Florida, United States

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Jacksonville, Florida, United States

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Kissimmee, Florida, United States

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Marianna, Florida, United States

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Miami, Florida, United States

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New Port Richey, Florida, United States

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Ocala, Florida, United States

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Tallahassee, Florida, United States

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Tampa, Florida, United States

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Decatur, Georgia, United States

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Chicago, Illinois, United States

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Vernon Hills, Illinois, United States

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Elkhart, Indiana, United States

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Lafayette, Indiana, United States

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Iowa City, Iowa, United States

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Waterloo, Iowa, United States

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Topeka, Kansas, United States

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Lexington, Kentucky, United States

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Munfordville, Kentucky, United States

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New Orleans, Louisiana, United States

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West Monroe, Louisiana, United States

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Baltimore, Maryland, United States

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Chester, Maryland, United States

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Prince Frederick, Maryland, United States

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Boston, Massachusetts, United States

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Kansas City, Missouri, United States

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St Louis, Missouri, United States

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Kalispell, Montana, United States

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Omaha, Nebraska, United States

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Las Vegas, Nevada, United States

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Toms River, New Jersey, United States

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Albuquerque, New Mexico, United States

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Charlotte, North Carolina, United States

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Greensboro, North Carolina, United States

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Morehead City, North Carolina, United States

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Salisbury, North Carolina, United States

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Sparta, North Carolina, United States

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Wilmington, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Athens, Ohio, United States

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Columbus, Ohio, United States

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Lyndhurst, Ohio, United States

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Oklahoma City, Oklahoma, United States

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Tulsa, Oklahoma, United States

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Eugene, Oregon, United States

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Portland, Oregon, United States

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Carlisle, Pennsylvania, United States

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Langhorne, Pennsylvania, United States

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Levittown, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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Charleston, South Carolina, United States

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Duncan, South Carolina, United States

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Bristol, Tennessee, United States

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Austin, Texas, United States

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Bryan, Texas, United States

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Carrollton, Texas, United States

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Dallas, Texas, United States

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Houston, Texas, United States

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San Antonio, Texas, United States

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Temple, Texas, United States

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Salt Lake City, Utah, United States

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Hampton, Virginia, United States

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Virginia Beach, Virginia, United States

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Olympia, Washington, United States

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Spokane, Washington, United States

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Buenos Aires, Buenos Aires, Argentina

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Mar del Plata, Buenos Aires, Argentina

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Córdoba, Córdoba Province, Argentina

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Rosario, Santa Fe Province, Argentina

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Sydney, New South Wales, Australia

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Woollongong, New South Wales, Australia

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Brisbane, Queensland, Australia

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Kippa-Ring, Queensland, Australia

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Meadowbrook, Queensland, Australia

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Adelaide, South Australia, Australia

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Woodville South, South Australia, Australia

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Perth, Western Australia, Australia

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Fortaleza, Ceará, Brazil

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Belém, Pará, Brazil

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Porto Alegre, Rio Grande do Sul, Brazil

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Campinas, São Paulo, Brazil

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Marília, São Paulo, Brazil

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São Paulo, São Paulo, Brazil

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Calgary, Alberta, Canada

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Coquitlam, British Columbia, Canada

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Kelowna, British Columbia, Canada

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Surrey, British Columbia, Canada

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Brandon, Manitoba, Canada

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Portage la Prairie, Manitoba, Canada

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Winnipeg, Manitoba, Canada

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Bathurst, New Brunswick, Canada

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Mount Pearl, Newfoundland and Labrador, Canada

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St. John's, Newfoundland and Labrador, Canada

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Aylmer, Ontario, Canada

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London, Ontario, Canada

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Oakville, Ontario, Canada

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Sarnia, Ontario, Canada

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Thornhill, Ontario, Canada

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Toronto, Ontario, Canada

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Woodstock, Ontario, Canada

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Charlottetown, Prince Edward Island, Canada

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Drummondville, Quebec, Canada

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Fleurimont, Quebec, Canada

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Longueuil, Quebec, Canada

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Saint-Léonard, Quebec, Canada

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Saskatoon, Saskatchewan, Canada

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Santiago, Santiago Metropolitan, Chile

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Durango, Durango, Mexico

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Celaya, Guanajuato, Mexico

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Guadalajara, Jalisco, Mexico

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Distrito Federal, Mexico City, Mexico

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Morelia, Michioacan, Mexico

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Monterrey, Nuevo León, Mexico

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Hermosillo, Sonora, Mexico

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Mérida, Yucatán, Mexico

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Carolina, Puerto Rico

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Ponce, Puerto Rico

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Rio Pieoras, Puerto Rico

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San Juan, Puerto Rico

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Hualien City, Taiwan

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Taichung, Taiwan

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Taipei, Taiwan

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Related Publications (7)

  • DeFronzo RA, Hissa MN, Garber AJ, Luiz Gross J, Yuyan Duan R, Ravichandran S, Chen RS; Saxagliptin 014 Study Group. The efficacy and safety of saxagliptin when added to metformin therapy in patients with inadequately controlled type 2 diabetes with metformin alone. Diabetes Care. 2009 Sep;32(9):1649-55. doi: 10.2337/dc08-1984. Epub 2009 May 28.

    PMID: 19478198BACKGROUND
  • Bailey CJ, Del Prato S, Wei C, Reyner D, Saraiva G. Durability of glycaemic control with dapagliflozin, an SGLT2 inhibitor, compared with saxagliptin, a DPP4 inhibitor, in patients with inadequately controlled type 2 diabetes. Diabetes Obes Metab. 2019 Nov;21(11):2564-2569. doi: 10.1111/dom.13841. Epub 2019 Aug 26.

  • Perl S, Cook W, Wei C, Iqbal N, Hirshberg B. Saxagliptin Efficacy and Safety in Patients With Type 2 Diabetes and Moderate Renal Impairment. Diabetes Ther. 2016 Sep;7(3):527-35. doi: 10.1007/s13300-016-0184-9. Epub 2016 Jul 11.

  • Bonora E, Bryzinski B, Hirshberg B, Cook W. A post hoc analysis of saxagliptin efficacy and safety in patients with type 2 diabetes stratified by UKPDS 10-year cardiovascular risk score. Nutr Metab Cardiovasc Dis. 2016 May;26(5):374-9. doi: 10.1016/j.numecd.2015.11.004. Epub 2015 Dec 1.

  • Rosenstock J, Gross JL, Aguilar-Salinas C, Hissa M, Berglind N, Ravichandran S, Fleming D. Long-term 4-year safety of saxagliptin in drug-naive and metformin-treated patients with Type 2 diabetes. Diabet Med. 2013 Dec;30(12):1472-6. doi: 10.1111/dme.12267. Epub 2013 Jul 19.

  • Karyekar CS, Frederich R, Ravichandran S. Clinically relevant reductions in HbA1c without hypoglycaemia: results across four studies of saxagliptin. Int J Clin Pract. 2013 Aug;67(8):759-67. doi: 10.1111/ijcp.12212. Epub 2013 Jun 24.

  • Karyekar C, Donovan M, Allen E, Fleming D, Ravichandran S, Chen R. Efficacy and safety of saxagliptin combination therapy in US patients with type 2 diabetes. Postgrad Med. 2011 Jul;123(4):63-70. doi: 10.3810/pgm.2011.07.2305.

MeSH Terms

Conditions

Diabetes Mellitus, Type 2

Interventions

saxagliptinMetforminPioglitazone

Condition Hierarchy (Ancestors)

Diabetes MellitusGlucose Metabolism DisordersMetabolic DiseasesNutritional and Metabolic DiseasesEndocrine System Diseases

Intervention Hierarchy (Ancestors)

BiguanidesGuanidinesAmidinesOrganic ChemicalsThiazolidinedionesThiazolesSulfur CompoundsAzolesHeterocyclic Compounds, 1-RingHeterocyclic Compounds

Results Point of Contact

Title
Boaz Hirschberg
Organization
AstraZeneca Pharmaceuticals

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 18, 2005

First Posted

July 21, 2005

Study Start

August 1, 2005

Primary Completion

October 1, 2006

Study Completion

February 1, 2010

Last Updated

April 29, 2015

Results First Posted

April 8, 2011

Record last verified: 2015-03

Locations