NCT03199053

Brief Summary

The primary objective of this study is to determine if there will be a greater mean reduction from baseline in glycated hemoglobin (HbA1c) achieved after 26 weeks of oral double-blind add-on therapy of dapagliflozin or saxagliptin compared to placebo in paediatric T2DM patients with HbA1c levels of 6.5 to 10.5% on diet and exercise and metformin, insulin, or metformin plus insulin.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
256

participants targeted

Target at P25-P50 for phase_3 diabetes-mellitus-type-2

Timeline
Completed

Started Oct 2017

Longer than P75 for phase_3 diabetes-mellitus-type-2

Geographic Reach
23 countries

122 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 22, 2017

Completed
4 days until next milestone

First Posted

Study publicly available on registry

June 26, 2017

Completed
4 months until next milestone

Study Start

First participant enrolled

October 11, 2017

Completed
5.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 1, 2023

Completed
11 months until next milestone

Study Completion

Last participant's last visit for all outcomes

January 3, 2024

Completed
4 months until next milestone

Results Posted

Study results publicly available

April 17, 2024

Completed
Last Updated

June 21, 2024

Status Verified

May 1, 2024

Enrollment Period

5.3 years

First QC Date

June 22, 2017

Results QC Date

January 31, 2024

Last Update Submit

May 28, 2024

Conditions

Keywords

Type 2 Diabetes Mellitus

Outcome Measures

Primary Outcomes (2)

  • Dapagliflozin Versus Placebo: Adjusted Mean Change From Baseline in HbA1c at Week 26

    Data was analysed with an ANCOVA model with treatment, sex, age group and background antidiabetes medication as factors and Baseline HbA1c as covariate. Missing Week 26 data was handled based on multiple imputation washout (MI-WO) within each arm using the data from placebo participants with Week 26 data.

    Baseline and Week 26

  • Saxagliptin Versus Placebo: Adjusted Mean Change From Baseline in HbA1c at Week 26

    Data was analysed with an ANCOVA model with treatment, sex, age group and background antidiabetes medication as factors and Baseline HbA1c as covariate. Missing Week 26 data was handled based on MI-WO within each arm using the data from placebo participants with Week 26 data.

    Baseline and Week 26

Secondary Outcomes (17)

  • Dapagliflozin Low-dose/High-dose Versus Placebo (Weighted): Adjusted Mean Change From Baseline in HbA1c at Week 26

    Baseline and Week 26

  • Saxagliptin Low-dose/High-dose Versus Placebo (Weighted): Adjusted Mean Change From Baseline in HbA1c at Week 26

    Baseline and Week 26

  • Dapagliflozin Low-dose Versus Placebo (Weighted): Adjusted Mean Change From Baseline in HbA1c at Week 26

    Baseline and Week 26

  • Saxagliptin Low-dose Versus Placebo (Weighted): Adjusted Mean Change From Baseline in HbA1c at Week 26

    Baseline and Week 26

  • Dapagliflozin Versus Placebo: Adjusted Mean Change From Baseline in Fasting Plasma Glucose (FPG) at Week 26

    Baseline and Week 26

  • +12 more secondary outcomes

Study Arms (5)

Low dose Dapagliflozin

EXPERIMENTAL

Oral route. Start with a low dose of dapagliflozin administered once daily and remain on the low dose regardless of your HbA1c at week 12.

Drug: Dapagliflozin

Low dose/high dose Dapagliflozin

EXPERIMENTAL

Oral route. Start with a low dose of Dapagliflozin administered once daily and up titrate to the high dose Dapagliflozin administered once daily if HbA1c \>= 7% at week 12

Drug: Dapagliflozin

Low dose Saxagliptin

EXPERIMENTAL

Oral route. Start with a low dose of saxagliptin administered once daily and remain on the low dose regardless of your HbA1c at week 12

Drug: Saxagliptin

Low dose/high dose Saxagliptin

EXPERIMENTAL

Oral route. Start with a low dose of saxagliptin administered once daily and up titrate to the high dose if HbA1c \>= 7% at week 12

Drug: Saxagliptin

Placebo arm

PLACEBO COMPARATOR

Oral route. Placebo tablets administered for 52 weeks

Drug: Placebo

Interventions

Tablets, Oral, 5mg , Once daily Tablets, Oral, 10mg, Once daily

Also known as: Forxiga
Low dose DapagliflozinLow dose/high dose Dapagliflozin

Tablets, Oral, 2.5mg Once daily Tablets, Oral, 5mg, Once daily

Also known as: Onglyza
Low dose SaxagliptinLow dose/high dose Saxagliptin

Matching placebo to dapagliflozin 5mg and 10 mg/saxagliptin 2.5 mg and 5 mg, Tablets, oral, Once daily

Placebo arm

Eligibility Criteria

Age10 Years - 18 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Signed Written Informed Consent
  • Target Population
  • Previously diagnosed with Type 2 Diabetes Mellitus by World Health Organization/ADA criteria
  • HbA1c between 6.5% and 10.5% obtained at screening.
  • Currently on diet and exercise and stable dose of at least 1000 mg metformin (IR or XR) for a minimum of 8 weeks, or stable dose of insulin for a minimum of 8 weeks, or a stable combination of at least 1000 mg metformin (IR or XR) and insulin for a minimum of 8 weeks prior to randomization. For those children on insulin, investigators will confirm that attempts at removing insulin from the subject's therapeutic regimen had been previously made but had not been successful.
  • Age and Reproductive Status
  • Male and female patients eligible if 10 years of age, up to but not including 18 years of age at the time of enrollment/screening. At least 30% of total subjects will be between the ages of 10 and 14 years and at least one third, but no more than two thirds, female subjects.
  • Women of childbearing potential must have a negative pregnancy test within 24 hours prior to the start of study drug.
  • Women must not be breastfeeding.
  • Women of childbearing potential must agree to follow instructions for method(s) of contraception for the duration of treatment with study drugs: saxagliptin, and dapagliflozin, plus 5 half-lives of study drugs or 30 days (whichever is longer), plus 30 days (duration of ovulatory cycle) for a total of 60 days post treatment completion.

You may not qualify if:

  • Target Disease Exceptions
  • Presence of Type 1 diabetes, as demonstrated by Preexisting diagnosis of Type 1 diabetes,
  • Previous diagnosis of monogenic etiology of Type 2 diabetes
  • Diabetes ketoacidosis (DKA) within 6 months of screening
  • Current use of the following medications for the treatment of diabetes, or use within the specified timeframe prior to screening for the main study:
  • Eight weeks: sulfonylureas, alpha glucosidase inhibitors, metiglinide, oral or injectable incretins or incretin mimetics, other antidiabetes medications not otherwise specified.
  • Sixteen weeks: thiazolidinediones, DPP-4 inhibitors (with no reported medication related AEs related to DPP-4 inhibitors), sodium glucose cotransporter-2 (SGLT-2) inhibitors (with no reported medication related AEs related to SGLT-2 inhibitors)
  • Initiation or discontinuation of prescription or non-prescription weight loss drugs within 8 weeks of screening. Use of prescription or non-prescription weight loss drugs must be stable during the study.
  • Medical History and Concurrent Diseases
  • Pregnant, positive serum pregnancy test, planning to become pregnant during the clinical trials, or breastfeeding
  • History of unstable or rapidly progressive renal disease
  • History of unresolved vesico-ureteral reflux
  • History of or current, acute or chronic pancreatitis
  • History of hemoglobinopathy, with the exception of sickle cell trait or thalassemia minor; or chronic or recurrent hemolysis
  • Malignancy within 5 years of the screening visit (with the exception of treated basal cell or treated squamous cell carcinoma)
  • +18 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (122)

Research Site

Sacramento, California, 95821, United States

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New Haven, Connecticut, 06519, United States

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Hialeah, Florida, 33012, United States

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Hialeah, Florida, 33016, United States

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Hollywood, Florida, 33021, United States

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Miami, Florida, 33144, United States

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Miami, Florida, 33155, United States

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Miami, Florida, 33165, United States

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Miami Springs, Florida, 33166, United States

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Atlanta, Georgia, 30322, United States

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Atlanta, Georgia, 30341, United States

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Idaho Falls, Idaho, 83404, United States

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Neptune City, New Jersey, 07753, United States

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Memphis, Tennessee, 38116, United States

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Memphis, Tennessee, 38119, United States

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Edinburg, Texas, 78539, United States

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Harlingen, Texas, 78550, United States

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McAllen, Texas, 78503, United States

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San Antonio, Texas, 78229, United States

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Charlottesville, Virginia, 22903, United States

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Buenos Aires, 6500, Argentina

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Buenos Aires, C1180AAX, Argentina

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CABA, C1119ACN, Argentina

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Ciudad de Buenos Aires, C1405BCH, Argentina

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San Miguel de Tucumán, 4000, Argentina

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San Miguel de Tucumán, T4000IHE, Argentina

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Blacktown, 2148, Australia

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Brasília, 71625-009, Brazil

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Curitiba, 80810-040, Brazil

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Fortaleza, 60170-320, Brazil

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Fortaleza, 60430-270, Brazil

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Passo Fundo, 99010-080, Brazil

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Porto Alegre, 90430-001, Brazil

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Porto Alegre, 91350-250, Brazil

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Ribeirão Preto, 14051-104, Brazil

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Santa Maria, 97015-530, Brazil

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São Paulo, 01223-001, Brazil

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São Paulo, 05652-900, Brazil

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Montreal, Quebec, H1T 2M4, Canada

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Santiago, 7500710, Chile

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Armenia, 630004, Colombia

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Barranquilla, 80020, Colombia

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Tampere, 33520, Finland

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Ahmedabad, 380008, India

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Aurangabad, 431003, India

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Bangalore, 560002, India

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Bikaner, 334003, India

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Chandigarh, 160012, India

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Coimbatore, 641009, India

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Hyderabad, 500012, India

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Kolkata, 700054, India

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Kozhikode, 67300, India

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Nashik, 422002, India

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Pune, 411030, India

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Visakhapatnam, 531011, India

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Haifa, 3109601, Israel

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Ancona, 60123, Italy

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Napoli, 80138, Italy

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Roma, 00165, Italy

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George Town, 10450, Malaysia

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Ipoh, 30990, Malaysia

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Johor Bahru, 80100, Malaysia

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Klang, 41200, Malaysia

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Kota Kinabalu, 88996, Malaysia

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Kuala Lumpur, 50586, Malaysia

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Kuching, 93586, Malaysia

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Malacca, 75400, Malaysia

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Putrajaya, 62250, Malaysia

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Seremban, 70300, Malaysia

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Seri Manjung, 32040, Malaysia

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Taiping, 34000, Malaysia

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Boca del Rio, 94290, Mexico

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Celaya, 38000, Mexico

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Ciudad Madero, 89440, Mexico

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Cuernavaca, 62209, Mexico

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Cuernavaca, 62290, Mexico

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Culiacán, 80230, Mexico

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Durango, 34000, Mexico

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Guadalajara, 44150, Mexico

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Juriquilla, 76230, Mexico

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Mérida, 97000, Mexico

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México, 06700, Mexico

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México, D.F., 11410, Mexico

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Monterrey, 64460, Mexico

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Monterrey, 64620, Mexico

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San Juan del Río, 76800, Mexico

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Veracruz, 91900, Mexico

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Zapopan, 45116, Mexico

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Grafton, 1023, New Zealand

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Tauranga, 3110, New Zealand

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Wellington, 6021, New Zealand

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Quezon City, 1100, Philippines

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Quezon City, 1112, Philippines

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San Fernando City, 2000, Philippines

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Warsaw, 01-868, Poland

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Izhevsk, 426009, Russia

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Moscow, 125993, Russia

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Ufa, 450000, Russia

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Daejeon, 35233, South Korea

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Incheon, 22332, South Korea

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Wŏnju, 26426, South Korea

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Tainan, 704, Taiwan

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Taipei, 112, Taiwan

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Bangkok, 10400, Thailand

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Hat Yai, 90110, Thailand

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Aydin, 9010, Turkey (Türkiye)

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Bursa, 16059, Turkey (Türkiye)

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Eskişehir, 26480, Turkey (Türkiye)

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Istanbul, 34020, Turkey (Türkiye)

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Izmir, 35210, Turkey (Türkiye)

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Izmir, 35330, Turkey (Türkiye)

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Kocaeli, 41380, Turkey (Türkiye)

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Kurupelit, 55139, Turkey (Türkiye)

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Manisa, 45030, Turkey (Türkiye)

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Dnipro, 49023, Ukraine

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Kyiv, 01021, Ukraine

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Vinnytsia, 21010, Ukraine

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Birmingham, B4 6NH, United Kingdom

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London, E1 1BB, United Kingdom

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London, SE5 9RS, United Kingdom

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Middlesbrough, TS4 3BW, United Kingdom

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Nottingham, NG7 2UH, United Kingdom

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Related Publications (1)

  • Shehadeh N, Barrett T, Galassetti P, Karlsson C, Monyak J, Iqbal N, Tamborlane WV. Dapagliflozin or Saxagliptin in Pediatric Type 2 Diabetes. NEJM Evid. 2023 Dec;2(12):EVIDoa2300210. doi: 10.1056/EVIDoa2300210. Epub 2023 Oct 4.

Related Links

MeSH Terms

Conditions

Diabetes Mellitus, Type 2

Interventions

dapagliflozinsaxagliptin

Condition Hierarchy (Ancestors)

Diabetes MellitusGlucose Metabolism DisordersMetabolic DiseasesNutritional and Metabolic DiseasesEndocrine System Diseases

Limitations and Caveats

Due to legal dispute, the source documents could not be accessed for 11 participants at 1 site. All data from this site were excluded as documented in the statistical analysis plan.

Results Point of Contact

Title
Global Clinical Lead
Organization
AstraZeneca

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Masking Details
sponsor
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: Eligible subjects with HbA1c of 6.5% to 10.5% at screening will be randomized 1:1:1 to receive dapagliflozin 5 mg, saxagliptin 2.5 mg, or placebo. Blinded HbA1c assessment will be performed at Week 12. All subjects with Week 12 HbA1c \< 7% will remain on previously assigned randomized treatment. Subjects taking dapagliflozin with Week 12 HbA1c ≥ 7% will be re-randomized in a 1:1 ratio to continue on the low-dose treatment (dapagliflozin 5 mg) or up titrate to the high-dose treatment (dapagliflozin 10 mg). Subjects taking saxagliptin with Week 12 HbA1c ≥ 7% will be re-randomized in a 1:1 ratio to continue on the low-dose treatment (saxagliptin 2.5 mg) or up-titrate to the high-dose treatment (saxagliptin 5 mg). Subjects taking placebo with Week 12 HbA1c ≥ 7% will continue on placebo treatment. All placebo subjects and all subjects taking saxagliptin or dapagliflozin with HbA1c \< 7% at Week 12 will go through a dummy 2nd randomization process for maintaining the blinding.
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 22, 2017

First Posted

June 26, 2017

Study Start

October 11, 2017

Primary Completion

February 1, 2023

Study Completion

January 3, 2024

Last Updated

June 21, 2024

Results First Posted

April 17, 2024

Record last verified: 2024-05

Data Sharing

IPD Sharing
Will share

Qualified researchers can request access to anonymized individual patient-level data from AstraZeneca group of companies sponsored clinical trials via the request portal. All request will be evaluated as per the AZ disclosure commitment: https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure. Yes, indicates that AZ are accepting requests for IPD, but this does not mean all requests will be shared.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
AstraZeneca will meet or exceed data availability as per the commitments made to the EFPIA Pharma Data Sharing Principles. For details of our timelines, please rerefer to our disclosure commitment at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
Access Criteria
When a request has been approved AstraZeneca will provide access to the de-identified individual patient-level data in an approved sponsored tool . Signed Data Sharing Agreement (non-negotiable contract for data accessors) must be in place before accessing requested information. Additionally, all users will need to accept the terms and conditions of the SAS MSE to gain access. For additional details, please review the Disclosure Statements at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
More information

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