NCT00108953

Brief Summary

The purpose of this study is to evaluate the safety and efficacy of doxorubicin plus sorafenib versus doxorubicin plus placebo in patients with advanced hepatocellular carcinoma (HCC).

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
96

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Apr 2005

Typical duration for phase_2

Geographic Reach
6 countries

28 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

April 1, 2005

Completed
20 days until next milestone

First Submitted

Initial submission to the registry

April 21, 2005

Completed
1 day until next milestone

First Posted

Study publicly available on registry

April 22, 2005

Completed
2.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2008

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2008

Completed
1.2 years until next milestone

Results Posted

Study results publicly available

June 11, 2009

Completed
Last Updated

October 31, 2014

Status Verified

October 1, 2014

Enrollment Period

3 years

First QC Date

April 21, 2005

Results QC Date

April 23, 2009

Last Update Submit

October 24, 2014

Conditions

Keywords

CancerLiver CancerHepatocellular carcinomaHCC

Outcome Measures

Primary Outcomes (1)

  • Time to Progression (TTP)

    TTP was defined as the time from randomization to radiological disease progression by independent assessment.

    from date of randomization of the first patient until 3 years later

Secondary Outcomes (7)

  • Overall Survival

    from date of randomization of the first patient until 3 years later

  • Progression Free Survival (PFS)

    from date of randomization of the first patient until 3 years later

  • Percentage of Participants in Each Category of Best Tumor Response

    achieved during treatment or within 30 days after termination of active therapy

  • Time to Symptomatic Progression (TTSP)

    from date of randomization of the first patient until 3 years later

  • Duration of Response

    from date of randomization of the first patient until 3 years later

  • +2 more secondary outcomes

Study Arms (2)

Sorafenib + Doxorubicin

EXPERIMENTAL

"Sorafenib + Doxorubicin" -- combination therapy: Sorafenib (Nexavar, BAY43-9006) 200 mg tablets by mouth (orally) twice daily + doxorubicin 60 mg/m2 intravenous infusion every 21 days for 6 cycles (18 weeks)

Drug: Sorafenib (Nexavar, BAY43-9006) plus Doxorubicin

Placebo + Doxorubicin

ACTIVE COMPARATOR

"Placebo + Doxorubicin" -- monotherapy: Sorafenib (Nexavar, BAY43-9006) matching placebo tablets by mouth (orally) twice daily + doxorubicin 60 mg/m2 intravenous infusion every 21 days for 6 cycles (18 weeks)

Drug: Doxorubicin/Placebo

Interventions

Multi kinase inhibitor plus Chemotherapy

Sorafenib + Doxorubicin

Chemotherapy plus Placebo

Placebo + Doxorubicin

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients who have a life expectancy of at least 12 weeks
  • Patients with advanced HCC (unresectable, and/or metastatic) which has been histologically or cytologically documented
  • Patients must have at least one tumor lesion that meets both of the following criteria:
  • can be accurately measured in at least one dimension according to Response Evaluation Criteria in Solid Tumors (RECIST)
  • has not been previously treated with local therapy
  • Patients who have received local therapy except chemoembolization, such as surgery, radiation therapy, hepatic arterial embolization, radiofrequency ablation, percutaneous ethanol injection or cryoablation are eligible, provided that they either have a target lesion which has not been subjected to local therapy and/or the target lesion(s) within the field of the local therapy has shown an increase of 25% in the size. Local therapy must be completed at least 4 weeks prior to the baseline scan
  • Patients who have an Eastern Cooperative Oncology Group (ECOG) performance status of 0, 1 or 2

You may not qualify if:

  • Previous or concurrent cancer that is distinct in primary site or histology from HCC, EXCEPT cervical carcinoma in situ, treated basal cell carcinoma, and superficial bladder tumors (Ta, Tis \& T1). Any cancer curatively treated \> 3 years prior to entry is permitted
  • History of cardiac disease
  • Serious myocardial dysfunction
  • Active, clinically serious infections
  • Known history of Human Immunodeficiency Virus (HIV) infection
  • Known Central Nervous System (CNS) tumors including metastatic brain disease
  • Patients with clinically significant gastrointestinal bleeding within 30 days prior to study entry

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (28)

Unknown Facility

Birmingham, Alabama, 35294, United States

Location

Unknown Facility

Beverly Hills, California, 90211-1850, United States

Location

Unknown Facility

Orange, California, 92668-3298, United States

Location

Unknown Facility

Palo Alto, California, 94304-1207, United States

Location

Unknown Facility

San Francisco, California, 94115, United States

Location

Unknown Facility

San Francisco, California, 94121, United States

Location

Unknown Facility

Sylmar, California, 91342, United States

Location

Unknown Facility

Miami, Florida, 33136, United States

Location

Unknown Facility

Lafayette, Louisiana, 70506, United States

Location

Unknown Facility

Minneapolis, Minnesota, 55455, United States

Location

Unknown Facility

Hackensack, New Jersey, 07601, United States

Location

Unknown Facility

New York, New York, 10065, United States

Location

Unknown Facility

Rochester, New York, 14642, United States

Location

Unknown Facility

Nashville, Tennessee, 37203, United States

Location

Unknown Facility

Seattle, Washington, 98101, United States

Location

Unknown Facility

Buenos Aires, Ciudad Auton. de Buenos Aires, C1264AAA, Argentina

Location

Unknown Facility

Neuquén, Neuquén Province, Q8300HDH, Argentina

Location

Unknown Facility

Buenos Aires, Argentina

Location

Unknown Facility

Toronto, Ontario, M5G 2M9, Canada

Location

Unknown Facility

Hong Kong, Hong Kong, Hong Kong

Location

Unknown Facility

Kazan', 420111, Russia

Location

Unknown Facility

Kirov, 610002, Russia

Location

Unknown Facility

Krasnodar, 350040, Russia

Location

Unknown Facility

Maidstone, Kent, ME16 9QQ, United Kingdom

Location

Unknown Facility

London, London, W12 0HS, United Kingdom

Location

Unknown Facility

Manchester, Manchester, M20 4BX, United Kingdom

Location

Unknown Facility

Bebington, Merseyside, CH63 4JY, United Kingdom

Location

Unknown Facility

Birmingham, West Midlands, B15 2TT, United Kingdom

Location

Related Publications (2)

  • Abou-Alfa GK, Schwartz L, Ricci S, Amadori D, Santoro A, Figer A, De Greve J, Douillard JY, Lathia C, Schwartz B, Taylor I, Moscovici M, Saltz LB. Phase II study of sorafenib in patients with advanced hepatocellular carcinoma. J Clin Oncol. 2006 Sep 10;24(26):4293-300. doi: 10.1200/JCO.2005.01.3441. Epub 2006 Aug 14.

  • Abou-Alfa GK, Johnson P, Knox JJ, Capanu M, Davidenko I, Lacava J, Leung T, Gansukh B, Saltz LB. Doxorubicin plus sorafenib vs doxorubicin alone in patients with advanced hepatocellular carcinoma: a randomized trial. JAMA. 2010 Nov 17;304(19):2154-60. doi: 10.1001/jama.2010.1672.

Related Links

MeSH Terms

Conditions

Carcinoma, HepatocellularNeoplasmsLiver Neoplasms

Interventions

SorafenibDoxorubicin

Condition Hierarchy (Ancestors)

AdenocarcinomaCarcinomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeDigestive System NeoplasmsNeoplasms by SiteDigestive System DiseasesLiver Diseases

Intervention Hierarchy (Ancestors)

Phenylurea CompoundsUreaAmidesOrganic ChemicalsBenzene DerivativesHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsNiacinamideNicotinic AcidsAcids, HeterocyclicHeterocyclic CompoundsPyridinesHeterocyclic Compounds, 1-RingDaunorubicinAnthracyclinesNaphthacenesPolycyclic Aromatic HydrocarbonsPolycyclic CompoundsAminoglycosidesGlycosidesCarbohydrates

Limitations and Caveats

The study had been prematurely terminated by the sponsor because positive results were obtained in another Nexavar trial (Phase 3 study 100554 NCT00105443). NCI-CTC was translated to MedDRA for SOCs only.

Results Point of Contact

Title
Therapeutic Area Head
Organization
BAYER

Study Officials

  • Bayer Study Director

    Bayer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 21, 2005

First Posted

April 22, 2005

Study Start

April 1, 2005

Primary Completion

April 1, 2008

Study Completion

April 1, 2008

Last Updated

October 31, 2014

Results First Posted

June 11, 2009

Record last verified: 2014-10

Locations