NCT00098722

Brief Summary

Maraviroc (UK-427,857), a selective and reversible CCR5 coreceptor antagonist, has been shown to be active in vitro against a wide range of clinical isolates (including those resistant to existing classes). In HIV-1 infected patients, maraviroc (UK-427,857) given as monotherapy for 10 days reduced HIV-1 viral load by up to 1.6 log, consistent with currently available agents. Safety and toleration have been studied in over 400 subjects for up to 28 days at 300 mg twice daily. No significant effects were seen on the QTc interval. The purpose of this study is to evaluate the antiretroviral activity of maraviroc (UK-427,857) in HIV infected, treatment experienced patients who are failing their current antiretroviral regimen and infected with R5-tropic virus exclusively. This study will involve more than 100 centers in Europe and Australia to achieve a total randomized subject population of 500 subjects. Patients will be randomly (2:2:1) assigned to one of three groups: Optimized Background Therapy \[OBT (3-6 drugs based on treatment history and resistance testing)\] + maraviroc (UK-427,857) 150 mg taken once daily, OBT + maraviroc (UK-427,857) 150 mg taken twice daily, or OBT alone. The study will enroll over approximately a 9 month period with 48 weeks of treatment. This may be extended for an additional year depending on the results at 48 weeks. Physical examinations will be performed at study entry, weeks 4, 8, 12, 16, 20, 24, 32, 40 and 48. Blood samples will also be taken at study entry, weeks 2, 4, 8, 12, 16, 20, 24, 32, 40 and 48. Additionally, blood samples will be drawn twice, at least 30 minutes apart, at weeks 2 and 24 for maraviroc (UK-427,857) pharmacokinetic analysis. As part of this clinical study a blood sample will also be taken for non-anonymized pharmacogenetic analysis. Patients will undergo a 12-lead electrocardiogram at study entry, weeks 24 and 48.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
474

participants targeted

Target at P75+ for phase_2 hiv-infections

Timeline
Completed

Started Dec 2004

Longer than P75 for phase_2 hiv-infections

Geographic Reach
13 countries

172 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

December 1, 2004

Completed
6 days until next milestone

First Submitted

Initial submission to the registry

December 7, 2004

Completed
1 day until next milestone

First Posted

Study publicly available on registry

December 8, 2004

Completed
2.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2007

Completed
4 years until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2011

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

May 16, 2012

Completed
Last Updated

May 16, 2012

Status Verified

April 1, 2012

Enrollment Period

2.3 years

First QC Date

December 7, 2004

Results QC Date

April 16, 2012

Last Update Submit

April 16, 2012

Conditions

Outcome Measures

Primary Outcomes (3)

  • Log 10-transformed Human Immunodeficiency Virus Ribonucleic Acid (HIV-1 RNA) Levels at Baseline

    Baseline value calculated as average of pre-dose measurements collected at screening, randomization, and immediately pre-dose.

    Baseline

  • Change From Baseline in Log 10-transformed HIV-1 RNA Levels at Week 24

    Change from baseline in log 10-transformed plasma viral load (HIV-1 RNA) levels (log10 copies/mL). Baseline value calculated as average of pre-dose measurements collected at screening, randomization, and immediately pre-dose.

    Baseline and Week 24

  • Change From Baseline in Log 10-transformed HIV-1 RNA Levels at Week 48

    Change from baseline in log 10-transformed plasma viral load (HIV-1 RNA) levels (log10 copies/mL). Baseline value calculated as average of pre-dose measurements collected at screening, randomization, and immediately pre-dose.

    Baseline and Week 48

Secondary Outcomes (15)

  • Percentage of Participants With HIV-1 RNA Levels Less Than 400 Copies/mL

    Week 24 and 48

  • Percentage of Participants With HIV-1 RNA Levels Less Than 400 Copies/ml or With at Least 0.5 log10 Decrease From Baseline

    Week 24 and 48

  • Percentage of Participants With HIV-1 RNA Levels Less Than 400 Copies/ml or With at Least 1.0 log10 Decrease From Baseline

    Week 24 and 48

  • Percentage of Participants With HIV-1 RNA Levels Less Than 50 Copies/mL

    Week 24 and 48

  • Cluster of Differentiation 4 (CD4) and Cluster of Differentiation 8 (CD8) Cell Count at Baseline

    Baseline

  • +10 more secondary outcomes

Study Arms (3)

1

EXPERIMENTAL
Drug: Maraviroc (UK-427,857)Drug: optimized background therapy

2

PLACEBO COMPARATOR
Drug: Maraviroc (UK-427,857)Drug: optimized background therapy

3

EXPERIMENTAL
Drug: optimized background therapy

Interventions

maraviroc (UK-427,857) 150 mg taken once daily, OBT + maraviroc (UK-427,857) 150 mg taken twice daily, or OBT alone.

1

\[OBT (3-6 drugs based on treatment history and resistance testing)\]

Also known as: Selzentry
1

Eligibility Criteria

Age16 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Men or women at least 16 yers of age (or minimum age as determined by local regulatory authorities)
  • HIV-1 RNA viral load of greater than or equal to 5,000 copies/mL
  • Stable pre-study antiretroviral regimen, or on no antiretroviral agents, for at least 4 weeks
  • Documented genotypic or phenotypic resistance to three of the four antiretroviral drug classes, OR, Antiretroviral-class experience greater than or equal to 6 months (sequential or cumulative) with at least three of the following: One nucleoside or nucleotide reverse transcriptase inhibitor, one non-nucleoside reverse transcriptase inhibitor, two protease inhibitors (excluding low-dose ritonavir) and/or enfuvirtide
  • Be willing to remain on randomized treatment without any changes or additions to the OBT regimen, except for toxicity management or upon meeting criteria for treatment failure
  • A negative urine pregnancy test at the baseline visit for Women of Child Bearing Potential (WOCBP)
  • Effective barrier contraception for WOCBP and males

You may not qualify if:

  • Patients requiring treatment with more than 6 antiretroviral agents (excluding low-dose ritonavir)
  • Prior treatment with maraviroc (UK-427,857) or another experimental HIV entry inhibitor for more than 14 days
  • Suspected or documented active, untreated HIV-1 related opportunistic infection (OI) or other condition requiring acute therapy
  • Treatment for an active opportunistic infection, or unexplained temperature \>38.5 degrees Celsius for 7 consecutive days
  • Active alcohol or substance abuse sufficient, in the Investigator's judgment, to prevent adherence to study medication and/or follow up
  • Lactating women, or planned pregnancy during the trial period
  • Significant renal insufficiency
  • Initiating therapy with a potentially myelosuppressive, neurotoxic, hepatotoxic and/or cytotoxic agent within 60 days prior to randomization or the expected need for such therapy during the study period
  • Documented or suspected acute hepatitis or pancreatitis within 30 days prior to randomization
  • Significantly elevated liver enzymes or cirrhosis
  • Significant neutropenia, anemia or thrombocytopenia
  • Malabsorption or an inability to tolerate oral medications
  • Certain medications
  • Malignancy requiring parenteral chemotherapy that must be continued for the duration of the trial
  • X4- or dual/mixed-tropic virus or repeated assay failure
  • +1 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (172)

Pfizer Investigational Site

Hobson City, Alabama, 36201, United States

Location

Pfizer Investigational Site

Garden Grove, California, 92845, United States

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Pfizer Investigational Site

Los Angeles, California, 90036, United States

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Pfizer Investigational Site

Oakland, California, 94609-3480, United States

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Pfizer Investigational Site

Palm Springs, California, 92262, United States

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Pfizer Investigational Site

Tarzana, California, 91356, United States

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Pfizer Investigational Site

Norwalk, Connecticut, 06851, United States

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Pfizer Investigational Site

Southport, Connecticut, 06490, United States

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Pfizer Investigational Site

Stratford, Connecticut, 06614, United States

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Pfizer Investigational Site

Washington D.C., District of Columbia, 20007, United States

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Pfizer Investigational Site

Washington D.C., District of Columbia, 20010-2976, United States

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Pfizer Investigational Site

Clearwater, Florida, 33765, United States

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Pfizer Investigational Site

Hollywood, Florida, 33021-6327, United States

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Pfizer Investigational Site

Miami, Florida, 33137, United States

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Pfizer Investigational Site

Miami, Florida, 33145, United States

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Pfizer Investigational Site

Miami, Florida, 33155, United States

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Pfizer Investigational Site

Miami Beach, Florida, 33139, United States

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Pfizer Investigational Site

Pensacola, Florida, 32504, United States

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Pfizer Investigational Site

Safety Harbor, Florida, 34695, United States

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Pfizer Investigational Site

St. Petersburg, Florida, 33713, United States

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Pfizer Investigational Site

Tampa, Florida, 33611, United States

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Pfizer Investigational Site

Tampa, Florida, 33614, United States

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Pfizer Investigational Site

Atlanta, Georgia, 30309, United States

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Pfizer Investigational Site

Atlanta, Georgia, 30318-2513, United States

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Pfizer Investigational Site

Atlanta, Georgia, 30339-3915, United States

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Pfizer Investigational Site

Jonesboro, Georgia, 30236, United States

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Pfizer Investigational Site

Chicago, Illinois, 60613, United States

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Pfizer Investigational Site

Chicago, Illinois, 60657, United States

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Pfizer Investigational Site

Springfield, Illinois, 62702, United States

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Pfizer Investigational Site

Metairie, Louisiana, 70006, United States

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Pfizer Investigational Site

Baltimore, Maryland, 21201, United States

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Pfizer Investigational Site

Silver Spring, Maryland, 20910, United States

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Pfizer Investigational Site

Ann Arbor, Michigan, 48109-0008, United States

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Pfizer Investigational Site

Ann Arbor, Michigan, 48109-0352, United States

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Pfizer Investigational Site

Detroit, Michigan, 48201, United States

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Pfizer Investigational Site

Detroit, Michigan, 48202, United States

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Pfizer Investigational Site

Kansas City, Missouri, 64106, United States

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Pfizer Investigational Site

St Louis, Missouri, 63139-2909, United States

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Pfizer Investigational Site

Buffalo, New York, 14215, United States

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Pfizer Investigational Site

East Meadow, New York, 11554, United States

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Pfizer Investigational Site

Elmira, New York, 14905, United States

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Pfizer Investigational Site

New York, New York, 10011, United States

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Pfizer Investigational Site

New York, New York, 10016, United States

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Pfizer Investigational Site

New York, New York, 10025, United States

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Pfizer Investigational Site

New York, New York, 10029, United States

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Pfizer Investigational Site

Greenville, North Carolina, 27834, United States

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Pfizer Investigational Site

Akron, Ohio, 44304, United States

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Pfizer Investigational Site

Cleveland, Ohio, 44109, United States

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Pfizer Investigational Site

Tulsa, Oklahoma, 74135, United States

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Pfizer Investigational Site

Portland, Oregon, 97210, United States

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Pfizer Investigational Site

Portland, Oregon, 97227, United States

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Pfizer Investigational Site

West Reading, Pennsylvania, 19611, United States

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Pfizer Investigational Site

Charleston, South Carolina, 29403, United States

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Pfizer Investigational Site

Charleston, South Carolina, 29425, United States

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Pfizer Investigational Site

Dallas, Texas, 75219, United States

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Pfizer Investigational Site

Fort Worth, Texas, 76104, United States

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Pfizer Investigational Site

Fort Worth, Texas, 76107, United States

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Pfizer Investigational Site

Pasadena, Texas, 77505-4245, United States

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Pfizer Investigational Site

Danville, Virginia, 24541, United States

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Pfizer Investigational Site

Hampton, Virginia, 23666, United States

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Pfizer Investigational Site

Lynchburg, Virginia, 24501, United States

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Pfizer Investigational Site

Richmond, Virginia, 23298, United States

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Pfizer Investigational Site

Burwood, New South Wales, 2134, Australia

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Pfizer Investigational Site

Darlinghurst, New South Wales, 2010, Australia

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Pfizer Investigational Site

Surry Hills, New South Wales, 2010, Australia

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Pfizer Investigational Site

Sydney, New South Wales, 2010, Australia

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Pfizer Investigational Site

Wentworthville, New South Wales, 2145, Australia

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Pfizer Investigational Site

Herston, Queensland, 4029, Australia

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Pfizer Investigational Site

Miami, Queensland, 4220, Australia

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Pfizer Investigational Site

Fitzroy North, Victoria, 3068, Australia

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Pfizer Investigational Site

Melbourne, Victoria, 3004, Australia

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Pfizer Investigational Site

South Yarra, Victoria, 3141, Australia

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Pfizer Investigational Site

Darlinghurst, 2010, Australia

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Pfizer Investigational Site

Brussels, 1000, Belgium

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Pfizer Investigational Site

Brussels, 1070, Belgium

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Pfizer Investigational Site

Brussels, 1200, Belgium

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Pfizer Investigational Site

Ghent, 9000, Belgium

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Pfizer Investigational Site

Liège, 4000, Belgium

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Pfizer Investigational Site

Montreal, Quebec, H2L 2W5, Canada

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Pfizer Investigational Site

Montreal, Quebec, H2L 4M1, Canada

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Pfizer Investigational Site

Toulon, Bp1412, 83056, France

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Pfizer Investigational Site

Lyon, Cedex 02, 69288, France

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Pfizer Investigational Site

Orléans, Cedex 02, 45067, France

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Pfizer Investigational Site

Marseille, Cedex 09, 13274, France

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Pfizer Investigational Site

Paris, Cedex 10, 75475, France

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Pfizer Investigational Site

Paris, Cedex 12, 75571, France

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Pfizer Investigational Site

Bobigny, Cedex, 93009, France

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Pfizer Investigational Site

Caen, Cedex, 14033, France

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Pfizer Investigational Site

Le Kremlin-BicĂªtre, 94270, France

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Pfizer Investigational Site

Montpellier, 34295, France

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Pfizer Investigational Site

Nantes, 44093, France

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Pfizer Investigational Site

Nice Cedex 3, 06, 06202, France

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Pfizer Investigational Site

Paris, 75015, France

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Pfizer Investigational Site

Paris, 75018, France

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Pfizer Investigational Site

Paris, 75020, France

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Pfizer Investigational Site

Aachen, 52062, Germany

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Pfizer Investigational Site

Berlin, 12157, Germany

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Pfizer Investigational Site

Bochum, 44791, Germany

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Pfizer Investigational Site

Bonn, 53105, Germany

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Pfizer Investigational Site

Cologne, 50924, Germany

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Pfizer Investigational Site

DĂ¼sseldorf, 40225, Germany

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Pfizer Investigational Site

Erlangen, 91054, Germany

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Pfizer Investigational Site

Essen, 45122, Germany

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Pfizer Investigational Site

Frankfurt, 60590, Germany

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Pfizer Investigational Site

Freiburg im Breisgau, 79098, Germany

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Pfizer Investigational Site

FĂ¼rth, 90762, Germany

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Pfizer Investigational Site

Hamburg, 20099, Germany

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Pfizer Investigational Site

Hamburg, 20246, Germany

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Pfizer Investigational Site

Hanover, 30625, Germany

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Pfizer Investigational Site

Mannheim, 68161, Germany

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Pfizer Investigational Site

MĂ¼nchen, 80336, Germany

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Pfizer Investigational Site

OsnabrĂ¼ck, 49090, Germany

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Pfizer Investigational Site

Stuttgart, 70197, Germany

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Pfizer Investigational Site

Ulm, 89081, Germany

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Pfizer Investigational Site

Antella (FI), 50011, Italy

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Pfizer Investigational Site

Brescia, 25123, Italy

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Pfizer Investigational Site

Florence, 50193, Italy

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Pfizer Investigational Site

Genova, 16132, Italy

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Pfizer Investigational Site

Milan, 20100, Italy

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Pfizer Investigational Site

Modena, 41100, Italy

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Pfizer Investigational Site

Monserrato, CA, 09042, Italy

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Pfizer Investigational Site

Roma, 00161, Italy

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Pfizer Investigational Site

Roma, 00184, Italy

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Pfizer Investigational Site

Roma, 00185, Italy

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Pfizer Investigational Site

Torino, 10149, Italy

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Pfizer Investigational Site

Venezia, 30170, Italy

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Pfizer Investigational Site

Amsterdam, 1081 HV, Netherlands

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Pfizer Investigational Site

Amsterdam, 1105 AZ, Netherlands

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Pfizer Investigational Site

Arnhem, 6815 AD, Netherlands

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Pfizer Investigational Site

Rotterdam, 3015 GD, Netherlands

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Pfizer Investigational Site

Utrecht, 3584 CX, Netherlands

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Pfizer Investigational Site

Bialystok, 15-540, Poland

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Pfizer Investigational Site

Bydgoszcz, 85-030, Poland

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Pfizer Investigational Site

ChorzĂ³w, 41-500, Poland

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Pfizer Investigational Site

Gdansk, 80-214, Poland

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Pfizer Investigational Site

Krakow, 31-531, Poland

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Pfizer Investigational Site

Szczecin, 71-455, Poland

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Pfizer Investigational Site

Warsaw, 01-201, Poland

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Pfizer Investigational Site

Elche, Alicante, 03202, Spain

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Pfizer Investigational Site

Badalona, Barcelona, 08916, Spain

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Pfizer Investigational Site

Barcelona, Barcelona, 08025, Spain

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Pfizer Investigational Site

Barcelona, Barcelona, 08036, Spain

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Pfizer Investigational Site

CĂ³rdoba, Cordoba, 14004, Spain

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Pfizer Investigational Site

Madrid, Madrid, 28006, Spain

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Pfizer Investigational Site

Madrid, Madrid, 28029, Spain

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Pfizer Investigational Site

Madrid, Madrid, 28041, Spain

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Pfizer Investigational Site

Madrid, Madrid, 28046, Spain

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Pfizer Investigational Site

Seville, Sevilla, 41013, Spain

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Pfizer Investigational Site

Seville, Sevilla, 41014, Spain

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Pfizer Investigational Site

Donostia / San Sebastian, 20014, Spain

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Pfizer Investigational Site

Madrid, 28034, Spain

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Pfizer Investigational Site

Venhalsan, Stockholm County, 118 83, Sweden

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Pfizer Investigational Site

Gothenburg, 41685, Sweden

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Pfizer Investigational Site

Malmo, 214 01, Sweden

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Pfizer Investigational Site

Basel, 4031, Switzerland

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Pfizer Investigational Site

Geneva, Switzerland

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Pfizer Investigational Site

Lausanne, 1011, Switzerland

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Pfizer Investigational Site

Lugano, 6900, Switzerland

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Pfizer Investigational Site

Sankt Gallen, 9007, Switzerland

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Pfizer Investigational Site

Zurich, 8091, Switzerland

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Pfizer Investigational Site

Leicester, Leics, LE1 5WW, United Kingdom

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Pfizer Investigational Site

Edinburgh, Loth, ED4 2XU, United Kingdom

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Pfizer Investigational Site

Birmingham, B9 5SS, United Kingdom

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Pfizer Investigational Site

Brighton, BN2 1ES, United Kingdom

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Pfizer Investigational Site

Edinburgh, EH4 2XU, United Kingdom

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Pfizer Investigational Site

London, NW3 2QG, United Kingdom

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Pfizer Investigational Site

London, SE5 9RS, United Kingdom

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Pfizer Investigational Site

London, SW10 9TH, United Kingdom

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Pfizer Investigational Site

London, SW17 0QT, United Kingdom

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Pfizer Investigational Site

London, W2 1NY, United Kingdom

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Pfizer Investigational Site

Manchester, M8 5RB, United Kingdom

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Pfizer Investigational Site

Newcastle Upon Tyre, NE4 6BE, United Kingdom

Location

Related Publications (5)

  • Lewis ME, Simpson P, Mori J, Jubb B, Sullivan J, McFadyen L, van der Ryst E, Craig C, Robertson DL, Westby M. V3-Loop genotypes do not predict maraviroc susceptibility of CCR5-tropic virus or clinical response through week 48 in HIV-1-infected, treatment-experienced persons receiving optimized background regimens. Antivir Chem Chemother. 2021 Jan-Dec;29:20402066211030380. doi: 10.1177/20402066211030380.

  • Gulick RM, Fatkenheuer G, Burnside R, Hardy WD, Nelson MR, Goodrich J, Mukwaya G, Portsmouth S, Heera JR. Five-year safety evaluation of maraviroc in HIV-1-infected treatment-experienced patients. J Acquir Immune Defic Syndr. 2014 Jan 1;65(1):78-81. doi: 10.1097/QAI.0b013e3182a7a97a.

  • Hardy WD, Gulick RM, Mayer H, Fatkenheuer G, Nelson M, Heera J, Rajicic N, Goodrich J. Two-year safety and virologic efficacy of maraviroc in treatment-experienced patients with CCR5-tropic HIV-1 infection: 96-week combined analysis of MOTIVATE 1 and 2. J Acquir Immune Defic Syndr. 2010 Dec 15;55(5):558-64. doi: 10.1097/QAI.0b013e3181ee3d82.

  • Fatkenheuer G, Nelson M, Lazzarin A, Konourina I, Hoepelman AI, Lampiris H, Hirschel B, Tebas P, Raffi F, Trottier B, Bellos N, Saag M, Cooper DA, Westby M, Tawadrous M, Sullivan JF, Ridgway C, Dunne MW, Felstead S, Mayer H, van der Ryst E; MOTIVATE 1 and MOTIVATE 2 Study Teams. Subgroup analyses of maraviroc in previously treated R5 HIV-1 infection. N Engl J Med. 2008 Oct 2;359(14):1442-55. doi: 10.1056/NEJMoa0803154.

  • Gulick RM, Lalezari J, Goodrich J, Clumeck N, DeJesus E, Horban A, Nadler J, Clotet B, Karlsson A, Wohlfeiler M, Montana JB, McHale M, Sullivan J, Ridgway C, Felstead S, Dunne MW, van der Ryst E, Mayer H; MOTIVATE Study Teams. Maraviroc for previously treated patients with R5 HIV-1 infection. N Engl J Med. 2008 Oct 2;359(14):1429-41. doi: 10.1056/NEJMoa0803152.

Related Links

MeSH Terms

Conditions

HIV Infections

Interventions

Maraviroc

Condition Hierarchy (Ancestors)

Blood-Borne InfectionsCommunicable DiseasesInfectionsSexually Transmitted Diseases, ViralSexually Transmitted DiseasesLentivirus InfectionsRetroviridae InfectionsRNA Virus InfectionsVirus DiseasesGenital DiseasesUrogenital DiseasesImmunologic Deficiency SyndromesImmune System Diseases

Intervention Hierarchy (Ancestors)

CyclohexanesCycloparaffinsHydrocarbons, AlicyclicHydrocarbons, CyclicHydrocarbonsOrganic ChemicalsTriazolesAzolesHeterocyclic Compounds, 1-RingHeterocyclic Compounds

Results Point of Contact

Title
Pfizer ClinicalTrials.gov Call Center
Organization
Pfizer, Inc.

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 7, 2004

First Posted

December 8, 2004

Study Start

December 1, 2004

Primary Completion

April 1, 2007

Study Completion

April 1, 2011

Last Updated

May 16, 2012

Results First Posted

May 16, 2012

Record last verified: 2012-04

Locations