NCT00077610

Brief Summary

This study will assess the efficacy and safety of intravenous Mircera, given as maintenance treatment for renal anemia in chronic kidney disease patients on dialysis who were previously receiving iv epoetin. The anticipated time on study treatment is 1-2 years and the target sample size is 100-500 individuals.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
673

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Feb 2004

Geographic Reach
8 countries

99 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

February 1, 2004

Completed
9 days until next milestone

First Submitted

Initial submission to the registry

February 10, 2004

Completed
3 days until next milestone

First Posted

Study publicly available on registry

February 13, 2004

Completed
1.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 1, 2005

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

August 1, 2005

Completed
10.6 years until next milestone

Results Posted

Study results publicly available

February 29, 2016

Completed
Last Updated

January 13, 2017

Status Verified

September 1, 2016

Enrollment Period

1.5 years

First QC Date

February 10, 2004

Results QC Date

January 29, 2016

Last Update Submit

November 23, 2016

Conditions

Outcome Measures

Primary Outcomes (1)

  • Mean Change in Hemoglobin (Hb) Concentration From Baseline to Evaluation Period

    A time adjusted mean change in Hb concentration was calculated using an Area Under the Curve (AUC) approach, for both periods separately. Change in Hb concentration between the Baseline and evaluation periods was calculated by subtracting the calculated average baseline Hb from the average evaluation period Hb. At the end of the Week 36, data allowing the evaluation of the therapeutic response was available for 188 out of 221 eligible participants in RO0503821 (1x/2 Weeks) arm; 172 out of 220 eligible participants in RO0503821 (1x/4 Weeks); and 180 out of 225 participants in Epoetin (1-3x/Weeks) arm.

    Baseline, Week 29 to Week 36

Secondary Outcomes (7)

  • Number of Participants Maintaining Average Hemoglobin Concentration During Evaluation Period Within +/- 1 Gram Per Deciliter (g/dl) of Average Baseline Hemoglobin Concentration.

    Baseline, Week 29 to Week 36

  • The Incidence of Red Blood Cell (RBC) Transfusions During the Titration and Evaluation Periods

    Week 1 to Week 36

  • Number of Participants With Marked Laboratory Abnormalities in Platelet, White Blood Cell Counts (WBC) and Red Blood Cells (RBC)

    Up to Week 53

  • Number of Participants With Marked Laboratory Abnormalities for Blood Chemistry and Electrolytes

    Up to Week 53

  • Mean Change in Blood Pressure From Baseline at Week 36 and Week 52

    Baseline, Week 36 and Week 52

  • +2 more secondary outcomes

Study Arms (3)

RO0503821 (1x/2 Weeks)

EXPERIMENTAL

Participants received RO0503821 (Mircera \[methoxy polyethylene glycol-epoetin beta\]) once every two weeks intravenously for 52 weeks. Participants received a starting dose of RO0503821 (60, 100, or 180 microgram \[mcg\]) that was based on the Epoetin dose (\<8000, 8000-16000, \>16000 International units \[IU\]/Week) administered during the week preceding the switch to the study drug.

Drug: RO0503821 (1x/2 Weeks)

RO0503821 (1x/4 Weeks)

EXPERIMENTAL

Participants received RO0503821 once every four weeks intravenously for 52 weeks. Participants received a starting dose of RO0503821 (120, 200, or 360 mcg) that was based on the Epoetin dose (\<8000, 8000-16000, \>16000 IU/Week) administered during the week preceding the switch to the study drug.

Drug: RO0503821 (1x/4 Weeks)

Epoetin (1-3x/Weeks)

ACTIVE COMPARATOR

Participants received their ongoing weekly intravenous dose of Epoetin alfa or beta one, two or three times weekly for 52 weeks.

Drug: Epoetin alfa or beta

Interventions

intravenously 3 times weekly for 52 weeks, as prescribed

Also known as: Epoetin
Epoetin (1-3x/Weeks)

60, 100, or 180 microgram (mcg) (starting dose) once every two weeks intravenously for 52 weeks.

Also known as: Mircera
RO0503821 (1x/2 Weeks)

120, 200 or 360 mcg (starting dose) once every four weeks intravenously for 52 weeks.

Also known as: Mircera
RO0503821 (1x/4 Weeks)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • adult patients \>=18 years of age;
  • chronic renal anemia;
  • on dialysis therapy for at least 12 weeks before screening;
  • receiving IV epoetin for at least 8 weeks before screening.

You may not qualify if:

  • women who are pregnant, breastfeeding or using unreliable birth control methods;
  • administration of another investigational drug within 4 weeks before screening, or during the study period.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (99)

Unknown Facility

Birmingham, Alabama, 35211, United States

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Mobile, Alabama, 36608, United States

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Montgomery, Alabama, 36106, United States

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Encino, California, 91356, United States

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Irvine, California, 92868, United States

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Los Angeles, California, 90095, United States

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Monterey Park, California, 91754, United States

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Riverside, California, 92501, United States

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Sacramento, California, 95816-5119, United States

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San Diego, California, 92103-8342, United States

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San Diego, California, 92120, United States

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San Francisco, California, 94117, United States

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San Jose, California, 95116-1906, United States

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Colorado Springs, Colorado, 80909, United States

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Denver, Colorado, 80262, United States

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Lakewood, Colorado, 80260, United States

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Ocala, Florida, 34471, United States

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Pembroke Pines, Florida, 33028, United States

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Atlanta, Georgia, 30342, United States

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Augusta, Georgia, 30901, United States

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Chicago, Illinois, 60612, United States

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Maywood, Illinois, 60153, United States

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Louisville, Kentucky, 40202-1718, United States

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Covington, Louisiana, 70433, United States

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Boston, Massachusetts, 02115, United States

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Boston, Massachusetts, 02215, United States

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Springfield, Massachusetts, 01107, United States

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Detroit, Michigan, 48202-2689, United States

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Brooklyn Center, Minnesota, 55430, United States

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Paterson, New Jersey, 07503, United States

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Albuquerque, New Mexico, 87131, United States

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Brooklyn, New York, 11203, United States

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Great Neck, New York, 11021, United States

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Mineola, New York, 11501, United States

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New York, New York, 10021, United States

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New York, New York, 10128, United States

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Stony Brook, New York, 11794-8161, United States

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The Bronx, New York, 10467, United States

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Chapel Hill, North Carolina, 27599-7155, United States

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Raleigh, North Carolina, 27609, United States

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Winston-Salem, North Carolina, 27157-1023, United States

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Cincinnati, Ohio, 45267-0585, United States

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Toledo, Ohio, 43606, United States

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Portland, Oregon, 97210, United States

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Erie, Pennsylvania, 16502, United States

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Philadelphia, Pennsylvania, 19104, United States

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Pittsburgh, Pennsylvania, 15224, United States

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Pittsburgh, Pennsylvania, 15261, United States

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Orangeburg, South Carolina, 29118, United States

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Chattanooga, Tennessee, 37404, United States

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Nashville, Tennessee, 37205, United States

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Nashville, Tennessee, 37232, United States

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Austin, Texas, 78705, United States

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Houston, Texas, 77054, United States

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Houston, Texas, 77099, United States

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San Antonio, Texas, 78229, United States

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Burlington, Vermont, 05401, United States

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Fairfax, Virginia, 22031, United States

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Richmond, Virginia, 23298, United States

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Marshfield, Wisconsin, 54449, United States

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St. John's, Newfoundland and Labrador, A1B 3V6, Canada

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Kingston, Ontario, K7L 3N6, Canada

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London, Ontario, N6A 5A5, Canada

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Mississauga, Ontario, L5M 2V8, Canada

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Scarborough Village, Ontario, M1H 3G4, Canada

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Toronto, Ontario, M5G 2C4, Canada

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Toronto, Ontario, M9N 1N8, Canada

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Montreal, Quebec, H3A 1A1, Canada

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Saskatoon, Saskatchewan, S7K 1N4, Canada

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Aubervilliers, 93307, France

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Bordeaux, 33076, France

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La Tronche, 38700, France

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Paris, 75 016, France

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Paris, 75015, France

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Paris, 75651, France

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Toulouse, 31059, France

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Dortmund, 44263, Germany

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Ellwangen, 73479, Germany

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München, 80804, Germany

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Nuremberg, 90431, Germany

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Stuttgart, 70191, Germany

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Wiesbaden, 65191, Germany

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Wiesloch, 69168, Germany

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Como, 22100, Italy

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Lecco, 23900, Italy

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Lodi, 26900, Italy

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Milan, 20162, Italy

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Pavia, 27100, Italy

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Bergen, 5021, Norway

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Levanger, 7600, Norway

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Lillehammer, 2629, Norway

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Trondheim, 7006, Norway

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A Coruña, 15006, Spain

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Barcelona, 08003, Spain

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Madrid, 28007, Spain

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Málaga, 29010, Spain

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Seville, 41013, Spain

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Lausanne, 1003, Switzerland

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Lausanne, 1011, Switzerland

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Related Publications (2)

  • Chung EY, Palmer SC, Saglimbene VM, Craig JC, Tonelli M, Strippoli GF. Erythropoiesis-stimulating agents for anaemia in adults with chronic kidney disease: a network meta-analysis. Cochrane Database Syst Rev. 2023 Feb 13;2(2):CD010590. doi: 10.1002/14651858.CD010590.pub3.

  • Levin NW, Fishbane S, Canedo FV, Zeig S, Nassar GM, Moran JE, Villa G, Beyer U, Oguey D; MAXIMA study investigators. Intravenous methoxy polyethylene glycol-epoetin beta for haemoglobin control in patients with chronic kidney disease who are on dialysis: a randomised non-inferiority trial (MAXIMA). Lancet. 2007 Oct 20;370(9596):1415-21. doi: 10.1016/S0140-6736(07)61599-2.

MeSH Terms

Conditions

Anemia

Interventions

Epoetin AlfaErythropoietincontinuous erythropoietin receptor activator

Condition Hierarchy (Ancestors)

Hematologic DiseasesHemic and Lymphatic Diseases

Intervention Hierarchy (Ancestors)

Colony-Stimulating FactorsGlycoproteinsGlycoconjugatesCarbohydratesHematopoietic Cell Growth FactorsCytokinesIntercellular Signaling Peptides and ProteinsPeptidesAmino Acids, Peptides, and ProteinsProteinsBiological Factors

Results Point of Contact

Title
Roche Trial Information Hotline
Organization
F. Hoffmann-La Roche AG

Study Officials

  • Clinical Trials

    Hoffmann-La Roche

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 10, 2004

First Posted

February 13, 2004

Study Start

February 1, 2004

Primary Completion

August 1, 2005

Study Completion

August 1, 2005

Last Updated

January 13, 2017

Results First Posted

February 29, 2016

Record last verified: 2016-09

Locations