NCT00064701

Brief Summary

The purpose of this study is to compare the safety and efficacy of tacrolimus/mycophenolate mofetil (MMF), cyclosporine/MMF and tacrolimus modified release/MMF in de novo kidney transplant recipients.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
668

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Jun 2003

Longer than P75 for phase_3

Geographic Reach
3 countries

57 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

June 1, 2003

Completed
1 month until next milestone

First Submitted

Initial submission to the registry

July 10, 2003

Completed
4 days until next milestone

First Posted

Study publicly available on registry

July 14, 2003

Completed
1.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2005

Completed
4 years until next milestone

Study Completion

Last participant's last visit for all outcomes

March 1, 2009

Completed
4.6 years until next milestone

Results Posted

Study results publicly available

September 26, 2013

Completed
Last Updated

December 5, 2013

Status Verified

November 1, 2013

Enrollment Period

1.8 years

First QC Date

July 10, 2003

Results QC Date

July 25, 2013

Last Update Submit

November 12, 2013

Conditions

Keywords

De Novo Kidney TransplantcyclosporinePrograf®mycophenolate mofetiltacrolimus

Outcome Measures

Primary Outcomes (1)

  • Percentage of Participants With Efficacy Failure

    Efficacy failure is defined as any participant who died, experienced a graft failure (permanent return to dialysis \[\> 30 days\] or retransplant), had a biopsy-confirmed (Banff Grade ≥ I) acute rejection (BCAR), or was lost to follow-up. Biopsies were graded according to the 1997 Banff criteria: Borderline: No intimal arteritis present but foci of mild tubulitis; Grade I: Significant interstitial infiltration and foci of moderate to severe tubulitis; Grade II: Mild to severe intimal arteritis Grade III: Transmural arteritis and/or arterial fibrinoid change and necrosis of medial smooth muscle cells with accompanying lymphocytic infiltrate in vessel.

    one year

Secondary Outcomes (14)

  • Patient Survival at One Year

    One year

  • Graft Survival at One Year

    One year

  • Percentage of Participants With Biopsy Confirmed Acute Rejection at 6 and 12 Months

    Six months and 12 months

  • Time to First Biopsy-confirmed Acute Rejection Episode

    one year

  • Number of Participants Requiring Anti-lymphocyte Antibody Therapy for Treatment of Rejection

    one year

  • +9 more secondary outcomes

Study Arms (3)

Tacrolimus

EXPERIMENTAL

Participants received a first dose of tacrolimus between 0.075 and 0.10 mg/kg twice daily, orally prior to or within 48 hours of the completion of the transplant procedure, and subsequently as twice daily oral doses adjusted based on clinical evidence of efficacy, blood concentrations of tacrolimus and adverse events. Participants also received 1.0 g mycophenolate mofetil orally twice daily throughout the study.

Drug: TacrolimusDrug: mycophenolate mofetil

Tacrolimus Modified Release

ACTIVE COMPARATOR

Participants received a first dose of tacrolimus modified release between 0.15 and 0.20 mg/kg/day, given as a single oral dose in the morning, prior to or within 48 hours following the completion of the transplant procedure, and subsequently as once daily oral doses adjusted based on clinical evidence of efficacy, blood concentrations of tacrolimus and adverse events. Participants also received 1.0 g mycophenolate mofetil orally twice daily throughout the study.

Drug: Tacrolimus Modified Release (MR)Drug: mycophenolate mofetil

Cyclosporine

ACTIVE COMPARATOR

Participants received a first dose of cyclosporine between 4 to 5 mg/kg orally prior to or within 48 hours following the completion of the transplant procedure and subsequently as twice daily oral doses adjusted based on clinical evidence of efficacy, blood concentrations of tacrolimus and adverse events. Participants also received 1.0 g mycophenolate mofetil orally twice daily throughout the study.

Drug: cyclosporine microemulsionDrug: mycophenolate mofetil

Interventions

The target range for whole blood tacrolimus trough concentrations was 7 to 16 ng/mL for days 0 through 90, and 5 to 15 ng/mL thereafter.

Also known as: Advagraf, FK506, FKMR, MR4, Astagraf XL
Tacrolimus Modified Release

The target range for whole blood tacrolimus trough concentrations was the recommended trough concentration range for Prograf: 7 to 16 ng/mL for days 0 through 90 and 5 to 15 ng/mL thereafter.

Also known as: Prograf, FK506
Tacrolimus

The target range for whole blood cyclosporine trough concentrations was 125 to 400 ng/mL for days 0 through 90, and 100 to 300 ng/mL thereafter.

Also known as: Neoral, CsA
Cyclosporine

Oral

Also known as: CellCept, MMF
CyclosporineTacrolimusTacrolimus Modified Release

Eligibility Criteria

Age12 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Recipient of a primary or retransplanted non-human leukocyte antigen (HLA)-identical living or non-HLA-identical cadaveric kidney transplant
  • Age greater or equal to 12 years

You may not qualify if:

  • Recipient or donor is known seropositive for human immunodeficiency virus (HIV)
  • Has current malignancy or history of malignancy
  • Has significant liver disease
  • Has uncontrolled concomitant infection or any other unstable medical condition
  • Is receiving everolimus or enteric coated mycophenolic acid at any time during the study
  • Received kidney with a cold ischemia time of equal or more than 36 hours
  • Received kidney transplant from a cadaveric donor equal or more than 60 years of age
  • Received intravenous immunoglobulin (IVIG) therapy prior to randomization

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (57)

Unknown Facility

Birmingham, Alabama, 35294, United States

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Mobile, Alabama, 36617, United States

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Loma Linda, California, 92354, United States

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Los Angeles, California, 90033, United States

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Los Angeles, California, 90057, United States

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Los Angeles, California, 90058, United States

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Los Angeles, California, 90095-7306, United States

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Palo Alto, California, 94304, United States

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San Diego, California, 92103, United States

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San Diego, California, 92123, United States

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San Francisco, California, 94115, United States

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Denver, Colorado, 80262, United States

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Washington D.C., District of Columbia, 20010, United States

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Gainesville, Florida, 32610-0224, United States

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Jacksonville, Florida, 32216, United States

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Augusta, Georgia, 30912, United States

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Chicago, Illinois, 60612, United States

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Chicago, Illinois, 60637, United States

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Indianapolis, Indiana, 46202, United States

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Lexington, Kentucky, 40536, United States

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New Orleans, Louisiana, 70112, United States

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New Orleans, Louisiana, 70121, United States

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Boston, Massachusetts, 02214, United States

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Ann Arbor, Michigan, 48109-0364, United States

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Detroit, Michigan, 48202, United States

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Livingston, New Jersey, 07039, United States

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New Brunswick, New Jersey, 08901, United States

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Albany, New York, 12208, United States

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Buffalo, New York, 14203, United States

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New York, New York, 10029, United States

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Valhalla, New York, 10595, United States

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Chapel Hill, North Carolina, 27599-7211, United States

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Durham, North Carolina, 27710, United States

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Cincinnati, Ohio, 45267, United States

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Portland, Oregon, 97210, United States

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Portland, Oregon, 97239-2940, United States

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Harrisburg, Pennsylvania, 17104, United States

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Philadelphia, Pennsylvania, 19104, United States

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Philadelphia, Pennsylvania, 19107, United States

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Nashville, Tennessee, 37212-4750, United States

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Dallas, Texas, 75235, United States

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Dallas, Texas, 75246, United States

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Houston, Texas, 77030, United States

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San Antonio, Texas, 78229-3900, United States

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Salt Lake City, Utah, 84132, United States

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Fairfax, Virginia, 22031, United States

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Madison, Wisconsin, 53792-7375, United States

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Milwaukee, Wisconsin, 53226, United States

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Porto Alegre, 90240-520, Brazil

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Rio de Janeiro, 21041-003, Brazil

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São Paulo, 04013-043, Brazil

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São Paulo, 04038-002, Brazil

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Unknown Facility

São Paulo, 05465-040, Brazil

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Edmonton, Alberta, Canada

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Vancouver, British Columbia, Canada

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Toronto, Ontario, Canada

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Unknown Facility

Montreal, Quebec, Canada

Location

Related Publications (1)

  • Silva HT Jr, Yang HC, Abouljoud M, Kuo PC, Wisemandle K, Bhattacharya P, Dhadda S, Holman J, Fitzsimmons W, First MR. One-year results with extended-release tacrolimus/MMF, tacrolimus/MMF and cyclosporine/MMF in de novo kidney transplant recipients. Am J Transplant. 2007 Mar;7(3):595-608. doi: 10.1111/j.1600-6143.2007.01661.x. Epub 2007 Jan 11.

    PMID: 17217442BACKGROUND

MeSH Terms

Interventions

TacrolimusCyclosporineMycophenolic Acid

Intervention Hierarchy (Ancestors)

MacrolidesLactonesOrganic ChemicalsCyclosporinsPeptides, CyclicMacrocyclic CompoundsPolycyclic CompoundsPeptidesAmino Acids, Peptides, and ProteinsCaproatesAcids, AcyclicCarboxylic AcidsFatty AcidsLipids

Limitations and Caveats

Company makes no warranties or representations of any kind as to the posting, expressed or implied, including warranties of merchantability and fitness for a particular purpose, and shall not be liable for any damages.

Results Point of Contact

Title
Vice President, Therapeutic Area Head, Transplantation
Organization
Astellas Pharma Global Development, Inc.

Study Officials

  • Use Central Contact

    Astellas Pharma Global Development

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 10, 2003

First Posted

July 14, 2003

Study Start

June 1, 2003

Primary Completion

March 1, 2005

Study Completion

March 1, 2009

Last Updated

December 5, 2013

Results First Posted

September 26, 2013

Record last verified: 2013-11

Locations