NCT00059475

Brief Summary

This study will examine the effectiveness and side effects of an experimental vaccine to prevent recurrence of melanoma. The likelihood of melanoma returning is higher in patients who have melanoma lesions deep in the skin, in patients who have had positive lymph nodes, and in patients who have had surgery for metastatic disease (cancer that has spread beyond the primary site). Melanoma tumors produce proteins called glycoprotein 100 (gp100) and melanoma-associated antigen recognized by T cells 1 (MART-1). Vaccination with specific pieces of these proteins (peptides) may boost the immune system's fight against the cancer. The vaccine injections are mixed with an oil-based substance called Montanide ISA-51, which is intended to increase the immune response to the peptide. Patients 16 years of age and older whose melanoma has been surgically removed and who are currently free of disease may be eligible for this study. Candidates will be screened with a physical examination and blood and urine tests. An electrocardiogram (EKG), x-rays and other imaging studies will be done if recent results are not available. Some candidates may require heart tests, such as a cardiac stress test or echocardiogram, or lung function tests. In addition, all candidates will be tested for human leukocyte antigen (HLA) tissue type; patients must be type human leukocyte antigens (HLA-A)\*0201, the type on which this vaccine is based. Participants will be randomly assigned to receive one of four different vaccines to determine which peptides offer the best immunity. Each treatment course consists of two injections of the vaccines every 3 weeks for four times. The injections are given under the skin of the thigh. After every other treatment course (every 6 months), patients will undergo a series of x-rays and scans to look for tumor. The immunizations may continue for up to 12 months as long as the melanoma does not return. The injections are given at the National Institutes of Health (NIH) Clinical Center. Patients are monitored for 1 hour after each injection and have blood tests and a physical examination to look for treatment side effects. Patients will be followed with blood tests every 12 weeks to monitor body functions. They will also undergo leukapheresis-a procedure to collect white blood cells-before starting treatment and about 3 to 4 weeks after the fourth vaccine to evaluate how the vaccines affect the action of the immune system cells. For this procedure, blood is drawn through a needle in the arm, similar to donating blood. The blood goes through a machine that separates out the lymphocytes (white blood cells), and the rest of the blood is returned through a needle in the other arm. Some patients may undergo a biopsy-surgical removal of a small piece of tissue under local anesthetic-of normal skin and tumor or lymph node tissue to examine the effects of the vaccines on the tumor immune cells. Patients whose disease returns during the first course of vaccine therapy will have surgery to remove the tumor and will continue to receive the vaccine treatment. Patients whose tumor returns after completing one course of therapy may receive a substance called interleukin-2 (IL-2), which can boost immune function against the tumor. interleukin-2 (IL-2) is given intravenously (through a small tube placed in a vein) every 8 hours for 4 days. This regimen is repeated after 10 to 14 days. Those who respond to interleukin-2 (IL-2) will have a third course of treatment after 2 months. Patients whose disease recurs after treatment will be taken off the study and will be referred back to their referring physician or to another study, if an appropriate one is available.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
138

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Apr 2003

Longer than P75 for phase_2

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

April 1, 2003

Completed
25 days until next milestone

First Submitted

Initial submission to the registry

April 26, 2003

Completed
2 days until next milestone

First Posted

Study publicly available on registry

April 28, 2003

Completed
7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2010

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2010

Completed
2.3 years until next milestone

Results Posted

Study results publicly available

August 14, 2012

Completed
Last Updated

October 23, 2012

Status Verified

October 1, 2012

Enrollment Period

7.1 years

First QC Date

April 26, 2003

Results QC Date

March 30, 2012

Last Update Submit

October 17, 2012

Conditions

Keywords

Adjuvant TherapyMART-1 PeptidesGP100 PeptideImmunologic ResponseMelanoma

Outcome Measures

Primary Outcomes (2)

  • Immunologic Response Rate

    Immunologic monitoring will be conducted using in vitro sensitization assays. The immunologic response in these assays will be considered positive if at least a two-fold increase in vaccine specific interferon gamma (y-IFN) secretion is seen between post vaccination specimens compared to the pre vaccination specimens.

    11 months

  • Response Rate

    Response is measured from the time measurement criteria are first met for complete response (CR) or partial response (PR) (whichever is first) until the first date that recurrent disease is objectively documented. Complete response is the disappearance of all target lesions. Partial response is at least a 30% decrease in the sum of the longest diameter (LD) of target lesions taking as reference the baseline sum LD.

    6 years

Secondary Outcomes (1)

  • Number of Participants With Adverse Events

    11 months

Study Arms (8)

Adj-2 MART-1: 27-35

EXPERIMENTAL

melanoma antigen recognized by T-cells (MART)-1:27-35 peptide every three weeks for four cycles (Arm I).

Drug: Montanide ISA 51Drug: Melanoma antigen recognized by T-cells (MART)-1: 27-35

Adj-2 HD IL-2 after MART-1: 27-35

EXPERIMENTAL

High-dose (HD) bolus interleukin-2 (IL-2) (720,000 IU/kg every 8 hours for up to 12 doses) after enrollment on Arm I (Arm IA)

Drug: Interleukin-2 (IL-2)Drug: Montanide ISA 51Drug: Melanoma antigen recognized by T-cells (MART)-1: 27-35

Adj-2 27-35 (27L) MART-1 (Mod9mer) peptide Q3wks x 4

EXPERIMENTAL

27-35(27L):melanoma antigen recognized by T-cells (MART)-1 peptide every three weeks for four cycles (Arm II).

Drug: Montanide ISA 51Drug: 27-35 (27L): melanoma antigen recognized by T-cells (MART)-1

Adj-2 HD IL-2 after 27-35 (27L): MART-1 (Mod9mer)

EXPERIMENTAL

High-dose (HD) bolus interleukin-2 (IL-2) (720,000 IU/kg every 8 hours for up to 12 doses) after enrollment on Arm II (Arm IIA)

Drug: Interleukin-2 (IL-2)Drug: Montanide ISA 51Drug: 27-35 (27L): melanoma antigen recognized by T-cells (MART)-1

Adj-2 MART-1: 26-35 (27L) (Mod10mer) peptide Q3wks x 4

EXPERIMENTAL

melanoma antigen recognized by T-cells (MART)-1:26-35(27L) peptide every three weeks for four cycles (Arm III).

Drug: Montanide ISA 51Drug: melanoma antigen recognized by T-cells (MART)-1: 26-35(27L)

Adj-2 HD IL-2 after MART-1: 26-35 (27L) (Mod10mer)

EXPERIMENTAL

High-dose (HD) bolus interleukin-2 (IL-2) (720,000 IU/kg every 8 hours for up to 12 doses) after enrollment on Arm III (Arm IIIA)

Drug: Interleukin-2 (IL-2)Drug: Montanide ISA 51Drug: melanoma antigen recognized by T-cells (MART)-1: 26-35(27L)

Adj-2 27-35 (27L): MART-1 + gp100: 209-217 (210M) Q3wks x 4

EXPERIMENTAL

27-35(27L):melanoma antigen recognized by T-cells (MART)-1 peptide plus the gp100:209-217(210M) peptide emulsified together every three weeks for four cycles (Arm IV).

Drug: Glycoprotein 100 (GP100): 209-217 (210M)Drug: Montanide ISA 51Drug: 27-35 (27L): melanoma antigen recognized by T-cells (MART)-1

Adj-2 HD IL-2 after 27-35 (27L): MART-1 + gp209-2M

EXPERIMENTAL

High-dose (HD) bolus interleukin-2 (IL-2) (720,000 IU/kg every 8 hours for up to 12 doses) after enrollment on Arm IV (Arm IVA)

Drug: Interleukin-2 (IL-2)Drug: Montanide ISA 51Drug: 27-35 (27L): melanoma antigen recognized by T-cells (MART)-1

Interventions

Adj-2 27-35 (27L): MART-1 + gp100: 209-217 (210M) Q3wks x 4

720,000 IU/kg as an intravenous bolus over a 15 minute period every 8 hours and continuing for up to 4 days (a maximum of 12 doses).

Also known as: Interleukin-2
Adj-2 HD IL-2 after 27-35 (27L): MART-1 (Mod9mer)Adj-2 HD IL-2 after 27-35 (27L): MART-1 + gp209-2MAdj-2 HD IL-2 after MART-1: 26-35 (27L) (Mod10mer)Adj-2 HD IL-2 after MART-1: 27-35
Adj-2 27-35 (27L) MART-1 (Mod9mer) peptide Q3wks x 4Adj-2 27-35 (27L): MART-1 + gp100: 209-217 (210M) Q3wks x 4Adj-2 HD IL-2 after 27-35 (27L): MART-1 (Mod9mer)Adj-2 HD IL-2 after 27-35 (27L): MART-1 + gp209-2MAdj-2 HD IL-2 after MART-1: 26-35 (27L) (Mod10mer)Adj-2 HD IL-2 after MART-1: 27-35Adj-2 MART-1: 26-35 (27L) (Mod10mer) peptide Q3wks x 4Adj-2 MART-1: 27-35
Adj-2 HD IL-2 after MART-1: 27-35Adj-2 MART-1: 27-35
Adj-2 27-35 (27L) MART-1 (Mod9mer) peptide Q3wks x 4Adj-2 27-35 (27L): MART-1 + gp100: 209-217 (210M) Q3wks x 4Adj-2 HD IL-2 after 27-35 (27L): MART-1 (Mod9mer)Adj-2 HD IL-2 after 27-35 (27L): MART-1 + gp209-2M
Adj-2 HD IL-2 after MART-1: 26-35 (27L) (Mod10mer)Adj-2 MART-1: 26-35 (27L) (Mod10mer) peptide Q3wks x 4

Eligibility Criteria

Age7 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Human leukocyte antigens (HLA-A)\*0201 patients, age greater than or equal to 16 years, with lesions greater than or equal to 1.5 mm in thickness, or greater than or equal to 1 positive lymph node, or ulcerated lesions, or local recurrence, or completely resected metastatic melanoma, within 6 months of surgical resection will be considered. Patients must be clinically disease free at the time of protocol entry as documented by radiologic studies within 6 weeks of patient entry.
  • Serum creatinine of 2.0 mg/dl or less.
  • Total bilirubin 1.6 mg/dl or less, except for patients with Gilbert's Syndrome who must have a total bilirubin less than 3.0 mg/dl.
  • White blood cell (WBC) 3000/mm\^3 or greater.
  • Platelet count 90,000 mm\^3 or greater.
  • Serum aspartate aminotransferase (AST)/alanine aminotransferase (ALT) less than three times normal.
  • Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1.
  • Patients of both genders must be willing to practice effective birth control during this trial because the potential for teratogenic effects are unknown.
  • Patients may have had prior adjuvant treatment with immunotherapy, including interferon, or may have had treatment for metastatic disease and are now no evidence of disease (NED), including chemotherapy or biotherapy, as long as 3 weeks have elapsed since prior systemic therapy.

You may not qualify if:

  • Patients will be excluded:
  • who have ocular or mucosal melanoma.
  • who are undergoing or have undergone in the past 3 weeks any systemic therapy except surgery for their cancer, and must have recovered from any adverse effects of treatment prior to entry, other than those that do not have clinical implications, e.g. vitiligo, alopecia.
  • have active systemic infections, autoimmune disease or any known immunodeficiency disease.
  • who require systemic steroid therapy.
  • who are pregnant or breastfeeding.
  • who are known to be positive for hepatitis B surface antigen (B(s)AG) or human immunodeficiency virus (HIV) antibody.
  • who have any form of active primary or secondary immunodeficiency or who have not recovered immune competence after chemotherapy or radiation therapy.
  • who have previously been immunized with melanoma antigen recognized by T-cells (MART)-1.
  • who have known hypersensitivity to any of the agents used in this study.
  • ELIGIBILITY FOR ADMINISTRATION OF Interleukin-2 (IL-2):
  • Patients who develop progressive disease while receiving peptide alone must meet the following criteria to be eligible to receive Interleukin-2 (IL-2):
  • Patients must have measurable metastatic melanoma.
  • Patients may not have active major medical illnesses such as cardiac ischemia, myocardial infarction, cardiac arrhythmias, obstructive or restrictive pulmonary disease.
  • Patients with recent prolonged history of cigarette smoking or symptoms of respiratory dysfunction must have a normal pulmonary function test as evidenced by a forced expiratory volume 1 (FEV 1) greater than 60% predicted.
  • +6 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

National Cancer Institute (NCI)

Bethesda, Maryland, 20892, United States

Location

Related Publications (1)

  • Kawakami Y, Eliyahu S, Delgado CH, Robbins PF, Rivoltini L, Topalian SL, Miki T, Rosenberg SA. Cloning of the gene coding for a shared human melanoma antigen recognized by autologous T cells infiltrating into tumor. Proc Natl Acad Sci U S A. 1994 Apr 26;91(9):3515-9. doi: 10.1073/pnas.91.9.3515.

    PMID: 8170938BACKGROUND

Related Links

MeSH Terms

Conditions

Melanoma

Interventions

Interleukin-2montanide ISA 51

Condition Hierarchy (Ancestors)

Neuroendocrine TumorsNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasmsNeoplasms, Nerve TissueNevi and MelanomasSkin NeoplasmsNeoplasms by SiteSkin DiseasesSkin and Connective Tissue Diseases

Intervention Hierarchy (Ancestors)

InterleukinsCytokinesIntercellular Signaling Peptides and ProteinsPeptidesAmino Acids, Peptides, and ProteinsLymphokinesProteinsBiological Factors

Results Point of Contact

Title
Steven A. Rosenberg, M.D.
Organization
National Cancer Institute, National Institutes of Health

Study Officials

  • Steven A Rosenberg, M.D.

    National Cancer Institute, National Institutes of Health

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
NIH
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Dr. Steven Rosenberg

Study Record Dates

First Submitted

April 26, 2003

First Posted

April 28, 2003

Study Start

April 1, 2003

Primary Completion

May 1, 2010

Study Completion

May 1, 2010

Last Updated

October 23, 2012

Results First Posted

August 14, 2012

Record last verified: 2012-10

Locations