NCT00041717

Brief Summary

Normally, nerve fibers carry electrical impulses through the spinal cord, providing communication between the brain and the arms and legs. In people with spinal cord injury, some fibers may be destroyed at the site of injury, while others remain connected but do not work correctly to carry electrical impulses. As a result, subjects with an incomplete spinal cord injury may have spasticity which is muscle spasms or muscle stiffness that makes movement difficult. Fampridine-SR is an experimental drug that increases the ability of the nerve to conduct electrical impulses. This study will examine the effects of Fampridine-SR on moderate to severe lower-limb spasticity, as well as the effects on bodily functions such as bladder control, bowel function and sexual function. The study will also examine the possible risks of taking Fampridine-SR.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
213

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Jul 2002

Geographic Reach
2 countries

45 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

July 1, 2002

Completed
11 days until next milestone

First Submitted

Initial submission to the registry

July 12, 2002

Completed
4 days until next milestone

First Posted

Study publicly available on registry

July 16, 2002

Completed
1.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 1, 2004

Completed
3 months until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2004

Completed
9.1 years until next milestone

Results Posted

Study results publicly available

May 31, 2013

Completed
Last Updated

January 14, 2020

Status Verified

April 1, 2013

Enrollment Period

1.6 years

First QC Date

July 12, 2002

Results QC Date

February 26, 2013

Last Update Submit

January 6, 2020

Conditions

Keywords

spinal cord injurymuscle spasticity

Outcome Measures

Primary Outcomes (2)

  • Double-blind Change From Baseline in Ashworth Score Evaluating Spasticity

    The Ashworth Score is the average rating (based on a scale of 1 to 5) of four lower extremity muscle groups; left and right knee flexors and extensors (hamstrings and quadriceps muscles). A higher Ashworth Score indicates a greater degree of abnormal muscle tone (spasticity) and a negative change in score indicates improvement.

    Baseline (visits 2,3) average score days 7,14 and double blind treatment period (visits 4-7) average score days 28-98

  • Double-blind Change From Baseline in Subject's Global Impression (SGI) of Treatment

    This questionnaire asked the patient to evaluate the effects of investigational drug on his/her quality of life during the preceding week using a 7-point scale (from 1=terrible to 7=delighted). A positive change score in SGI indicates improved outcome.

    Baseline (visits 2,3) average score days 7,14 and double blind treatment period (visits 4-7) average score days 28-98

Study Arms (2)

fampridine-SR 50mg/day

ACTIVE COMPARATOR
Drug: Fampridine-SR

Placebo

PLACEBO COMPARATOR
Other: Placebo

Interventions

25mg bid (twice daily)

fampridine-SR 50mg/day
PlaceboOTHER

Placebo

Placebo

Eligibility Criteria

Age18 Years - 70 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Incomplete traumatic Spinal Cord Injury (at least 18 months prior and stable for 6 months)
  • Moderate to severe lower-limb spasticity
  • Able to give informed consent and willing to comply with protocol

You may not qualify if:

  • Pregnancy
  • History of seizures
  • Existing or history of frequent Urinary Tract Infections
  • History of drug or alcohol abuse
  • Allergy to pyridine-containing substances
  • Received a botox injection 4 months prior to study
  • Received an investigational drug within 30 days
  • Previously treated with 4-aminopyridine (4-AP)
  • Not on stable medication dosing in 3 weeks prior to study
  • Abnormal ECG or laboratory value at screening

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (45)

Lakeshore Rehabilitation Hospital

Birmingham, Alabama, 35209, United States

Location

Barrow Neurological Institute

Phoenix, Arizona, 85013, United States

Location

Baptist Medical Center

Little Rock, Arkansas, 72205, United States

Location

VA Palo Alto Health Care System

Palo Alto, California, 94304, United States

Location

Neuro-Therapeutics, Inc

Pasadena, California, 91005, United States

Location

Neurology Associates, P.A.

Wilmington, Delaware, 19806, United States

Location

National Rehabilitation Hospital

Washington D.C., District of Columbia, 20010, United States

Location

Miami Center to Cure Paralysis at the Univ. of Miami School of Medicine

Miami, Florida, 33136, United States

Location

Rehabilitation Hospital

Sunrise, Florida, 33351, United States

Location

Shepherd Spinal Center

Atlanta, Georgia, 30309, United States

Location

Rehabilitation Institute of Chicago

Chicago, Illinois, 60611, United States

Location

Advocate Christ Medical Center-Dept. of Physical Medicine & Rehabilitation-EMG

Oak Lawn, Illinois, 60453, United States

Location

Springfield Clinic-Neuroscience Institute

Springfield, Illinois, 62702, United States

Location

Spaulding Rehabilitation Hospital

Boston, Massachusetts, 02114, United States

Location

HEALTHSOUTH Braintree Rehabilitation Hospital

Braintree, Massachusetts, 02185, United States

Location

HEALTHSOUTH New England Rehabilitation Hospital

Woburn, Massachusetts, 01801, United States

Location

Mary Free Bed Hospital & Rehabilitation Center

Grand Rapids, Michigan, 49503, United States

Location

Mayo Clinic

Rochester, Minnesota, 55905, United States

Location

Washington University School of Medicine, Div. of Rehab/Neurology

St Louis, Missouri, 63110, United States

Location

Montana Neuroscience

Missoula, Montana, 59802, United States

Location

Kessler Institute of Rehabilitation

West Orange, New Jersey, 07052, United States

Location

The Burke Rehabilitation Hospital

White Plains, New York, 10605, United States

Location

UNC Chapel Hill

Chapel Hill, North Carolina, 27599, United States

Location

East Carolina University

Greenville, North Carolina, 27858, United States

Location

Wake Forest University

Winston-Salem, North Carolina, 27157, United States

Location

Clinical Research Services

Bismarck, North Dakota, 58501, United States

Location

Drake Center

Cincinnati, Ohio, 45216, United States

Location

Cleveland VAMC

Cleveland, Ohio, 44106, United States

Location

Good Shepherd Rehabilitation

Allentown, Pennsylvania, 18103, United States

Location

Bryn Mawr Rehabilitation Hospital

Malvern, Pennsylvania, 19355, United States

Location

University of Pittsburgh

Pittsburgh, Pennsylvania, 15213, United States

Location

HEALTHSOUTH Harmarville Rehabilitation Hospital

Pittsburgh, Pennsylvania, 15238, United States

Location

Northeastern Rehabilitation Associates

Scranton, Pennsylvania, 18501, United States

Location

Rehabilitation Services University of Utah Hospitals and Clinics

Salt Lake City, Utah, 84132, United States

Location

Hampton VA Hospital

Hampton, Virginia, 23667, United States

Location

Richmond VA Medical Center (Hunter Holmes McGuire)

Richmond, Virginia, 23249, United States

Location

CAMC Health Education & Research Institute

Charleston, West Virginia, 25304, United States

Location

Foothills Provincial General Hospital

Calgary, Alberta, T2N 2T9, Canada

Location

Glenrose Rehabilitation Hospital

Edmonton, Alberta, T5G 0B7, Canada

Location

G.F. Strong Rehabilitation Centre

Vancouver, British Columbia, V5Z 2G9, Canada

Location

Stan Cassidy Centre for Rehabilitation

Fredericton, New Brunswick, E3B 4R3, Canada

Location

QEII HSC-Nova Scotia Rehabilitation Centre

Halifax, Nova Scotia, B3M 4K4, Canada

Location

Parkwood Hospital Site, St. Joseph's Health Care

London, Ontario, N6C 5J1, Canada

Location

The Rehabilitation Centre

Ottawa, Ontario, K1H 8M2, Canada

Location

Toronto Rehabilitation Institute, Lyndhurst Centre

Toronto, Ontario, M5G 3V9, Canada

Location

Related Links

MeSH Terms

Conditions

Spinal Cord InjuriesMuscle Spasticity

Interventions

4-Aminopyridine

Condition Hierarchy (Ancestors)

Spinal Cord DiseasesCentral Nervous System DiseasesNervous System DiseasesTrauma, Nervous SystemWounds and InjuriesMuscular DiseasesMusculoskeletal DiseasesMuscle HypertoniaNeuromuscular ManifestationsNeurologic ManifestationsSigns and SymptomsPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

AminopyridinesAminesOrganic ChemicalsPyridinesHeterocyclic Compounds, 1-RingHeterocyclic Compounds

Results Point of Contact

Title
Andrew Blight, Ph.D. Chief Scientific Officer
Organization
Acorda Therapeutics, Inc.

Study Officials

  • Andrew Blight

    Acorda Therapeutics

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 12, 2002

First Posted

July 16, 2002

Study Start

July 1, 2002

Primary Completion

February 1, 2004

Study Completion

May 1, 2004

Last Updated

January 14, 2020

Results First Posted

May 31, 2013

Record last verified: 2013-04

Locations