NCT00005098

Brief Summary

OBJECTIVES: I. Establish cell lines from patients with alpha 1-antitrypsin deficiency in order to examine genetic traits that predispose to liver injury.

Trial Health

35
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
160

participants targeted

Target at P50-P75 for all trials

Geographic Reach
1 country

1 active site

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

March 1, 1999

Completed
1.1 years until next milestone

First Submitted

Initial submission to the registry

April 6, 2000

Completed
1 day until next milestone

First Posted

Study publicly available on registry

April 7, 2000

Completed
Last Updated

June 24, 2005

Status Verified

May 1, 2002

First QC Date

April 6, 2000

Last Update Submit

June 23, 2005

Conditions

Keywords

alpha 1-antitrypsin deficiencygenetic diseases and dysmorphic syndromesrare disease

Eligibility Criteria

Age0 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)
* Alpha 1-antitrypsin deficiency

Contact the study team to discuss eligibility requirements. They can help determine if this study is right for you.

Sponsors & Collaborators

Study Sites (1)

Children's Hospital of Pittsburgh

Pittsburgh, Pennsylvania, 15213, United States

Location

MeSH Terms

Conditions

alpha 1-Antitrypsin DeficiencyGenetic Diseases, InbornRare Diseases

Condition Hierarchy (Ancestors)

Liver DiseasesDigestive System DiseasesLung DiseasesRespiratory Tract DiseasesCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesSubcutaneous EmphysemaEmphysemaPathologic ProcessesPathological Conditions, Signs and SymptomsDisease Attributes

Study Officials

  • David H. Perlmutter

    University of Pittsburgh

    STUDY CHAIR

Study Design

Study Type
observational
Sponsor Type
NIH

Study Record Dates

First Submitted

April 6, 2000

First Posted

April 7, 2000

Study Start

March 1, 1999

Last Updated

June 24, 2005

Record last verified: 2002-05

Locations