NCT00003535

Brief Summary

RATIONALE: Current therapies for children with recurrent/progressive high grade gliomas provide very limited benefit to the patient. The anti-cancer properties of Antineoplaston therapy suggest that it may prove beneficial in the treatment of children with recurrent/progressive high grade gliomas. PURPOSE: This study is being performed to determine the effects (good and bad) that Antineoplaston therapy has on children (\> 6 months of age) with recurrent/progressive high grade gliomas.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
9

participants targeted

Target at below P25 for phase_2

Timeline
Completed

Started Apr 1994

Typical duration for phase_2

Geographic Reach
1 country

1 active site

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

April 1, 1994

Completed
3.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 1, 1998

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

January 1, 1998

Completed
1.8 years until next milestone

First Submitted

Initial submission to the registry

November 1, 1999

Completed
3.2 years until next milestone

First Posted

Study publicly available on registry

January 27, 2003

Completed
14.9 years until next milestone

Results Posted

Study results publicly available

December 13, 2017

Completed
Last Updated

March 21, 2018

Status Verified

March 1, 2018

Enrollment Period

3.8 years

First QC Date

November 1, 1999

Results QC Date

August 1, 2017

Last Update Submit

March 7, 2018

Conditions

Keywords

childhood anaplastic astrocytomachildhood glioblastoma multiforme

Outcome Measures

Primary Outcomes (1)

  • Number of Participants With Objective Response

    Objective response rate per Response Assessment in Neuro-Oncology (RANO) for target lesions and assessed by MRI: Complete Response (CR), disappearance of all disease sustained for at least four weeks; Partial Response (PR), \>=50% decrease in the sum of the products of of the greatest perpendicular diameters of all measurable enhancing lesions, sustained for at least four weeks.

    12 months

Secondary Outcomes (1)

  • Percentage of Participants Who Survived

    6 months, 12 months, 24 months

Study Arms (1)

Antineoplaston therapy

EXPERIMENTAL

Antineoplaston therapy (Atengenal + Astugenal) by IV infusion every four hours for at least 12 months. Study subjects receive increasing dosages of Atengenal and Astugenal until the maximum tolerated dose is reached.

Drug: Antineoplaston therapy (Atengenal + Astugenal)

Interventions

Children with a recurrent/progressive high grade glioma will receive Antineoplaston therapy (Atengenal + Astugenal).

Also known as: A10 (Atengenal); AS2-1 (Astugenal)
Antineoplaston therapy

Eligibility Criteria

Age6 Months - 18 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Histologically confirmed high-grade glioma (glioblastoma multiforme or anaplastic astrocytoma) that is recurrent or progressive or with residual tumor after standard therapy, including radiotherapy
  • Measurable tumor by MRI scan performed within two weeks prior to study entry
  • Male or female patients
  • Children 6 months to 17 years
  • Performance status: Karnofsky 60-100%
  • Life expectancy of at least 2 months
  • WBC greater than 1,500/mm\^3
  • Platelet count greater than 50,000/mm\^3
  • No evidence of hepatic or renal insufficiency and a total bilirubin and serum creatinine no greater than 2.5 mg/dL and SGOT/SGPT no greater than 5 times upper limit of normal
  • Must have recovered from adverse effect of previous therapy
  • At least 8 weeks elapsed since last dose of radiation
  • At least 4 weeks elapsed since last dose of chemotherapy (6 weeks for nitrosoureas)
  • Corticosteroids permitted using the smallest dose that is compatible with preservation of optimal neurologic function
  • Acceptable methods of birth control (in females of child-bearing potential or in sexually active males)during and up to four weeks following completion of study

You may not qualify if:

  • Prior A10 and AS2-1 treatment
  • Severe heart disease
  • Uncontrolled hypertension
  • Lung disease
  • Hepatic failure
  • Serious active infections, fever or other serious concurrent disease that would interfere with the evaluation of the treatment drug.
  • Pregnant or nursing
  • Serious concurrent disease
  • Concurrent antineoplastic or immunomodulatory agents

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Burzynski Clinic

Houston, Texas, 77055-6330, United States

Location

Related Links

MeSH Terms

Conditions

GliomaAstrocytoma

Interventions

antineoplaston A10antineoplaston AS 2-1

Condition Hierarchy (Ancestors)

Neoplasms, NeuroepithelialNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasmsNeoplasms, Glandular and EpithelialNeoplasms, Nerve Tissue

Results Point of Contact

Title
S. R. Burzynski, MD, PhD
Organization
Burzynski Research Institute, Inc.

Study Officials

  • Stanislaw R. Burzynski, MD, PhD

    Burzynski Research Institute

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 1, 1999

First Posted

January 27, 2003

Study Start

April 1, 1994

Primary Completion

January 1, 1998

Study Completion

January 1, 1998

Last Updated

March 21, 2018

Results First Posted

December 13, 2017

Record last verified: 2018-03

Data Sharing

IPD Sharing
Will not share

Locations