Key Highlights

Risk & Performance

Pipeline Risk Assessment

Pipeline Risk Assessment

Based on historical performance

High Risk

Score: 100/100

Failure Rate

56.9%

33 terminated/withdrawn out of 58 trials

Success Rate

38.9%

-47.6% vs industry average

Late-Stage Pipeline

0%

0 trials in Phase 3/4

Results Transparency

0%

0 of 21 completed trials have results

Key Signals

6 terminated27 withdrawn

Enrollment Performance

Analytics

No phase data available

Activity Timeline

Global Presence

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Clinical Trials (58)

Showing 20 of 58 trials
NCT03866603Completed

Rostock International Parkinson's Disease Study (ROPAD)

Role: lead

NCT05075187Completed

Epidemiological Study in FRONtoTemporal Dementia

Role: lead

NCT03237494Completed

TRAMmoniTTR Study Genetic Screening of an At-risk Population for hATTR and Monitoring of TTR Positive Subjects

Role: lead

NCT05526664Active Not Recruiting

Omics Gaucher Study: Multiomic Approach

Role: lead

NCT06040008Completed

Investigating the Impact of Environmental Factors on the Transcriptomics Profile in Healthy Individuals

Role: lead

NCT01536327Withdrawn

Biomarker for Metachromatic Leukodystrophy (BioMeta) Disease

Role: lead

NCT02837523Withdrawn

Biomarker for Cystinosis Disease: BioCystinosis (BioCystinosis)

Role: lead

NCT02298647Withdrawn

Biomarker for Gangliosidosis: BioGM1/BioGM2 (BioGM1/GM2)

Role: lead

NCT02712138Withdrawn

Biomarker for Gilbert Disease (BioGilbert)

Role: lead

NCT02778295Withdrawn

Biomarker for Patients With Fabry Disease (BioFabry)

Role: lead

NCT02298712Withdrawn

Biomarker for Hurler Disease (BioHurler)

Role: lead

NCT02298699Withdrawn

Biomarker for Sly Disease (MPS VII) (BioSly)

Role: lead

NCT01425489Withdrawn

Biomarker for Krabbe Disease (BioKrabbe)

Role: lead

NCT02603042Withdrawn

Biomarker for Hypophosphatasia Disease (BioHypophos)

Role: lead

NCT03284658Withdrawn

Biomarker for the Early Diagnosis and Monitoring in Tyrosinemia Type 1 (BioTyrosin)

Role: lead

NCT02298673Withdrawn

Biomarker for Mucolipidosis Disorder Type I, II, III, IV (BioML)

Role: lead

NCT01458613Withdrawn

Biomarker for Maroteaux-Lamy Disease (BioMaroteaux)

Role: lead

NCT02298686Withdrawn

Biomarker for Sanfilippo Type A-B-C-D Disease (BioSanfilippo)

Role: lead

NCT01306604Withdrawn

Biomarker for Niemann Pick Type C Disease (BioNPC)

Role: lead

NCT01331642Withdrawn

Biomarker for Gaucher Disease: BioGaucher (BioGaucher)

Role: lead