Research Impact

h-index

N/A

Research impact score

Publications

0

Total publications

Trial Results

0

Published trial results

Citations

0

Total citations

Drug Portfolio

MIXED(1)
1 unique interventions1 categories

Analytics

Trial Phases

Phase 11
Phase 21

Trial Status

Completed1

Role Distribution

Other Roles1

Activity Timeline

Research Network

Collaboration Network

1 collaborators·0 connections
Network Legend
KOL
Current Investigator
CO
High-influence Collaborator
CO
Collaborator
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Similar Key Opinion Leaders

Discover other key opinion leaders with similar research profiles, therapeutic areas, and collaboration networks.

10 similar investigators found

Ronald G. Crystal, MD

Weill Medical College of Cornell University

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Ronald G Crystal, MD

Weill Medical College of Cornell University

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Shared therapeutic areas:

Juvenile Neuronal Ceroid LipofuscinosisLate-Infantile Neuronal Ceroid Lipofuscinosis
Similarity Score15%

Ronald Crystal, MD

Weill Medical College of Cornell University

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6 trials

Shared therapeutic areas:

Juvenile Neuronal Ceroid LipofuscinosisLate-Infantile Neuronal Ceroid Lipofuscinosis
Similarity Score15%

An N Dang Do, M.D.

Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)

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Juvenile Neuronal Ceroid Lipofuscinosis
Similarity Score8%

Laura Andres-Martin, PhD

New York Stem Cell Foundation Research Institute

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Juvenile Neuronal Ceroid Lipofuscinosis
Similarity Score8%

Mitchell S Cairo, MD

New York Medical College

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Juvenile Neuronal Ceroid Lipofuscinosis
Similarity Score8%

Kathrin C Meyer, PhD

Neela Therapeutics

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Shared therapeutic areas:

Juvenile Neuronal Ceroid Lipofuscinosis
Similarity Score8%

Gary D. Clark, MD

Texas Children Hospital

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1 trials

Shared therapeutic areas:

Juvenile Neuronal Ceroid Lipofuscinosis
Similarity Score8%

Erika F Augustine, MD

University of Rochester

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Shared therapeutic areas:

Juvenile Neuronal Ceroid Lipofuscinosis
Similarity Score8%

Publications (0)

No publications found for this investigator.

Clinical Trials (1)

Showing 1 of 1 trials

NCT01907087Phase 1/2StudyDirector

A Phase 1/2 Open-Label Dose-Escalation Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Efficacy of Intracerebroventricular BMN 190 in Patients With Late-Infantile Neuronal Ceroid Lipofuscinosis (CLN2) Disease

Batten DiseaseCLN2 DiseaseJansky-Bielschowsky Disease+1 more
Completed

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