Batten Disease

Investigations of Juvenile Neuronal Ceroid Lipofuscinosis

Longitudinal Study of Neurodegenerative Disorders

Examining Developmental Outcomes of Children Diagnosed With CLN2 Disease

Long-Term Follow Up of CLN6 Batten Disease Subjects Following Gene Transfer

Clinical and Neuropsychological Investigations in Batten Disease

An Open-label Safety, Pharmacokinetic, and Efficacy Study of Miglustat for the Treatment of Subjects With Batten Ceroid Lipofuscinosis, Neuronal 3 (CLN3) Disease

UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells

Gene Therapy for Children With CLN3 Batten Disease

Natural History of Neuronal Ceroid Lipofuscinosis, Batten's CLN6 Diseae

Natural History Study of Batten Disease

Inherited Retinal Degenerative Disease Registry

NYSCF Scientific Discovery Biobank

A Safety, Tolerability, and Efficacy Study of BMN 190 in Pediatric Patients < 18 Years of Age With CLN2 Disease

Human Placental-Derived Stem Cell Transplantation

An Extension Study to Evaluate the Long-Term Efficacy and Safety of BMN 190 in Patients With CLN2 Disease

Natural History and Longitudinal Clinical Assessments in NCL / Batten Disease, the International DEM-CHILD Database

Safety Study of a Gene Transfer Vector (Rh.10) for Children With Late Infantile Neuronal Ceroid Lipofuscinosis (LINCL)

AAVRh.10 Administered to Children With Late Infantile Neuronal Ceroid Lipofuscinosis

Genotype-Phenotype Correlations of Late Infantile Neuronal Ceroid Lipofuscinosis

Safety Study of a Gene Transfer Vector for Children With Late Infantile Neuronal Ceroid Lipofuscinosis