Research Impact

h-index

N/A

Research impact score

Publications

Total publications

Trial Results

Published trial results

Citations

Total citations

Drug Portfolio

DIAGNOSTIC_TEST(1)

GENETIC(1)

SPK-3006

1 trial

phase_1_2

spark-therapeutics-inc

Neutralizing Antibody to SPK-3006 capsid

1 trial

not_applicable

spark-therapeutics-inc

2 unique interventions2 categories

Analytics

Trial Phases

Phase 11

Phase 21

Trial Status

Completed1

Other1

Role Distribution

Principal Investigator2

PI Rate100%

Activity Timeline

Clinical Trials (2)

NCT04093349Phase 1/2Active Not Recruiting

A Gene Transfer Study for Late-Onset Pompe Disease (RESOLUTE)

Acid Maltase DeficiencyGlycogen Storage Disease Type 2Glycogen Storage Disease Type II+4 more

PrincipalinvestigatorStart date: 2020-10-01

NCT03893240Not ApplicableCompleted

Neutralizing Antibody Seroprevalence Study With a Retrospective Component in Participants With Late-Onset Pompe Disease

Acid Maltase DeficiencyGlycogen Storage Disease Type 2LOPD+3 more

PrincipalinvestigatorStart date: 2019-06-12

Research Network

Collaboration Network

1 collaborators·0 connections

Network Legend

KOL

Current Investigator

High-influence Collaborator

Collaborator

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Research Areas & Affiliations

Therapeutic Areas

Acid Maltase Deficiency2 Glycogen Storage Disease Type II2 LOPD2 Lysosomal Storage Diseases2 Pompe Disease Late-Onset2

Affiliations

University of California Irvine Health

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Benedikt Schoser, MD

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Publications (0)

No publications found for this investigator.

Clinical Trials (2)

Showing 2 of 2 trials

NCT04093349Phase 1/2PrincipalInvestigator

A Gene Transfer Study for Late-Onset Pompe Disease (RESOLUTE)

Acid Maltase DeficiencyGlycogen Storage Disease Type 2Glycogen Storage Disease Type II+4 more

Active Not Recruiting

NCT03893240Not ApplicablePrincipalInvestigator

Neutralizing Antibody Seroprevalence Study With a Retrospective Component in Participants With Late-Onset Pompe Disease

Acid Maltase DeficiencyGlycogen Storage Disease Type 2LOPD+3 more

Completed

All 2 trials loaded