Pompe Disease Late-Onset

A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late Onset Pompe Disease (PROGRESS-GT LOPD)

Pompe Pregnancy Sub-Registry

A Study About Antibody Levels and Biomarkers in the Blood in People With Late-onset Pompe Disease

Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease

A Study to Assess the Long-term Safety and Efficacy of ATB200/AT2221 in Adult Subjects With Late-Onset Pompe Disease (LOPD)

Gene Transfer Study in Patients With Late Onset Pompe Disease

ZIP Study-OL Study of Safety, PK, Efficacy, PD, Immunogenicity of ATB200/AT2221 in Pediatrics Aged 0 to < 18 y.o. w/LOPD

Developing a Management Approach for Patients With "Late-Onset" Pompe Disease

A Study Comparing ATB200/AT2221 With Alglucosidase Alfa/Placebo in Adult Subjects With Late-onset Pompe Disease

Carbon-13 Magnetic Resonance Spectroscopy in Glycogen Storage Diseases

Evaluation of the Safety and Efficacy of Late-onset Pompe Disease Gene Therapy Drug

MSOT in Pompe Disease

A Gene Transfer Study for Late-Onset Pompe Disease (RESOLUTE)

Treatment Frequency Reduction in Pompe Disease

Evaluation of the Safety, Tolerability and Efficacy of Gene Therapy Drug for Late Onset Pompe Disease (LOPD)

Pompe & Pain - Study to Assess Nociceptive Pain in Adult Patients With Pompe Disease

Inspiratory Muscle Training (IMT) in Adult People With Pompe Disease

Neutralizing Antibody Seroprevalence Study With a Retrospective Component in Participants With Late-Onset Pompe Disease

Study Determining the Frequency of Duchenne Muscular Dystrophy and Late-onset Pompe Disease

Musculoskeletal Nociceptive Pain in Participants With Neuromuscular Disorders