Research Impact

h-index

N/A

Research impact score

Publications

0

Total publications

Trial Results

0

Published trial results

Citations

0

Total citations

Drug Portfolio

Analytics

Trial Phases

Phase 11
Phase 21

Trial Status

Completed3
Other1

Role Distribution

Principal Investigator4
PI Rate100%

Activity Timeline

Clinical Trials (4)

NCT01416467Completed
Characterization of the Patient Population With Galactosialidosis
Galactosialidosis
PrincipalinvestigatorStart date: 2012-02-08
NCT00513617Phase 2Completed
Effectiveness of Arginine as a Treatment for Sickle Cell Anemia
Anemia, Sickle Cell
Principalinvestigator
NCT05932914Not Yet Recruiting
Liver Biopsy Following Gene Therapy For Hemophilia
Hemophilia AHemophilia B
Principalinvestigator

Research Network

Collaboration Network

40 collaborators·66 connections
Network Legend
KOL
Current Investigator
CO
High-influence Collaborator
CO
Collaborator
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Research Areas & Affiliations

Affiliations

St. Jude Children's Research Hospital

Similar Key Opinion Leaders

Discover other key opinion leaders with similar research profiles, therapeutic areas, and collaboration networks.

10 similar investigators found

Program Director

CSL Behring

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12 trials

Shared therapeutic areas:

Hemophilia AHemophilia B
Similarity Score15%

Alessandra D'Azzo-Grosveld, PhD

St. Jude Children's Research Hospital

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1 trials

Shared therapeutic areas:

Galactosialidosis

Worked with same sponsors:

Assisi FoundationNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)+1 more
Collaborated on 1 trial
Similarity Score14%

Laura DeCastro, MD

Duke University

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2 trials

Shared therapeutic areas:

Anemia, Sickle Cell

Worked with same sponsors:

National Heart, Lung, and Blood Institute (NHLBI)UCSF Benioff Children's Hospital Oakland
Collaborated on 1 trial
Similarity Score14%

Lillian McMahon, MD

Boston Medical Center

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2 trials

Shared therapeutic areas:

Anemia, Sickle Cell

Worked with same sponsors:

National Heart, Lung, and Blood Institute (NHLBI)UCSF Benioff Children's Hospital Oakland
Collaborated on 1 trial
Similarity Score14%

Mary Fabry, MD

Albert Einstein College of Medicine

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1 trials

Shared therapeutic areas:

Anemia, Sickle Cell

Worked with same sponsors:

National Heart, Lung, and Blood Institute (NHLBI)UCSF Benioff Children's Hospital Oakland
Collaborated on 1 trial
Similarity Score14%

Thomas Moulton, MD

Children's Hospital of Montefiore

Related
1 trials

Shared therapeutic areas:

Anemia, Sickle Cell

Worked with same sponsors:

National Heart, Lung, and Blood Institute (NHLBI)UCSF Benioff Children's Hospital Oakland
Collaborated on 1 trial
Similarity Score14%

Carolyn Bigelow, MD

University of Mississippi Medical Center (Adult)

Related
1 trials

Shared therapeutic areas:

Anemia, Sickle Cell

Worked with same sponsors:

National Heart, Lung, and Blood Institute (NHLBI)UCSF Benioff Children's Hospital Oakland
Collaborated on 1 trial
Similarity Score14%

William Mentzer, MD

University of California, San Francisco

Related
1 trials

Shared therapeutic areas:

Anemia, Sickle Cell

Worked with same sponsors:

National Heart, Lung, and Blood Institute (NHLBI)UCSF Benioff Children's Hospital Oakland
Collaborated on 1 trial
Similarity Score14%

Joan Parkhurst Cain, MD

Children's Hospital of Oklahoma

Related
1 trials

Shared therapeutic areas:

Anemia, Sickle Cell

Worked with same sponsors:

National Heart, Lung, and Blood Institute (NHLBI)UCSF Benioff Children's Hospital Oakland
Collaborated on 1 trial
Similarity Score14%

Rathi Iyer, MD

University of Mississippi Medical Center (Pediatric)

Related
1 trials

Shared therapeutic areas:

Anemia, Sickle Cell

Worked with same sponsors:

National Heart, Lung, and Blood Institute (NHLBI)UCSF Benioff Children's Hospital Oakland
Collaborated on 1 trial
Similarity Score14%

Publications (0)

No publications found for this investigator.

Clinical Trials (4)

Showing 4 of 4 trials

NCT01416467PrincipalInvestigator

Characterization of the Patient Population With Galactosialidosis

Galactosialidosis
Completed
NCT00979238Phase 1PrincipalInvestigator

Dose-Escalation Study Of A Self Complementary Adeno-Associated Viral Vector For Gene Transfer in Hemophilia B

Hemophilia B
Completed
NCT00513617Phase 2PrincipalInvestigator

Effectiveness of Arginine as a Treatment for Sickle Cell Anemia

Anemia, Sickle Cell
Completed
NCT05932914PrincipalInvestigator

Liver Biopsy Following Gene Therapy For Hemophilia

Hemophilia AHemophilia B
Not Yet Recruiting

All 4 trials loaded