Research Impact

h-index

N/A

Research impact score

Publications

0

Total publications

Trial Results

0

Published trial results

Citations

0

Total citations

Drug Portfolio

Analytics

Trial Phases

Phase 22
Phase 32

Trial Status

Completed4

Role Distribution

Other Roles4

Activity Timeline

Research Network

Collaboration Network

1 collaborators·0 connections
Network Legend
KOL
Current Investigator
CO
High-influence Collaborator
CO
Collaborator
Click: view details
Double-click: go to profile
Drag: move node

Research Areas & Affiliations

Similar Key Opinion Leaders

Discover other key opinion leaders with similar research profiles, therapeutic areas, and collaboration networks.

10 similar investigators found

Celeste Decker, MD

BioMarin Pharmaceutical

Related
4 trials

Shared therapeutic areas:

Morquio A SyndromeMucopolysaccharidosis Type IV AMucopolysaccharidosis IVA+1 more

Worked with same sponsors:

BioMarin Pharmaceutical
Similarity Score24%

Ira J Fox, MD

University of Pittsburgh

Related
3 trials

Shared therapeutic areas:

Phenylketonurias
Similarity Score6%

Anita MacDonald, Professor

Birmingham Children´s Hospital

Related
2 trials

Shared therapeutic areas:

Phenylketonurias
Similarity Score6%

Tippi C MacKenzie, MD

University of California, San Francisco

Related
2 trials

Shared therapeutic areas:

Mucopolysaccharidosis IV A
Similarity Score6%

Desiree White, Ph.D.

Washington University School of Medicine

Related
2 trials

Shared therapeutic areas:

Phenylketonurias

Worked with same sponsors:

BioMarin Pharmaceutical
Similarity Score6%

Sylvia Stockler, MD

University of British Columbia

Related
1 trials

Shared therapeutic areas:

Phenylketonurias
Similarity Score6%

Heather W Saavedra, MS

The University of Texas Health Science Center, Houston

Related
2 trials

Shared therapeutic areas:

Phenylketonurias

Worked with same sponsors:

BioMarin Pharmaceutical
Similarity Score6%

Keiko Ueda, MPH, RD

Provincial Health Services Authority British Columbia

Related
1 trials

Shared therapeutic areas:

Phenylketonurias
Similarity Score6%

Sylvia Stockler-Ipsiroglu, MD

University of British Columbia

Related
1 trials

Shared therapeutic areas:

Phenylketonurias
Similarity Score6%

ali ismail, lecturer

Cairo University

Related
29 trials

Shared therapeutic areas:

Phenylketonurias
Similarity Score6%

Publications (0)

No publications found for this investigator.

Clinical Trials (4)

Showing 4 of 4 trials

NCT01275066Phase 3StudyDirector

A Double-Blind Study to Evaluate the Efficacy and Safety of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome)

MPS IV A
Completed
NCT01415427Phase 3StudyDirector

Long-Term Efficacy and Safety Extension Study of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome)

Morquio A SyndromeMPS IVAMucopolysaccharidosis IV A
Completed
NCT01515956Phase 2StudyDirector

Study of BMN 110 in Pediatric Patients < 5 Years of Age With Mucopolysaccharidosis IVA (Morquio A Syndrome)

Morquio A SyndromeMPS IVAMucopolysaccharidosis IVA
Completed
NCT01560286Phase 2StudyDirector

A Study to Evaluate Subcutaneously Administered rAvPAL-PEG in Patients With Phenylketonuria for 24 Weeks

Phenylketonuria
Completed

All 4 trials loaded