Research Impact

h-index

N/A

Research impact score

Publications

0

Total publications

Trial Results

0

Published trial results

Citations

0

Total citations

Drug Portfolio

MIXED(1)
GENETIC(1)
2 unique interventions2 categories

Analytics

Trial Phases

Phase 31

Trial Status

Recruiting1
Other1

Role Distribution

Other Roles2

Activity Timeline

Clinical Trials (2)

NCT06805695Recruiting
Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP)
Ornithine Transcarbamylase DeficiencyOrnithine Transcarbamylase Deficiency DiseaseUrea Cycle Disorders, Inborn
StudydirectorStart date: 2024-12-23
NCT06255782Phase 3Active Not Recruiting
An Open-label Study to Investigate ECUR-506 in Male Babies Less Than 9 Months of Age With Neonatal Onset OTC Deficiency
Ornithine Carbamoyltransferase Deficiency (Disorder)Ornithine Transcarbamylase DeficiencyOrnithine Transcarbamylase Deficiency Disease+1 more
StudydirectorStart date: 2024-04-08

Research Network

Collaboration Network

1 collaborators·0 connections
Network Legend
KOL
Current Investigator
CO
High-influence Collaborator
CO
Collaborator
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Similar Key Opinion Leaders

Discover other key opinion leaders with similar research profiles, therapeutic areas, and collaboration networks.

10 similar investigators found

Gloria Wong, MD

Q-Pharm Pty Ltd

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Ornithine Carbamoyltransferase Deficiency DiseaseUrea Cycle Disorders, Inborn
Similarity Score15%

Lindsay Burrage, MD, PhD

Baylor College of Medicine

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Mendel Tuchman, MD

Children's National Research Institute

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Margreet Wagenmakers

Erasmus Medical Center

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Ornithine Carbamoyltransferase Deficiency DiseaseUrea Cycle Disorders, Inborn
Similarity Score15%

Andrea Gropman, MD

Children's National Research Institute

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Urea Cycle Disorders, InbornOrnithine Carbamoyltransferase Deficiency Disease
Similarity Score15%

Andrea L Gropman, M.D.

Children's National Research Institute

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Ornithine Carbamoyltransferase Deficiency Disease
Similarity Score8%

Lyazzat M. Syrlybayeva, MD

West Kazakhstan Medical University

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Ornithine Carbamoyltransferase Deficiency Disease
Similarity Score8%

Vera Anastasoaie, MD

Boston Children's Hospital

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Urea Cycle Disorders, Inborn
Similarity Score8%

Ayca Kiykim

Istanbul University - Cerrahpasa

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Urea Cycle Disorders, Inborn
Similarity Score8%

Isabel Gonçalves, MD/Prof

Hospital Pediátrico de Coimbra (Portugal)

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Urea Cycle Disorders, Inborn
Similarity Score8%

Publications (0)

No publications found for this investigator.

Clinical Trials (2)

Showing 2 of 2 trials

NCT06805695StudyDirector

Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP)

Ornithine Transcarbamylase DeficiencyOrnithine Transcarbamylase Deficiency DiseaseUrea Cycle Disorders, Inborn
Recruiting
NCT06255782Phase 3StudyDirector

An Open-label Study to Investigate ECUR-506 in Male Babies Less Than 9 Months of Age With Neonatal Onset OTC Deficiency

Ornithine Carbamoyltransferase Deficiency (Disorder)Ornithine Transcarbamylase DeficiencyOrnithine Transcarbamylase Deficiency Disease+1 more
Active Not Recruiting

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