Usher Syndrome
13
4
4
4
Key Insights
Highlights
Success Rate
67% trial completion
Clinical Risk Assessment
Based on trial outcomes
High Risk
Score: 62/100
15.4%
2 terminated out of 13 trials
66.7%
-19.9% vs benchmark
15%
2 trials in Phase 3/4
25%
1 of 4 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.5%
Based on 4 completed trials
Clinical Trials (13)
A 24-Month Trial of NPI-001 for the Preservation of Photoreceptors in Retinitis Pigmentosa Associated With Usher Syndrome
A Study to Investigate the Safety of OpCT-001 in Adults Who Have Primary Photoreceptor Disease (CLARICO)
24-Month Trial of NPI-001 for the Preservation of Photoreceptors in Retinitis Pigmentosa Associated With Usher Syndrome
Inherited Retinal Degenerative Disease Registry
Observational Study to Investigate the Short-term Effects of Transcorneal Electrical Stimulation on Visual Performance
Natural History of Photoreceptor Degeneration in USH1B: Clinical Parameters and Validation of Functional Vision Tests in MYO7A
Auditory Neural Function in Implanted Patients With Usher Syndrome
Study of SAR421869 in Participants With Retinitis Pigmentosa Associated With Usher Syndrome Type 1B
Natural History and Genetic Studies of Usher Syndrome
Clinical and Genetic Testing of Patients With Usher Syndrome
Clinical and Genetic Examination of Usher Syndrome Patients' Cohort in Europe
Study of Dietary N-3 Fatty Acids in Patients With Retinitis Pigmentosa and Usher Syndrome
A Genetic Analysis of Usher Syndrome in Ashkenazi Jews