Telangiectasia, Hereditary Hemorrhagic
21
3
5
14
Key Insights
Highlights
Success Rate
93% trial completion (above average)
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 50/100
4.8%
1 terminated out of 21 trials
93.3%
+6.8% vs benchmark
10%
2 trials in Phase 3/4
21%
3 of 14 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.5%
Based on 14 completed trials
Clinical Trials (21)
Efficacy of Nintedanib for Treatment of Epistaxis in Hereditary Hemorrhagic Telangiectasia (HHT) Patients
Diagnostic Value of Ultra-low Dose Thoracic Scanner for the Pulmonary Arteriovenous Malformation Detection in HHT Patient
Efficacy of a Timolol Nasal Spray as a Treatment for Epistaxis in Hereditary Hemorrhagic Telangiectasia (HHT) - (TEMPO)
BABH Study: Efficacy and Safety of Bevacizumab on Severe Bleedings Associated With Hemorrhagic Hereditary Telangiectasia (HHT).
Efficacy of Nintedanib Per os as a Treatment for Epistaxis in HHT Disease.
Treatment of Hereditary Hemorrhagic Telangiectasia of the Nasal Mucosa by Intranasal Bevacizumab : Search for Effective Dose
Hereditary Hemorrhagic Telangiectasia and Neurovascular Manifestations, in the Danish HHT Database
Pomalidomide for the Treatment of Bleeding in HHT
Investigation of Plasma Proteins in Patients With Hereditary Haemorrhagic Telangiectasia and PAVMs
Case Notes Review on Patients With Hereditary Haemorrhagic Telangiectasia
Molecular Studies on Hereditary Haemorrhagic Telangiectasia Families
Investigation of Coagulation Parameters in Hereditary Haemorrhagic Telangiectasia
Study of Histological Samples From Patients With Hereditary Haemorrhagic Telangiectasia
Studies of White Blood Cells Derived From HHT Patients
The ELLIPSE Study: A Phase-1 Study Evaluating the Tolerance of Bevacizumab Nasal Spray to Treat Epistaxis in Hereditary Hemorrhagic Telangiectasia
Screening Behavior in Adults With Hereditary Hemorrhagic Telangiectasia
Study of Endothelial Cells in Patients With Hereditary Haemorrhagic Telangiectasia
ATERO : A Randomised Study With Tranexamic Acid in Epistaxis of Rendu Osler Syndrome
North American Study of Epistaxis in Hereditary Hemorrhagic Telangiectasia (HHT)
Evaluation of Pazopanib on Bleeding in Subjects With Hereditary Haemorrhagic Telangiectasia