Sickle Cell Disease (SCD)
23
5
6
6
Key Insights
Highlights
Success Rate
86% trial completion
Clinical Risk Assessment
Based on trial outcomes
Low Risk
Score: 27/100
4.3%
1 terminated out of 23 trials
85.7%
-0.8% vs benchmark
22%
5 trials in Phase 3/4
117%
7 of 6 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.6%
Based on 6 completed trials
Clinical Trials (23)
Standard of Care Comparative Arm of Phase 1/2 Gene Therapy Trial DREPAMIR" in Severe Sickle Cell Disease Patients
CPAP for Hypoxemic Acute Chest Syndrome in Sickle Cell Disease
Study of Two Doses of Crizanlizumab Versus Placebo in Adolescent and Adult Sickle Cell Disease Patients
Low Dose Bolus Ketamine For Use In Sickle Cell Pain Crisis
Risk Factors, Costs, and Impacts of ED Boarding
Epidemiology of Invasive Bacterial Infections in Children With Sickle Cell Disease in France Between 2020 and 2025
Comparing the Effectiveness of Matched Related Donor Hematopoietic Stem Cell Transplantation to Disease Modifying Therapy in Pediatric Patients With Sickle Cell Disease
Clinical and Biomarker Effects of Depot Medroxyprogesterone Acetate in Females With Sickle Cell Disease
Development of a Provider-Focused Intervention to Improve Health Outcomes in Pediatric Sickle Cell Disease
OMEGA-3-FATTY ACIDS IN CHILDREN WITH SICKLE CELL DISEASE
Sickle Cell Kidney Biorepository
Integrating Point of Care Testing (POCT) For Newborn Screening and Early Care for Sickle Cell Disease in Yopougon, Côte d'Ivoire
Study of Dose Confirmation and Safety of Crizanlizumab in Pediatric Sickle Cell Disease Patients
An Indian Multi-centric Phase IV Study to Assess the Safety of Crizanlizumab in Sickle Cell Disease Patients
Exploratory Study on Global Reflexology in Sickle Cell Disease
Megakaryocyte Heterogeneity in Sickle Cell Disease
Phenotypic and Transcriptomic Description of Megakaryocytes in Sickle Cell Patient
Relationship Between Biological Phenotype, Clinical Severity of Sickle Cell Disease, and Blood Coagulation
Safety, Efficacy, Pharmacokinetic, and Pharmacodynamic Study of ALXN1820 in Adult Participants With Sickle Cell Disease
Optimizing Hydroxyurea Dosage With Pharmakokinetic in Patients Suffering of Moderate to Severe Sickle Cell Anemia