Myasthenia Gravis, MuSK
4
3
3
0
Key Insights
Highlights
Treatment Research
2 treatments under study, led by Nmd670
Research Leaders
5 sponsors active, led by Alira Health
Related Conditions
Often studied with 17 related conditions
Clinical Risk Assessment
Based on trial outcomes
High Risk
Score: 90/100
25.0%
1 terminated out of 4 trials
0.0%
-86.6% vs benchmark
25%
1 trials in Phase 3/4
0%
1 of 0 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Clinical Trials (4)
Safety and Efficacy of 3 Dose Levels of NMD670 in Adult Patients With Myasthenia Gravis
AXIS MG Patient Registry
Myasthenia Gravis Foundation of America Global MG Patient Registry
Long Term Safety Study of Amifampridine Phosphate in MuSK-MG (Muscle Specific Tyrosine Kinase Myasthenia Gravis)
Research Network
Common Treatments
- Nmd6701
- Amifampridine Phosphate1
Active Sponsors
- Alira Health2
- NMD Pharma A/S1
- Catalyst Pharmaceuticals, Inc.1
- Autoimmune Neurology Alliance1
- Myasthenia Gravis Foundation of America1
Top Investigators
Alira Health
Yale University
University of Alabama at Birmingham
Yale University
Carlo Besta Neurological Institute
Related Conditions
- Myasthenia Gravis3
- Myasthenia Gravis Generalized2
- Myasthenia Gravis Thymectomy2
- Achr Myasthenia Gravis2
- Myasthenia Gravis Generalised2