Muscular Dystrophy
49
12
14
21
Key Insights
Highlights
Success Rate
91% trial completion (above average)
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 50/100
4.1%
2 terminated out of 49 trials
91.3%
+4.7% vs benchmark
2%
1 trials in Phase 3/4
14%
3 of 21 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.6%
Based on 21 completed trials
Clinical Trials (49)
Study of Inherited Neurological Disorders
Evaluating a New Knee-Ankle-Foot Brace to Improve Gait in Children With Movement Disorders
Investigational Use of Neuromuscular Ultrasound
A Study to Evaluate the Safety of AB-1003 (Previously LION-101) in Subjects With Genetic Confirmation of LGMD2I/R9 (Part1)
Evaluating VM100 Nutritional Supplement for Improving Quality of Life in Duchenne Muscular Dystrophy Patients
iBCI Optimization for Veterans With Paralysis
Study of Home Use of the Jaco Robotic Manipulation Device by Individuals With Tetraplegia
BrainGate2: Feasibility Study of an Intracortical Neural Interface System for Persons With Tetraplegia
Assessment of a Portable Digital Device for Quantified Analysis of Markerless Walking in Volunteers With Neuromuscular Diseases or Asymptomatic Volunteers
Vasodilator and Exercise Study for DMD (VASO-REx)
Nomad P-KAFO Study
Amino Acids and Exercise in FSHD
Clinical Trial Readiness Network FSHD France: Prospective 24 Months MRI Study
Evaluating Long-term Use of a Pediatric Robotic Exoskeleton (P.REX/Agilik) to Improve Gait in Children With Movement Disorders
Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry
Genetics of Cardiovascular and Neuromuscular Disease
Clinical Trial Readiness for the Dystroglycanopathies
Follow-up Study on Female Carriers With DMD Gene Variants
Effectiveness of 5-week Digital Respiratory Practice in Children With Duchenne and Becker Muscular Dystrophies.
Genetics of Pediatric-Onset Motor Neuron and Neuromuscular Diseases