Muscular Dystrophies
80
10
16
43
Key Insights
Highlights
Success Rate
90% trial completion (above average)
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 40/100
6.3%
5 terminated out of 80 trials
89.6%
+3.1% vs benchmark
11%
9 trials in Phase 3/4
23%
10 of 43 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.5%
Based on 43 completed trials
Clinical Trials (80)
Phase 2 Study of SAT-3247 in Pediatric Ambulatory Patients
ECoG BMI for Motor and Speech Control
Genetic and Physical Study of Childhood Nerve and Muscle Disorders
A Multi-Dimensional Model of cAre and transItion for Patients With cOmplex RAre Diseases
Managed Access Program for Del-zota in Participants With DMD Mutations Amenable to Exon 44 Skipping
Phase 1/2 Study of AOC 1020 in Participants With Facioscapulohumeral Muscular Dystrophy (FSHD)
Assessment of Safety and Acute Effects of a Lower-limb Powered Dermoskeleton in Patients With Neuromuscular Disorders
Assessment of Safety and Acute Effects of a Knee-hip Powered Soft Exoskeleton in Patients With Neuromuscular Disorders
Interfacing With NeuroTechnology to Expand Neural Throughput (INTENT)
Muscle Health Measurements Using Electrical Impedance Myography
Pro-inflammatory Cytokines in Facioscapulohumeral Muscular Dystrophy (CYTOKINE-FSH)
Long-Term Outcomes of Ataluren in Duchenne Muscular Dystrophy
Defining Clinical Endpoints in Limb Girdle Muscular Dystrophy (LGMD)
Observational Study to Observe Variations of Gait Parameters in Patients With Neuromuscular Diseases
A Study of Deramiocel (CAP-1002) in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular Dystrophy
Feasibility of the BrainGate2 Neural Interface System in Persons With Tetraplegia
Feasibility of the BrainGate2 Neural Interface System in Persons With Tetraplegia (BG-Speech-02)
Extension of AOC 1001-CS1 (MARINA) Study in Adult Myotonic Dystrophy Type 1 (DM1) Patients
Fear of Falling in Muscular Dystrophy
Defining Endpoints in Becker Muscular Dystrophy