Condition
Mucopolysaccharidosis IV
Total Trials
4
Recruiting
1
Active
1
Completed
1
Success Rate
50.0%-37% vs avg
Key Insights
Highlights
Success Rate
50% trial completion
Clinical Risk Assessment
Based on trial outcomes
High Risk
Score: 100/100
Termination Rate
25.0%
1 terminated out of 4 trials
Success Rate
50.0%
-36.5% vs benchmark
Late-Stage Pipeline
0%
0 trials in Phase 3/4
Results Transparency
0%
0 of 1 completed with results
Key Signals
50% success
Data Visualizations
Phase Distribution
Trial Status
Recruiting1
Completed1
Withdrawn1
Terminated1
Trial Success Rate
50.0%
Benchmark: 86.5%
Based on 1 completed trials
Clinical Trials (4)
Showing 4 of 4 trials
NCT06036693Recruiting
MPS (RaDiCo Cohort) (RaDiCo-MPS)
NCT02153255WithdrawnPrimary
Dynamic Gait Analysis in Children With Mucopolysaccharidosis Type IVa
NCT01752296Completed
Psychological Concomitants of Morquio Syndrome (The MAP Study)
NCT01675674Terminated
Study to Detect Unrecognized Mucopolysaccharidosis in Children Visiting Rheumatology, Hand or Skeletal Dysplasia Clinics
Showing all 4 trials