Condition
Methylmalonic Acidemia (MMA)
Total Trials
4
Recruiting
0
Active
0
Completed
0
Key Insights
Highlights
No notable highlights available yet
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 40/100
Termination Rate
0.0%
0 terminated out of 4 trials
Late-Stage Pipeline
25%
1 trials in Phase 3/4
Results Transparency
0%
0 of 0 completed with results
Key Signals
Data Visualizations
Phase Distribution
3Total
P 1 (2)
P 3 (1)
Trial Status
Not Yet Recruiting2
Withdrawn2
Clinical Trials (4)
Showing 4 of 4 trials
NCT07432880Not Yet RecruitingPrimary
A Prospective Study of Pediatric Participants up to 16 Years of Age With Methylmalonic Acidemia (MMA) Due to Mutations in the MMUT Gene
NCT07163364Phase 3Not Yet RecruitingPrimary
A Study to Evaluate the Effects and Safety of Hydroxocobalamin in Participants With Combined Methylmalonic Academia (cblC Type)
NCT05778877Phase 1WithdrawnPrimary
A Study to Evaluate the Safety, Tolerability, and Pharmacodynamics of SEL-302 in Pediatric Subjects With MMA
NCT03810690Phase 1WithdrawnPrimary
Open Label Study of mRNA-3704 in Patients With Isolated Methylmalonic Acidemia
Showing all 4 trials