Key Insights

Highlights

Success Rate

89% trial completion (above average)

Clinical Risk Assessment

Based on trial outcomes

Moderate Risk

Score: 37/100

Termination Rate

6.7%

2 terminated out of 30 trials

Success Rate

88.9%

+2.4% vs benchmark

Late-Stage Pipeline

3%

1 trials in Phase 3/4

Results Transparency

44%

7 of 16 completed with results

Key Signals

7 with results89% success

Data Visualizations

Phase Distribution

16Total
Not Applicable (6)
P 1 (6)
P 2 (3)
P 3 (1)

Trial Status

Completed16
Recruiting7
Active Not Recruiting3
Not Yet Recruiting2
Terminated2

Trial Success Rate

88.9%

Benchmark: 86.5%

Based on 16 completed trials

Clinical Trials (30)

Showing 20 of 20 trials
NCT06907875Phase 1RecruitingPrimary

A First-in-human Study of EPI-321 in Facioscapulohumeral Muscular Dystrophy

NCT03458832Active Not RecruitingPrimary

Clinical Trial Readiness to Solve Barriers to Drug Development in FSHD

NCT07435129Phase 2Not Yet RecruitingPrimary

Phase 2 Study Evaluating Apitegromab for the Treatment of FSHD

NCT06425445Not ApplicableCompletedPrimary

Quantitative Assessment of Orofacial Muscle Function in FSHD

NCT07409142Recruiting

BetterLife FSHD: A Patient-driven Health and Research Platform

NCT07038200Phase 3RecruitingPrimary

A Study to Evaluate Del-brax (Also Referred to as AOC 1020) in Participants With FSHD

NCT07331025CompletedPrimary

Ultrasound Detection of Early Facial Muscle Changes in FSHD: Thickness and Echo Intensity Findings

NCT05019625Recruiting

Biomarker Development for Muscular Dystrophies

NCT00082108Recruiting

Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry

NCT05453461Not ApplicableActive Not RecruitingPrimary

ADVANCED FSHD-COM: New Clinical Outcome Measures to Evaluate Non-ambulant FSHD Patients, a Pilot Study

NCT01671865Active Not RecruitingPrimary

Magnetic Resonance Imaging and Spectroscopy Biomarkers for Facioscapulohumeral Muscular Dystrophy

NCT06708468Not ApplicableRecruiting

Personalized Training for People With Rare Neuromuscular Disorders

NCT04001582RecruitingPrimary

The United Kingdom Facioscapulohumeral Muscular Dystrophy Patient Registry

NCT01931644Completed

At-Home Research Study for Patients With Autoimmune, Inflammatory, Genetic, Hematological, Infectious, Neurological, CNS, Oncological, Respiratory, Metabolic Conditions

NCT02836418Phase 1CompletedPrimary

Study to Evaluate the Long-Term Safety, Tolerability, and Biological Activity of ATYR1940 in Participants With Limb Girdle and Facioscapulohumeral Muscular Dystrophy (FSHD)

NCT02579239Phase 1Completed

Evaluate Safety and Biological Activity of ATYR1940 in Participants With Limb Girdle Muscular Dystrophy 2B (LGMD2B) and Facioscapulohumeral Muscular Dystrophy (FSHD)

NCT06086548Not Yet RecruitingPrimary

Unraveling Metabolic Involvement in Facioscapulohumeral Dystrophy Through Metabolomics

NCT05178706CompletedPrimary

Effectiveness of Upper Extremity Rehabilitation in pwFSHD (Patient With Facioscapulohumeral Dystrophia)

NCT02531217Phase 1CompletedPrimary

Safety, Tolerability, Pharmacokinetics (PK), and Activity of ATYR1940 in Participants With Muscular Dystrophy - Study Extension

NCT03123913Phase 1CompletedPrimary

Study of Testosterone and rHGH in FSHD

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