Facioscapulohumeral Muscular Dystrophy
30
7
10
16
Key Insights
Highlights
Success Rate
89% trial completion (above average)
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 37/100
6.7%
2 terminated out of 30 trials
88.9%
+2.4% vs benchmark
3%
1 trials in Phase 3/4
44%
7 of 16 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.5%
Based on 16 completed trials
Clinical Trials (30)
A First-in-human Study of EPI-321 in Facioscapulohumeral Muscular Dystrophy
Clinical Trial Readiness to Solve Barriers to Drug Development in FSHD
Phase 2 Study Evaluating Apitegromab for the Treatment of FSHD
Quantitative Assessment of Orofacial Muscle Function in FSHD
BetterLife FSHD: A Patient-driven Health and Research Platform
A Study to Evaluate Del-brax (Also Referred to as AOC 1020) in Participants With FSHD
Ultrasound Detection of Early Facial Muscle Changes in FSHD: Thickness and Echo Intensity Findings
Biomarker Development for Muscular Dystrophies
Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry
ADVANCED FSHD-COM: New Clinical Outcome Measures to Evaluate Non-ambulant FSHD Patients, a Pilot Study
Magnetic Resonance Imaging and Spectroscopy Biomarkers for Facioscapulohumeral Muscular Dystrophy
Personalized Training for People With Rare Neuromuscular Disorders
The United Kingdom Facioscapulohumeral Muscular Dystrophy Patient Registry
At-Home Research Study for Patients With Autoimmune, Inflammatory, Genetic, Hematological, Infectious, Neurological, CNS, Oncological, Respiratory, Metabolic Conditions
Study to Evaluate the Long-Term Safety, Tolerability, and Biological Activity of ATYR1940 in Participants With Limb Girdle and Facioscapulohumeral Muscular Dystrophy (FSHD)
Evaluate Safety and Biological Activity of ATYR1940 in Participants With Limb Girdle Muscular Dystrophy 2B (LGMD2B) and Facioscapulohumeral Muscular Dystrophy (FSHD)
Unraveling Metabolic Involvement in Facioscapulohumeral Dystrophy Through Metabolomics
Effectiveness of Upper Extremity Rehabilitation in pwFSHD (Patient With Facioscapulohumeral Dystrophia)
Safety, Tolerability, Pharmacokinetics (PK), and Activity of ATYR1940 in Participants With Muscular Dystrophy - Study Extension
Study of Testosterone and rHGH in FSHD