Diamond-Blackfan Anemia
21
3
4
13
Key Insights
Highlights
Success Rate
81% trial completion
Clinical Risk Assessment
Based on trial outcomes
High Risk
Score: 59/100
14.3%
3 terminated out of 21 trials
81.3%
-5.3% vs benchmark
5%
1 trials in Phase 3/4
62%
8 of 13 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.5%
Based on 13 completed trials
Clinical Trials (21)
Familial Investigations of Childhood Cancer Predisposition
Treosulfan-Based Conditioning Regimen Before a Blood or Bone Marrow Transplant for the Treatment of Bone Marrow Failure Diseases (BMT CTN 1904)
Investigation of the Genetics of Hematologic Diseases
CD34+ (Non-Malignant) Stem Cell Selection for Patients Receiving Allogeneic Stem Cell Transplantation
T-Cell Depleted Alternative Donor Bone Marrow Transplant for Sickle Cell Disease (SCD) and Other Anemias
Phase I/II Pilot Study of Mixed Chimerism to Treat Hemoglobinopathies
Human Placental-Derived Stem Cell Transplantation
Multi-Center Study of Iron Overload: Pilot Study
Multi-Center Study of Iron Overload: Survey Study (MCSIO)
Stem Cell Transplant for Hemoglobinopathy
Bone Marrow Transplant With Abatacept for Non-Malignant Diseases
Fludarabine Phosphate, Melphalan, and Low-Dose Total-Body Irradiation Followed by Donor Peripheral Blood Stem Cell Transplant in Treating Patients With Hematologic Malignancies
Allo-HCT MUD for Non-malignant Red Blood Cell (RBC) Disorders: Sickle Cell, Thal, and DBA: Reduced Intensity Conditioning, Co-tx MSCs
Stem Cell Transplant for Bone Marrow Failure Syndromes
Donor Umbilical Cord Blood Transplant in Treating Patients With Hematologic Cancer
Alemtuzumab, Fludarabine, and Busulfan Followed By Donor Stem Cell Transplant in Treating Young Patients With Hematologic Disorders
Alefacept and Allogeneic Hematopoietic Stem Cell Transplantation
Partially Matched Stem Cell Transplantation for Patients With Refractory Severe Aplastic Anemia or Refractory Cytopenias
Related Hematopoietic Stem Cell Transplantation (HSCT) for Genetic Diseases of Blood Cells
Magnetic Resonance Imaging (MRI) Assessments of the Heart and Liver Iron Load in Patients With Transfusion Induced Iron Overload