Congenital Myopathy
10
2
2
6
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 50/100
0.0%
0 terminated out of 10 trials
100.0%
+13.5% vs benchmark
0%
0 trials in Phase 3/4
0%
0 of 6 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.5%
Based on 6 completed trials
Clinical Trials (10)
Assessment of Safety and Acute Effects of a Knee-hip Powered Soft Exoskeleton in Patients With Neuromuscular Disorders
Assessment of Safety and Acute Effects of a Lower-limb Powered Dermoskeleton in Patients With Neuromuscular Disorders
Muscle Health Measurements Using Electrical Impedance Myography
Changes of Motor Function Tests in Congenital Myopathy Subjects Treated With Oral Salbutamol as Compared to no Treatment
Transcriptomic Analysis to Put an End to Misdiagnosis in Patients With Rare Muscle Diseases
The Prevalence of RYR1-related Disease
Contractile Cross Sectional Areas and Muscle Strength in Patients With Congenital Myopathies
Magnetic Resonance Imaging and Ultrasonography in Evaluation of Muscle Diseases
Bullying in Youth With Muscular Dystrophy and Congenital Myopathies
Aerobic Training in Patients With Congenital Myopathies