Congenital Adrenal Hyperplasia
63
10
13
29
Key Insights
Highlights
Success Rate
85% trial completion
Published Results
16 trials with published results (25%)
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 39/100
7.9%
5 terminated out of 63 trials
85.3%
-1.2% vs benchmark
16%
10 trials in Phase 3/4
55%
16 of 29 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.5%
Based on 29 completed trials
Clinical Trials (63)
A Study in Pediatric Participants With Congenital Adrenal Hyperplasia (Balance-CAH)
A Study to Evaluate Atumelnant in Adults With Congenital Adrenal Hyperplasia
Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Crinecerfont in Participants With Classic Congenital Adrenal Hyperplasia (CAH) Who Are Less Than 4 Years Old
Pharmacokinetics, Safety and Tolerability of Crinecerfont in Participants With Congenital Adrenal Hyperplasia Who Are Less Than 2 Years Old
Retrospective Multicentre Study on the Impact of Neonatal Screening for Congenital Adrenal Hyperplasia in Italy
A Trial of Lu AG13909 in Participants With Congenital Adrenal Hyperplasia
Long-term Safety Study of Chronocort in the Treatment of Participants With Congenital Adrenal Hyperplasia
Institutional Registry of Rare Diseases
A Phase 2 Study to Evaluate the Safety, Efficacy and PK of Tildacerfont in Children Aged 2-17 Years With CAH
A Study of Gene Therapy for Classic Congenital Adrenal Hyperplasia (CAH)
Prenatal Dex Study
A Study of a Virtual Education-Based Transition Intervention to Improve Transition Readiness in Adolescent and Young Adults With Congenital Adrenal Hyperplasia
Androgen Reduction in Congenital Adrenal Hyperplasia, Phase 1
Study of SPR001 in Adults With Classic Congenital Adrenal Hyperplasia
A Ph2b to Evaluate Tildacerfont in the Reduction of Glucocorticoid Steroid Doses in Adult CAH
Evaluate the Safety, Efficacy, and Pharmacokinetics of CRN04894 in Participants With Congenital Adrenal Hyperplasia (TouCAHn)
An Extension Study to Evaluate Safety and Efficacy in Participants Treated With CRN04894
Congenital Adrenal Hyperplasia Once Daily Hydrocortisone Treatment
Investigation of the Etiology of Hypertension and Endothelial Damage in Patients With Cytochrome P450 Oxidoreductase Deficiency
Baby Detect : Genomic Newborn Screening