NCT07592273

Brief Summary

Diabetic Retinopathy (DR) is a common eye condition caused by diabetes, where high blood sugar levels damage the blood vessels in the back part of the eye (called the retina). Over time, this damage can lead to vision problems and even blindness if not treated. This study will assess surabgene lomparvovec (sura-vec) as a potential one-time gene therapy administered in the suprachoroidal space (SCS) for the treatment of diabetic retinopathy (DR) and prevention of vision-threatening events (VTEs) in participants with non-proliferative DR (NPDR) without center-involved diabetic macular edema (CI-DME). This study will consist of 3 portions: a Phase 2b portion, a Phase 3 portion, and a bilateral treatment portion. Approximately 576 adult participants will be enrolled in the study across multiple sites in the United States and Puerto Rico. In the Phase 2b and Phase 3 portions, participants will be randomized to different groups to receive sura-vec and prophylactic steroids or sham and artificial tears in their study eye. If assigned to sham, participants will be given an opportunity to cross over and receive treatment with sura-vec. In the bilateral treatment portion, participants will be enrolled to receive sura-vec and prophylactic steroids in both eyes. In all 3 portions, follow-up in the study will continue through 5 years following administration of sura-vec in each eye. There may be higher treatment burden for participants in this trial compared to their standard of care. Participants will attend regular visits during the study at a clinic. The effect of the treatment will be checked by medical assessments, blood tests, checking for side effects and completing questionnaires.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
576

participants targeted

Target at P75+ for phase_2

Timeline
117mo left

Started May 2026

Longer than P75 for phase_2

Geographic Reach
1 country

2 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 24, 2026

Completed
24 days until next milestone

First Posted

Study publicly available on registry

May 18, 2026

Completed
2 days until next milestone

Study Start

First participant enrolled

May 20, 2026

Completed
2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2028

Expected
7.6 years until next milestone

Study Completion

Last participant's last visit for all outcomes

January 1, 2036

Last Updated

May 20, 2026

Status Verified

May 1, 2026

Enrollment Period

2 years

First QC Date

April 24, 2026

Last Update Submit

May 18, 2026

Conditions

Keywords

Diabetic RetinopathySevere Nonproliferative Diabetic RetinopathyABBV-RGX-314

Outcome Measures

Primary Outcomes (5)

  • Phase 2B: Percentage of Participants Achieving >= 2-Step Improvement from Baseline in Diabetic Retinopathy Severity Scale (DRSS) in the Study Eye

    The DRSS is a scale the measures the severity of DR with a higher score indicating greater severity.

    At Week 52

  • Phase 3: Percentage of Participants Achieving >= 2-Step Improvement from Baseline in Diabetic Retinopathy Severity Scale (DRSS) in the Study Eye

    The DRSS is a scale the measures the severity of DR with a higher score indicating greater severity.

    At Week 52

  • Bilateral Portion: Bilateral portion: Number of participants experiencing ocular Adverse Events (AEs), Serious Adverse Events (SAEs), or any Adverse Events of Special Interest (AESIs)

    Safety of bilateral administration with sura-vec will be assessed with Ocular AEs, SAEs, and AESIs. An AE is defined as any untoward medical occurrence in a patient or clinical investigation participant administered a pharmaceutical product which does not necessarily have a causal relationship with this treatment.

    Up to Approximately Week 104

  • Bilateral Portion: Participants Who Experience Intraocular Inflammation

    Percentage of participants who experience intraocular inflammation.

    Up to Approximately Week 104

  • Bilateral Portion: Participants Who Experience Scleral Inflammation Including Episcleritis

    Percentage of participants who experience scleral inflammation including episcleritis.

    Up to Approximately Week 104

Secondary Outcomes (57)

  • Phase 2B: Percentage of Participants Who Develop a Vision-Threatening Event (VTE) due to Diabetic Retinopathy (DR)

    Up to Approximately Week 52

  • Phase 2B: Percentage of Participants Who Develop a Vision-Threatening Event (VTE) due to Diabetic Retinopathy (DR)

    Up to Approximately Week 104

  • Phase 2B: Percentage of Participants Who Experience Progression to Proliferative Diabetic Retinopathy (PDR) or Anterior Segment Neovascularization (ASNV) in the Study Eye

    Up to Approximately Week 52

  • Phase 2B: Percentage of Participants Who Experience Progression to Proliferative Diabetic Retinopathy (PDR) or Anterior Segment Neovascularization (ASNV) in the Study Eye

    Up to Approximately Week 104

  • Phase 2B: Percentage of Participants Who Develop Center Involved-Diabetic Macular Edema (CI-DME) in the Study Eye

    Up to Approximately Week 52

  • +52 more secondary outcomes

Study Arms (8)

Phase 2b: Surabgene Lomparvovec + Steroid-Regimen A

EXPERIMENTAL

Participants will receive a single Suprachoroidal space (SCS) injection dose of surabgene lomparvovec (sura-vec) + steroid-Regimen A.

Drug: Surabgene LomparvovecDrug: Topical Steroid

Phase 2b: Surabgene Lomparvovec + Steroid-Regimen B

EXPERIMENTAL

Participants will receive a single SCS injection dose of surabgene lomparvovec (sura-vec) + steroid-Regimen B.

Drug: Surabgene LomparvovecDrug: Topical Steroid

Phase 2b: Sham + Artificial Tears -Regimen A

PLACEBO COMPARATOR

Participants will receive a single injection of sham+ artificial tears -Regimen A.

Drug: ShamDrug: Artificial Tears

Phase 2b: Sham + Artificial Tears -Regimen B

PLACEBO COMPARATOR

Participants will receive a single injection of Sham+ artificial tears -Regimen B.

Drug: ShamDrug: Artificial Tears

Phase 3: Surabgene Lomparvovec + Steroid

EXPERIMENTAL

Participants will receive a single SCS injection dose of Surabgene Lomparvovec + Steroid

Drug: Surabgene LomparvovecDrug: Topical Steroid

Phase 3: Sham + Artificial Tears

PLACEBO COMPARATOR

Participants will receive a single injection of Sham + artificial tears.

Drug: ShamDrug: Artificial Tears

Bilateral: B1-Surabgene Lomparvovec + Steroid

EXPERIMENTAL

Participants will receive a single SCS injection dose of Surabgene Lomparvovec + Steroid eye drops in each eye.

Drug: Surabgene LomparvovecDrug: Topical Steroid

Bilateral: B2-Surabgene Lomparvovec + Steroid

EXPERIMENTAL

Participants will receive a single SCS injection dose of Surabgene Lomparvovec +Steroid eye drops in each eye.

Drug: Surabgene LomparvovecDrug: Topical Steroid

Interventions

Solution Injection

Bilateral: B1-Surabgene Lomparvovec + SteroidBilateral: B2-Surabgene Lomparvovec + SteroidPhase 2b: Surabgene Lomparvovec + Steroid-Regimen APhase 2b: Surabgene Lomparvovec + Steroid-Regimen BPhase 3: Surabgene Lomparvovec + Steroid
ShamDRUG

needleless injection without fluid

Phase 2b: Sham + Artificial Tears -Regimen APhase 2b: Sham + Artificial Tears -Regimen BPhase 3: Sham + Artificial Tears

Topical Drops

Bilateral: B1-Surabgene Lomparvovec + SteroidBilateral: B2-Surabgene Lomparvovec + SteroidPhase 2b: Surabgene Lomparvovec + Steroid-Regimen APhase 2b: Surabgene Lomparvovec + Steroid-Regimen BPhase 3: Surabgene Lomparvovec + Steroid

Topical Drops

Phase 2b: Sham + Artificial Tears -Regimen APhase 2b: Sham + Artificial Tears -Regimen BPhase 3: Sham + Artificial Tears

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Ocular (Study Eye for Phase 2b and Phase 3 Portions; Both Eyes for Bilateral Portion)
  • Moderately severe or severe nonproliferative diabetic retinopathy (NPDR) (early treatment diabetic retinopathy study-diabetic retinopathy severity scale \[DRSS\] level 47 or 53) for which panretinal photocoagulation (PRP) or anti- vascular endothelial growth factor (VEGF) can be safely deferred for at least 6 months after Screening Visit 1.
  • Best-corrected visual acuity (BCVA) in the study eye of \>= 69 Early treatment diabetic retinopathy study letters (approximate Snellen equivalent 20/40 or better) at Screening Visit 1.
  • Systemic
  • Diabetic retinopathy (DR) secondary to diabetes mellitus Type 1 or 2 with a hemoglobin A1c (HbA1c)\< 12% within 60 days prior to Screening Visit 1.

You may not qualify if:

  • Ocular (Study Eye for Phase 2b and Phase 3 Portions; Both Eyes for Bilateral Portion)
  • Presence of active center involved-diabetic macular edema (CI-DME) in the study eye as determined by spectral domain optical coherence tomography (SD-OCT) evaluated by the central reading center (CRC), using the following threshold:
  • Central retinal thickness (CRT) \>= 320 μm as measured by Heidelberg Spectralis SD-OCT (conversion to equivalent measurement is required and performed by the CRC if imaging is done with another SD-OCT instrument).
  • Active ocular inflammation including scleral inflammation (including episcleritis) or ocular/ periocular infection present in either eye at Screening Visit 1 or Screening Visit 2
  • Neovascularization from a cause other than DR, per investigator
  • Evidence or documented history of panretinal photocoagulation (PRP) or retinal laser therapy
  • History of intravitreal therapy, including anti-VEGF and long- or short-acting steroid therapy, within the prior 6 months and documentation of more than 10 prior anti-VEGF or short acting steroid intravitreal injections within 36 months of Screening Visit 1
  • Pregnant and breastfeeding individuals are excluded from this clinical study.
  • Systemic
  • Initiation of intensive insulin treatment (pump or multiple daily injections) within the past 6 months or plans to do so within 52 weeks after Day 1
  • Initiation of any treatment containing a GLP-1 receptor agonist within the 3 months prior to Screening Visit 1 or plans to do so within 52 weeks after Day 1
  • Pregnant and breastfeeding individuals are excluded from this clinical study

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (2)

University Retina - Oak Forest /ID# 283021

Oak Forest, Illinois, 60452, United States

RECRUITING

Austin Research Center for Retina /ID# 276101

Austin, Texas, 78705, United States

RECRUITING

Related Links

MeSH Terms

Conditions

Diabetic Retinopathy

Interventions

salicylhydroxamic acidSteroidsLubricant Eye Drops

Condition Hierarchy (Ancestors)

Retinal DiseasesEye DiseasesDiabetic AngiopathiesVascular DiseasesCardiovascular DiseasesDiabetes ComplicationsDiabetes MellitusEndocrine System Diseases

Intervention Hierarchy (Ancestors)

Fused-Ring CompoundsPolycyclic CompoundsOphthalmic SolutionsPharmaceutical SolutionsSolutionsPharmaceutical PreparationsTherapeutic UsesPharmacologic ActionsChemical Actions and UsesLubricantsSpecialty Uses of Chemicals

Study Officials

  • ABBVIE INC.

    AbbVie

    STUDY DIRECTOR

Central Study Contacts

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 24, 2026

First Posted

May 18, 2026

Study Start

May 20, 2026

Primary Completion (Estimated)

June 1, 2028

Study Completion (Estimated)

January 1, 2036

Last Updated

May 20, 2026

Record last verified: 2026-05

Data Sharing

IPD Sharing
Will share

AbbVie is committed to responsible clinical trial data sharing. This includes access to anonymized, individual and trial-level data (analysis data sets), as well as other information.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
For details on when studies are available for sharing, visit https://vivli.org/ourmember/abbvie/
Access Criteria
To learn more about the process, or to submit a request, visit the following link https://www.abbvieclinicaltrials.com/hcp/data-sharing/
More information

Locations