NCT07467733

Brief Summary

This clinical study aims to evaluate the safety and preliminary therapeutic potential of mesenchymal stem cell-derived therapies in patients diagnosed with spinocerebellar palsy. The investigational treatment includes neuroinduced mesenchymal stem cells and their derived exosomes administered via intravenous and intranasal infusion.

Trial Health

63
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
90

participants targeted

Target at P75+ for phase_1

Timeline
35mo left

Started Jun 2026

Typical duration for phase_1

Geographic Reach
1 country

1 active site

Status
not yet recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

Study Progress7%
Jun 2026Jun 2029

First Submitted

Initial submission to the registry

March 9, 2026

Completed
3 days until next milestone

First Posted

Study publicly available on registry

March 12, 2026

Completed
3 months until next milestone

Study Start

First participant enrolled

June 1, 2026

Completed
2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2028

Expected
1 year until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2029

Last Updated

March 12, 2026

Status Verified

March 1, 2026

Enrollment Period

2 years

First QC Date

March 9, 2026

Last Update Submit

March 9, 2026

Conditions

Keywords

ataxiamesenchymal stem cellsexosomes

Outcome Measures

Primary Outcomes (2)

  • MDS-UPDRS

    Change in motor symptoms measured by the Movement Disorder Society Unified Parkinson's Disease Rating Scale (MDS-UPDRS) Part III - Motor Examination Range: 0-132 Where 132 is the worst motor impairment; 0 - the best motor impairment

    92 weeks

  • SARA

    Change in motor function as measured by the Scale for the Assessment and Rating of Ataxia (SARA) Range: 0-40 40 - the most severe ataxia; 0 - the mildest

    92 weeks

Secondary Outcomes (1)

  • ICARS

    92 weeks

Study Arms (3)

Neuroinduced Mesenchymal Stem Cells

EXPERIMENTAL
Drug: Intrathecal infusion

Mesenchymal Stem Cell Derived Exosomes

EXPERIMENTAL
Drug: Intranasal infusion

Saline solution

PLACEBO COMPARATOR
Drug: Intranasal infusion

Interventions

200,000,000 neuroinduced mesenchymal stem cells administered via intravenous infusion.

Neuroinduced Mesenchymal Stem Cells

Intranasal infusion of purified exosomes derived from mesenchymal stem cells

Mesenchymal Stem Cell Derived ExosomesSaline solution

Eligibility Criteria

Age18 Years - 45 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64)

You may qualify if:

  • Clinical diagnosis of spinocerebellar palsy confirmed by neurological examination; Disease duration ≤10 years; Ability to provide informed consent.

You may not qualify if:

  • Severe systemic illness; Active infection; History of malignancy within 5 years; Prior stem cell therapy; Pregnancy or breastfeeding.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

BioCells Medical

Warsaw, 02-797, Poland

Location

MeSH Terms

Conditions

Ataxia

Condition Hierarchy (Ancestors)

DyskinesiasNeurologic ManifestationsNervous System DiseasesSigns and SymptomsPathological Conditions, Signs and Symptoms

Central Study Contacts

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Biocells Medical

Study Record Dates

First Submitted

March 9, 2026

First Posted

March 12, 2026

Study Start

June 1, 2026

Primary Completion (Estimated)

June 1, 2028

Study Completion (Estimated)

June 1, 2029

Last Updated

March 12, 2026

Record last verified: 2026-03

Data Sharing

IPD Sharing
Will not share

Locations