NCT07419932

Brief Summary

This multicenter observational study aims to evaluate the safety and efficacy of neoadjuvant therapy in patients with locally advanced thyroid cancer, focusing on imaging, biochemical, and pathological responses, as well as short-term surgical outcomes and long-term prognosis.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
120

participants targeted

Target at P50-P75 for all trials

Timeline
38mo left

Started Dec 2025

Typical duration for all trials

Geographic Reach
1 country

1 active site

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

Study Progress12%
Dec 2025Jun 2029

Study Start

First participant enrolled

December 23, 2025

Completed
2 months until next milestone

First Submitted

Initial submission to the registry

February 6, 2026

Completed
13 days until next milestone

First Posted

Study publicly available on registry

February 19, 2026

Completed
2.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 31, 2028

Expected
6 months until next milestone

Study Completion

Last participant's last visit for all outcomes

June 30, 2029

Last Updated

February 19, 2026

Status Verified

February 1, 2026

Enrollment Period

3 years

First QC Date

February 6, 2026

Last Update Submit

February 12, 2026

Conditions

Keywords

Thyroid Cancerlocally advancedNeoadjuvant Therapy

Outcome Measures

Primary Outcomes (3)

  • Radiographic Response

    Radiographic response of tumors and lymph nodes to neoadjuvant treatment will be assessed using contrast-enhanced computed tomography (CT) and defined by RECIST v1.1. Complete Response (CR) is defined as disappearance of all target lesions. Partial response (PR) is defined as ≥30% decrease in the sum of the longest diameter of target lesion; progressive disease (PD) as ≥20% increase in the sum of the longest diameter of target lesions. Stable disease (SD) is defined as \<20% increase and \<30% decrease in the sum of the longest diameter of target lesions. The objective response rate (ORR) will be calculated as the proportion of patients achieving CR or PR.

    From baseline to preoperative imaging assessment after neoadjuvant therapy.

  • Pathologic Response

    Pathologic response in resected tumors and lymph nodes will be assessed on hematoxylin and eosin (H\&E)-stained slides of the entire tumor bed and all sampled lymph nodes. All slides will be digitally scanned and independently reviewed by two pathologists. Pathological complete response (pCR) is defined as the absence of viable tumor cells in all examined slides. For this study, pathological partial response (pPR) is defined as \<50% viable residual tumor, and pathological non-response (pNR) as ≥50% viable residual tumor in the resected specimen.

    At the time of surgery, based on postoperative pathological evaluation.

  • Progression-Free Survival (PFS)

    Time from surgery to the earliest date of disease progression or all-cause death.

    From the date of surgery until the first documented disease progression or death from any cause, whichever occurs first, assessed up to 24 months.

Secondary Outcomes (6)

  • Biochemical Response

    From 4 weeks to 12 months after surgery.

  • R0/1 Resection Rate

    At the time of surgery.

  • Change in Surgical Complexity and Morbidity Score

    From baseline to preoperative imaging assessment after neoadjuvant therapy.

  • Surgery Related Adverse Events

    During surgery or within 30 days after surgery.

  • Incidence of Grade ≥ 3 Neoadjuvant Treatment-Related Advert Events

    From baseline to 30 days after the last dose of neoadjuvant therapy.

  • +1 more secondary outcomes

Other Outcomes (1)

  • Tumor Microenvironment and Immune Profiling

    From baseline (pre-neoadjuvant therapy biopsy) to surgery.

Study Arms (2)

Neoadjuvant Treatment Group

Participants will undergo neoadjuvant treatment with multikinase inhibitors (mTKIs), specific receptor inhibitors (including RET inhibitors or BRAF ± MEK inhibitors), or combination regimens containing a PD-1 inhibitor. All regimens will be administered for at least two cycles prior to surgery.

Drug: Multitarget Tyrosine Kinase InhibitorsDrug: BRAF inhibitor dabrafenib and MEK inhibitor trametinibDrug: RET InhibitorDrug: PD(L)-1 inhibitorProcedure: BiopsyProcedure: Surgery

Upfront Surgery Group

The participants in this group will undergo radical surgery directly after the diagnosis of LATC, based on MDT consensus and patient's preference.

Procedure: BiopsyProcedure: Surgery

Interventions

Patients with or without actionable genomic alterations may receive a multikinase inhibitor (e.g., lenvatinib or anlotinib) as neoadjuvant therapy.

Also known as: Lenvatinib, Anlotinib
Neoadjuvant Treatment Group

Patients with BRAF V600E mutation may receive combination therapy with the BRAF inhibitor dabrafenib and the MEK inhibitor trametinib.

Also known as: Dabrafenib, Trametinib
Neoadjuvant Treatment Group

Patients with RET fusion may receive a selective RET inhibitor (e.g., selpercatinib).

Also known as: Selpercatinib, Pralsetinib
Neoadjuvant Treatment Group

In selected cases, combination regimens incorporating immunotherapy may be considered.

Also known as: Pembrolizumab, Nivolumab
Neoadjuvant Treatment Group
BiopsyPROCEDURE

While fine-needle aspiration (FNA) is the standard initial diagnostic modality for thyroid nodules, core needle biopsy (CNB) is performed to obtain tissue cores for histological subtyping and molecular profiling in locally advanced cases.

Also known as: Core Needle Biopsy, Fine-needle Aspiration
Neoadjuvant Treatment GroupUpfront Surgery Group
SurgeryPROCEDURE

Patients considered resectable after neoadjuvant therapy will undergo definitive surgery, as determined by consensus of the multidisciplinary team (MDT).

Neoadjuvant Treatment Group

Eligibility Criteria

Age14 Years - 80 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Patients diagnosed with LATC may be managed with either neoadjuvant therapy followed by surgery or upfront surgery, depending on resectability and multidisciplinary team assessment.

You may qualify if:

  • Age ≥ 14 years at enrollment.
  • Eastern Cooperative Oncology Group (ECOG) performance status of 0-2.
  • Histologically or cytologically confirmed thyroid carcinoma, including differentiated thyroid carcinoma (DTC), medullary thyroid carcinoma (MTC), poorly differentiated thyroid carcinoma (PDTC), and anaplastic thyroid carcinoma (ATC).
  • LATC defined as clinical stage T4N0-1 at baseline, as confirmed by a multidisciplinary thyroid oncology board.
  • For patients with distant metastasis, the potential benefit from surgical intervention must be documented by the treating team.
  • Presence of at least one measurable lesion, according to Response Evaluation Criteria in Solid Tumors (RECIST) version 1.1.
  • Normal function of major organs.
  • Written informed consent obtained.

You may not qualify if:

  • Patients who refuse tumor tissue biopsy or surgery.
  • Prior thyroid or major neck surgery.
  • History of other treatments for cancer, including surgery, chemotherapy, radiotherapy, or molecular targeted therapy, that may affect the current treatment plan.
  • Concurrent active malignancies.
  • Uncontrolled systemic diseases, including diabetes, hypertension, etc.
  • Pregnancy or breastfeeding.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Fujian Medical University Union Hospital

Fuzhou, Fujian, 350001, China

RECRUITING

Biospecimen

Retention: SAMPLES WITH DNA

Fresh tumor specimens will be prospectively collected from patients with locally advanced thyroid cancer (LATC) enrolled in this study after written informed consent is obtained. These specimens include tumor tissue obtained by core needle biopsy prior to neoadjuvant therapy, as well as matched fresh tumor tissue and adjacent non-tumor tissue collected during subsequent surgical resection.

MeSH Terms

Conditions

Thyroid Neoplasms

Interventions

lenvatinibanlotinibdabrafenibtrametinibselpercatinibpralsetinibpembrolizumabNivolumabBiopsyBiopsy, Large-Core NeedleBiopsy, Fine-NeedleSurgical Procedures, Operative

Condition Hierarchy (Ancestors)

Endocrine Gland NeoplasmsNeoplasms by SiteNeoplasmsHead and Neck NeoplasmsEndocrine System DiseasesThyroid Diseases

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulinsCytodiagnosisCytological TechniquesClinical Laboratory TechniquesDiagnostic Techniques and ProceduresDiagnosisSpecimen HandlingDiagnostic Techniques, SurgicalInvestigative TechniquesBiopsy, NeedlePunctures

Central Study Contacts

Wenxin Zhao, M.D., Ph.D.

CONTACT

Zihan Tang, M.D.

CONTACT

Study Design

Study Type
observational
Observational Model
CASE CONTROL
Time Perspective
PROSPECTIVE
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Professor and Chief Surgeon, Department of Thyroid Surgery

Study Record Dates

First Submitted

February 6, 2026

First Posted

February 19, 2026

Study Start

December 23, 2025

Primary Completion (Estimated)

December 31, 2028

Study Completion (Estimated)

June 30, 2029

Last Updated

February 19, 2026

Record last verified: 2026-02

Data Sharing

IPD Sharing
Will not share

Locations