NCT07161687

Brief Summary

A study to evaluate the safety of Hympavzi under the actual use in patients with congenital hemophilia who do not have inhibitors.

Trial Health

75
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
50

participants targeted

Target at P25-P50 for all trials

Timeline
48mo left

Started Oct 2025

Longer than P75 for all trials

Geographic Reach
1 country

1 active site

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress12%
Oct 2025Apr 2030

First Submitted

Initial submission to the registry

September 2, 2025

Completed
7 days until next milestone

First Posted

Study publicly available on registry

September 9, 2025

Completed
2 months until next milestone

Study Start

First participant enrolled

October 30, 2025

Completed
4.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 11, 2030

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 11, 2030

Last Updated

March 30, 2026

Status Verified

March 1, 2026

Enrollment Period

4.4 years

First QC Date

September 2, 2025

Last Update Submit

March 24, 2026

Conditions

Keywords

Marstacimab,Hympavzi,Hemophilia

Outcome Measures

Primary Outcomes (1)

  • Number of the participants with adverse drug reactions

    An adverse drug reaction (ADR) was a treatment-related adverse event, and any untoward medical occurrence attributed to Himpavzi in a participant who received Himpavzi. A serious adverse drug reaction (SADR) was a treatment-related adverse event resulting in any of the following outcomes or deemed significant for any other reason: death; life-threatening; initial or prolonged inpatient hospitalization; persistent or significant disability/incapacity; congenital anomaly/birth defect. Relatedness to Himpavzi was assessed by the physician.

    The evaluation period is from the first dose of Himpavzi up to 156 weeks (3 years).

Study Arms (1)

Marstacimab

hemophilia patients without inhibitor

Drug: Marstacimab

Interventions

For patients aged 12 years or older and weighing at least 35 kg, marstacimab is administered subcutaneously at a dose of 300 mg as the initial dose, followed by 150 mg once weekly. If the patient weighs 50 kg or more and shows an inadequate response, the dose may be increased to 300 mg once weekly for subcutaneous administration.

Also known as: Hympavzi
Marstacimab

Eligibility Criteria

Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)
Sampling MethodProbability Sample
Study Population

All patients who have received at least one dose of this drug after the launch of this drug.

You may qualify if:

  • Patients who have received at least one dose of this drug after the launch of this drug

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Pfizer

Tokyo, Japan

Location

Related Links

MeSH Terms

Conditions

Hemophilia A

Interventions

marstacimab

Condition Hierarchy (Ancestors)

Blood Coagulation Disorders, InheritedBlood Coagulation DisordersHematologic DiseasesHemic and Lymphatic DiseasesCoagulation Protein DisordersHemorrhagic DisordersGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and Abnormalities

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 2, 2025

First Posted

September 9, 2025

Study Start

October 30, 2025

Primary Completion (Estimated)

April 11, 2030

Study Completion (Estimated)

April 11, 2030

Last Updated

March 30, 2026

Record last verified: 2026-03

Data Sharing

IPD Sharing
Will not share

Pfizer will provide access to individual de-identified participant data and related study documents (e.g. protocol, Statistical Analysis Plan (SAP), Clinical Study Report (CSR)) upon request from qualified researchers, and subject to certain criteria, conditions, and exceptions. Further details on Pfizer's data sharing criteria and process for requesting access can be found at: https://www.pfizer.com/science/clinical\_trials/trial\_data\_and\_results/data\_requests.

Locations